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- US Clinical Trials Registry
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Search clinical trials for: Rod-cone Dystrophy
Total 1177 results
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FibroGenTerminatedDuchenne Muscular DystrophyUnited States
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Nationwide Children's HospitalParent Project Muscular DystrophyCompletedBecker Muscular Dystrophy | Sporadic Inclusion Body MyositisUnited States
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Sarepta Therapeutics, Inc.TerminatedMuscular Dystrophy, DuchenneUnited States, Canada
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Hospital for Special Surgery, New YorkCompleted
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Children's Hospital Medical Center, CincinnatiActive, not recruitingMusculoskeletal Abnormalities | Duchenne Muscular DystrophyUnited States
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Northwestern UniversityCompletedBecker Muscular Dystrophy | Limb-girdle Muscular DystrophyUnited States
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Children's National Research InstituteActive, not recruitingGenetic Diseases, Inborn | Musculoskeletal Diseases | Muscular Dystrophies | Cardiac FibrosisUnited States
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Sarepta Therapeutics, Inc.Active, not recruiting
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Children's National Research InstituteFoundation to Eradicate DuchenneActive, not recruitingDuchenne Muscular DystrophyUnited States
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Emory UniversityTerminated
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Kevin FlaniganActive, not recruitingDuchenne Muscular DystrophyUnited States
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Erasmus Medical CenterEnrolling by invitationComplex Regional Pain Syndromes | CRPS (Complex Regional Pain Syndromes)Netherlands
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AMO Pharma LimitedCompletedCongenital Myotonic DystrophyUnited States, Canada, New Zealand, Australia, United Kingdom
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Price Vision GroupKala Pharmaceuticals, Inc.CompletedCorneal Edema | Corneal Endothelial DystrophyUnited States
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Assistance Publique - Hôpitaux de ParisCompletedDuchenne Muscular Dystrophy | Spinal Muscular AtrophyFrance
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State University of New York at BuffaloActive, not recruitingFuchs DystrophyUnited States
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University Hospital, ToulouseCompleted
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Hugo W. Moser Research Institute at Kennedy Krieger...Active, not recruitingFacioscapulohumeral Muscular DystrophyUnited States
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Sarepta Therapeutics, Inc.TerminatedAn Extension Study to Evaluate Casimersen or Golodirsen in Patients With Duchenne Muscular DystrophyDuchenne Muscular DystrophyUnited States, Belgium, Canada, Spain, United Kingdom, Czechia, Germany, Israel, Bulgaria, France, Italy, Poland, Sweden
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Sarepta Therapeutics, Inc.TerminatedDuchenne Muscular DystrophyBelgium, France, Italy, United Kingdom
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aTyr Pharma, Inc.CompletedFacioscapulohumeral Muscular DystrophyUnited States, Italy, Netherlands
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Ondokuz Mayıs UniversityCompletedDuchenne Muscular Dystrophy (DMD)Turkey
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Solid Biosciences Inc.CompletedDuchenne Muscular DystrophyUnited States
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Assistance Publique - Hôpitaux de ParisNational Research Agency, FranceCompletedRheumatoid Arthritis | Uveitis | Vasculitis | Type 1 Diabetes | Crohn's Disease | Myositis | Healthy Volunteer | Ankylosing Spondylitis | FMF | Systemic Lupus Erythematosus/Antiphospholipid Syndrome | Cryopyrin-Associated Periodic Syndromes /TNF-receptor Associated Periodic Syndrome | Ulcerative Rectocolitis | Unclassified...France
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Sarepta Therapeutics, Inc.Hoffmann-La RocheEnrolling by invitation
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Hacettepe UniversityCompletedDuchenne Muscular Dystrophy | Ambulation Difficulty | Ambulation Disorder, NeurologicTurkey
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Daiichi Sankyo Co., Ltd.Active, not recruitingDuchenne Muscular DystrophyJapan
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University Eye Hospital, FreiburgCompletedFuchs' Endothelial DystrophyGermany
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IRCCS San Camillo, Venezia, ItalyUniversita di Verona; Fondazione IRCCS Ca' Granda, Ospedale Maggiore Policlinico and other collaboratorsEnrolling by invitationCalpain-3 Deficiency Limb Girdle Muscular Dystrophy Type 2AItaly
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Avidity Biosciences, Inc.Active, not recruitingNervous System Diseases | Genetic Diseases, Inborn | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Neurodegenerative Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Heredodegenerative Disorders, Nervous System | Myotonic Dystrophy | Myotonic Disorders | Myotonic Dystrophy... and other conditionsUnited States
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Alcon ResearchCompletedKeratoconjunctivitis | Corneal Edema | Corneal Ulcer | Bullous Keratopathy | Bell Palsy | Corneal Dystrophy | Entropion | Filamentary Keratitis | Corneal Erosion | Foreign Body in Cornea | Sicca Syndrome; Keratoconjunctivitis (Etiology)United States
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Alaska Blind Child DiscoverySuspendedAmblyopia | Color Vision Defects | Visual SuppressionUnited States
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.CompletedDuchenne Muscular DystrophySpain, United States, Russian Federation, Italy, China, Turkey
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Anita Syla LokajEnrolling by invitation
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Fulcrum TherapeuticsActive, not recruitingFacioscapulohumeral Muscular Dystrophy 1Netherlands
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Fulcrum TherapeuticsActive, not recruitingFacioscapulohumeral Muscular Dystrophy (FSHD)United States, Canada, France, Spain
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Batman Training and Research HospitalCompletedCorneal Dystrophy | Macular Dystrophy | Hyperemesis Gravidarum - SevereTurkey
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Sarepta Therapeutics, Inc.Nationwide Children's HospitalCompleted
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Helsinki University Central HospitalTurku University HospitalActive, not recruitingTranscranial Magnetic Stimulation | Complex Regional Pain Syndrome of Upper Limb (Disorder)Finland
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Brock UniversityCompletedMultiple Sclerosis | Inflammation | Muscular Dystrophies | Spinal Cord Injuries | Diet HabitCanada
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Élise DuchesneMuscular Dystrophy CanadaCompletedAutosomal Recessive Spastic Ataxia of Charlevoix-SaguenayCanada
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Universidad de AlmeriaCompletedNeurologic Disorder | Pediatric Disorder | Duchenne | Sensorimotor Disorder NosSpain
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University of RochesterCompletedFacioscapulohumeral Muscular DystrophyUnited States
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National Neuroscience InstituteNanyang Technological University; Institute for Infocomm Research; Institute... and other collaboratorsActive, not recruitingMotor Neuron Disease | Amyotrophic Lateral Sclerosis | Muscular Dystrophies | Spinal Cord Injuries | Tetraplegia | Tetraplegia/Tetraparesis | Locked-in SyndromeSingapore
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Vissum, Instituto Oftalmológico de AlicanteInstituto de Salud Carlos III; Universidad Miguel Hernandez de ElcheCompletedKeratoconus | Treatment | Therapy | Corneal Dystrophy | Ophthalmological DisorderSpain
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MeiraGTx UK II LtdJanssen, LPActive, not recruitingRetinitis PigmentosaUnited States, United Kingdom, Canada
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Hospital of South West JutlandTerminated
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Santhera PharmaceuticalsNo longer availableDuchenne Muscular DystrophyUnited States
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Edgewise Therapeutics, Inc.CompletedNervous System Diseases | Genetic Diseases, Inborn | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Healthy VolunteerUnited States