- ICH GCP
- US Clinical Trials Registry
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Search clinical trials for: Myotonic dystrophy
Total 1185 results
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Spark TherapeuticsActive, not recruitingConfirmed Biallelic RPE65 Mutation-associated Retinal DystrophyUnited States
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Columbia UniversityUniversitat Autonoma de Barcelona; Instituto de Salud Carlos III; University... and other collaboratorsActive, not recruitingThymidine Kinase 2 Deficiency | Mitochondrial DNA Depletion Syndrome 2 Myopathic TypeUnited States
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PTC TherapeuticsCompletedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, Duchenne | Musculoskeletal DiseaseUnited States, Taiwan, India, Korea, Republic of, Thailand, Australia, Brazil, Bulgaria, Canada, China, Hong Kong, Malaysia, Mexico, Poland, Puerto Rico, Russian Federation, Turkey, Japan
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Hospital of South West JutlandActive, not recruitingBariatric Surgery Candidate | Male Hypogonadism | Muscle LossDenmark
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Çağtay MadenCompleted
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ItalfarmacoCompletedDuchenne and Becker Muscular Dystrophy | Polycytemia VeraCanada
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Innostellar Biotherapeutics Co.,LtdActive, not recruitingInherited Retinal Dystrophy Associated With RPE65 MutationsChina
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University College, LondonRadboud University Medical Center; Groupe Hospitalier Pitie-Salpetriere; Leiden... and other collaboratorsCompletedDuchenne Muscular DystrophyNetherlands, France, United Kingdom
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Nanoscope Therapeutics Inc.CompletedRetinitis Pigmentosa | Retinal DystrophyUnited States, Puerto Rico
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Endo PharmaceuticalsCompletedCarpal Tunnel Syndrome | Complex Regional Pain Syndrome | Peripheral Neuropathy | Diabetic Neuropathy | Postherpetic Neuralgia | HIV Neuropathy | Idiopathic Sensory NeuropathyUnited States
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Sun Yat-sen UniversityCompletedRetinitis Pigmentosa | Inherited Retinal Dystrophy | Retina DisorderChina
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aTyr Pharma, Inc.CompletedFacioscapulohumeral Muscular Dystrophy | Limb Girdle Muscular DystrophyUnited States, Denmark, Italy
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University of AarhusActive, not recruitingFuchs' Endothelial DystrophyDenmark
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The Emmes Company, LLCJain Foundation; Coalition to Cure Calpain 3 (C3)Terminated
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Nanoscope Therapeutics Inc.Enrolling by invitationEye Diseases | Retinal Degeneration | Retinal Diseases | Retinitis Pigmentosa | Retinitis | Eye Diseases, Hereditary | Retinal DystrophiesUnited States, Puerto Rico
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Casa Colina Hospital and Centers for HealthcareCompletedMultiple Sclerosis | Amyotrophic Lateral Sclerosis | Muscular Dystrophies | Graves Disease | Myasthenia Gravis | Traumatic Brain Injury | Stroke, Ischemic | Stroke, Acute | Stroke Hemorrhagic | SCI - Spinal Cord Injury | Guillain-Barre Syndrome | Lupus Erythematosus | Stroke (CVA) or TIA | Ehlers-Danlos Syndromes...United States
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Hacettepe UniversityCompleted
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Sarepta Therapeutics, Inc.Active, not recruitingDuchenne Muscular DystrophyUnited States, Belgium, Spain, United Kingdom, Netherlands, Germany, Canada, Italy
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University of WashingtonNational Institute of Nursing Research (NINR)CompletedPhysical DisabilityUnited States
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Radboud University Medical CenterCompletedMDC1A | SELENON-related MyopathyNetherlands
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Rigshospitalet, DenmarkFunding: Toyota Foundation; Funding: Hede Nielsen Foundation; Funding: Grosserer... and other collaboratorsActive, not recruiting
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Centre Hospitalier Universitaire de NiceCompletedMuscular DystrophiesFrance
