- ICH GCP
- US Clinical Trials Registry
- Search trials
Search clinical trials for: sphingolipidoses
Total 483 results
-
University of RostockCompletedStroke, Acute | Cerebrovascular Accident | Cerebral StrokeGermany, Poland
-
Klinikum Wels-GrieskirchenGenzyme, a Sanofi CompanyCompletedFocus of Study: Prevalence of Fabry Disease in CKD PopulationAustria
-
The Hospital for Sick ChildrenCompletedGangliosidoses, GM2 | Tay-Sachs Disease | Sandhoff DiseaseCanada
-
University Hospital, GhentCompletedBelgian Screening Project for the Detection of Anderson-Fabry Disease in Hypertrophic CardiomyopathyLeft Ventricular HypertrophyBelgium
-
Nantes University HospitalCompletedPatients With Gaucher's DiseaseFrance
-
Francisco Marín OrtuñoHospital General Universitario Elche; Hospital Universitario San Juan de AlicanteUnknownRight Ventricular Hypertrophy | Fabry Disease, Cardiac Variant
-
National Institute of Neurological Disorders and...CompletedFabry DiseaseUnited States
-
Medical University of ViennaMedical University of GrazUnknownFabry Disease | Left Ventricular HypertrophyAustria
-
Centre Hospitalier Universitaire de NiceUnknown
-
The Cooper Health SystemCompletedMetachromatic LeukodystrophyUnited States
-
Assistance Publique - Hôpitaux de ParisShire; Zymenex A/S; European Leukodystrophy AssociationCompletedMetachromatic LeukodystrophyFrance
-
Amicus TherapeuticsCompleted
-
Amicus TherapeuticsTerminatedType 1 Gaucher DiseaseUnited States, United Kingdom
-
ActelionCompleted
-
Children's National Research InstituteActelionCompletedSandhoff Disease | GM2 Gangliosidoses | Tay-SachsUnited States
-
National Institute of Neurological Disorders and...CompletedBrain Neoplasm | Alzheimer's Disease | Niemann Pick DiseaseUnited States
-
National Institute of Neurological Disorders and...CompletedFabry DiseaseUnited States
-
National Institute of Neurological Disorders and...Completed
-
National Institute of Neurological Disorders and...CompletedHealthy | Fabry Disease | Cerebrovascular AccidentUnited States
-
National Institute of Neurological Disorders and...Completed
-
National Institute of Mental Health (NIMH)Completed
-
National Institute of Neurological Disorders and...Completed
-
National Institute of Neurological Disorders and...CompletedGaucher's DiseaseUnited States
-
National Institute of Neurological Disorders and...Completed
-
National Institute of Neurological Disorders and...CompletedHealthy | Fabry DiseaseUnited States
-
Assistance Publique - Hôpitaux de ParisUnknown
-
ProtalixCompleted
-
National Center for Research Resources (NCRR)University of PittsburghUnknownGaucher's DiseaseUnited States
-
National Center for Research Resources (NCRR)University of California, Los AngelesCompletedThrombocytopenia | Inborn Errors of Metabolism | Metachromatic Leukodystrophy | Fanconi's Anemia | Thalassemia Major | Pure Red-Cell AplasiaUnited States
-
Fairview University Medical CenterUnknownMucopolysaccharidosis I | Niemann-Pick Disease | Mucopolysaccharidosis VI | Wolman Disease | Adrenoleukodystrophy | Metachromatic Leukodystrophy | Pulmonary Complications | Fucosidosis | Globoid Cell Leukodystrophy | Gaucher's Disease | Mannosidosis | I Cell DiseaseUnited States
-
National Center for Research Resources (NCRR)Icahn School of Medicine at Mount SinaiCompletedMetabolism, Inborn Errors | Leukodystrophy, Globoid Cell | Tay-Sachs Disease | Porphyria, ErythropoieticUnited States
-
National Center for Research Resources (NCRR)National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); University...Completed