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Sarepta Therapeutics, Inc.Active, not recruiting
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National Institute of Geriatrics, Rheumatology...CompletedComplex Regional Pain SyndromesPoland
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Centre Hospitalier Universitaire de NiceCompletedFacio-Scapulo-Humeral DystrophyFrance
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Centre Hospitalier Universitaire de NiceCompletedMuscular Dystrophy, FacioscapulohumeralFrance
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Centre Hospitalier Universitaire de NiceCompletedMuscular Dystrophy, FacioscapulohumeralFrance
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FibroGenActive, not recruitingDuchenne Muscular DystrophyUnited States, Spain, Canada, Australia, China, Italy, Belgium, France, Netherlands, Austria, United Kingdom
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Nanoscope Therapeutics Inc.Completed
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Nanoscope Therapeutics Inc.Enrolling by invitationStargardt DiseaseUnited States
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Santhera PharmaceuticalsAvailableDuchenne Muscular DystrophyUnited States, Canada, Israel
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Sarepta Therapeutics, Inc.Hoffmann-La RocheActive, not recruitingDuchenne Muscular DystrophyUnited States, Japan, Taiwan, Belgium, Spain, Germany, Hong Kong, Italy, United Kingdom
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ItalfarmacoCromsourceEnrolling by invitationDuchenne Muscular DystrophySpain, United States, Canada, Belgium, France, Israel, Italy, Netherlands, Serbia, Germany, United Kingdom
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Trefoil Therapeutics, Inc.CompletedCorneal Endothelial DystrophyUnited States
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Trefoil Therapeutics, Inc.CompletedFuchs' Endothelial Dystrophy | Fuchs Dystrophy | FuchsUnited States
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ItalfarmacoCompletedDuchenne Muscular Dystrophy (DMD)Italy
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Trefoil Therapeutics, Inc.CompletedEndothelial Dysfunction | Corneal Endothelial Dystrophy | Pseudophakic Bullous Keratopathy | Fuchs Endothelial Corneal DystrophyUnited States
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.CompletedDuchenne Muscular DystrophyKorea, Republic of, Chile, Taiwan, China, United States, United Kingdom, Netherlands, Spain, Australia, Norway, Russian Federation, Greece, Italy, Turkey, Mexico, Canada, Hong Kong, New Zealand, Ukraine
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Lokman Hekim ÜniversitesiCompletedDuchenne Muscular DystrophyTurkey
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Kevin FlaniganSarepta Therapeutics, Inc.Completed
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Capricor Inc.Active, not recruiting
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University Hospital, MotolCompletedComplex Regional Pain Syndrome Type I
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Sarepta Therapeutics, Inc.CompletedMuscular Dystrophy, DuchenneUnited States
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Columbia UniversityActive, not recruitingAge-related Macular Degeneration | Retinitis Pigmentosa | Vitelliform Macular Dystrophy | Choroidal Ischemia | Central Serous RetinopathyUnited States
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Kevin FlaniganMuscular Dystrophy AssociationTerminated
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aTyr Pharma, Inc.CompletedLimb-Girdle Muscular Dystrophies | Facioscapulohumeral Muscular DystrophyUnited States, Denmark, France
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aTyr Pharma, Inc.CompletedFacioscapulohumeral Muscular Dystrophy (FSHD)United States, France, Italy
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Astellas Pharma IncTerminatedDuchenne Muscular Dystrophy (DMD)United States
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Seoul National UniversitySMG-SNU Boramae Medical CenterCompletedComplex Regional Pain Syndromes | Neuropathic Pain | Phantom Limb Pain | Postherpetic Neuralgia | Post-Traumatic Neuralgia | Chronic Post Surgical PainKorea, Republic of
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Solid Biosciences Inc.Active, not recruitingDuchenne Muscular DystrophyUnited States