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- US Clinical Trials Registry
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Search clinical trials for: AAV
Total 324 results
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Opus Genetics, IncRecruiting
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St. Jude Children's Research HospitalRecruitingSickle Cell DiseaseUnited States
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BioMarin PharmaceuticalRecruiting
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PfizerRecruitingHemophilia A | Hemophilia BAustralia, United States, Turkey
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Seventh Medical Center of PLA General HospitalGeneCradle Therapeutics, IncRecruiting
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Direction Centrale du Service de Santé des ArméesNot yet recruiting
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Prevail TherapeuticsEli Lilly and CompanyRecruitingGaucher Disease | Gaucher Disease, Type 1United States, Spain, Germany
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Lexeo TherapeuticsRecruitingAlzheimer DiseaseUnited States
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SwanBio Therapeutics, Inc.RecruitingAMN | AMN Gene Mutation | X-ALDNetherlands, United States
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Ultragenyx Pharmaceutical IncRecruitingOTC DeficiencyUnited States, Portugal, Italy, Spain, United Kingdom, Japan, Canada, Germany, France, Argentina, Netherlands, Brazil
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Xiangya Hospital of Central South UniversityThe Third Xiangya Hospital of Central South University; Hunan Provincial People... and other collaboratorsRecruiting
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Weill Medical College of Cornell UniversityNational Heart, Lung, and Blood Institute (NHLBI)RecruitingMyocardial Fibrosis | Cardiomyopathies | Friedreich Ataxia | Cardiac HypertrophyUnited States
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Vrije Universiteit BrusselUniversitair Ziekenhuis Brussel; Revalidatieziekenhuis InkendaaINot yet recruitingStroke | COVID-19 | Muscle Weakness | Frailty | SarcopeniaBelgium
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UniQure Biopharma B.V.RecruitingHuntington DiseasePoland, United Kingdom, Germany
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Institute of Hematology & Blood Diseases HospitalRecruiting
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University College, LondonRecruitingOrnithine Transcarbamylase DeficiencyUnited Kingdom
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Northwestern UniversityRecruiting
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Mark TuszynskiOhio State UniversityRecruitingMild Cognitive Impairment | Alzheimer's DiseaseUnited States
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Aspa TherapeuticsRecruitingCanavan DiseaseUnited States
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W. Michael HootenNational Institute on Drug Abuse (NIDA)Recruiting
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Beacon TherapeuticsRecruitingX-Linked Retinitis PigmentosaUnited States
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Adrenas Therapeutics IncRecruitingCongenital Adrenal HyperplasiaUnited States
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Passage Bio, Inc.RecruitingFrontotemporal Dementia | FTD | Dementia Frontotemporal | FTD-GRNUnited States, Brazil, Italy, Portugal, Canada
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BioMarin PharmaceuticalRecruitingHemophilia A With Inhibitor | Hemophilia A With Anti Factor VIIIUnited States, United Kingdom, Taiwan, Israel, Korea, Republic of, South Africa, Brazil, Italy, Germany
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Brain Neurotherapy Bio, Inc.Recruiting
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PfizerRecruitingHousehold ContactsUnited States
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AbbVieAbbVieRecruitingNeovascular Age-Related Macular Degeneration (nAMD)United States
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University College Hospital GalwayStewart R Walsh; Wael Tawfick; Thomas A Aherne; Mark Twyford; Marie O'ShaughnessyRecruiting
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Prevail TherapeuticsEli Lilly and CompanyRecruitingFrontotemporal DementiaUnited States, Australia, Belgium, Spain, United Kingdom, France
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Tianjin Anding HospitalRecruitingBPSD | Amisulpride | Olanzapine | Dementia of the Alzheimer TypeChina
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Prevail TherapeuticsEli Lilly and CompanyRecruitingParkinson DiseaseUnited States, Israel
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Aspa TherapeuticsRecruiting
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UniQure Biopharma B.V.RecruitingHuntington's DiseaseUnited States
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Brigham and Women's HospitalUnited States Department of Defense; Massachusetts Institute of Technology; Walter...Recruiting
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National Human Genome Research Institute (NHGRI)Sio Gene TherapiesRecruitingGangliosidosis | Lysosomal Diseases | GM1United States
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eyeDNA TherapeuticsRecruitingRetinitis PigmentosaFrance
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GenSight BiologicsRecruitingNon-syndromic Retinitis PigmentosaUnited States, France, United Kingdom
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University College, LondonMedical Research CouncilRecruiting
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Krzysztof BankiewiczNational Institute of Neurological Disorders and Stroke (NINDS); University...Recruiting
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Shirley Ryan AbilityLabCoapt, LLCActive, not recruitingLower Limb Amputation Below Knee (Injury) | Lower Limb Amputation Above Knee (Injury) | Amputation | Phantom Limb Pain | Phantom Pain | Phantom Sensation | Lower Limb Amputation Knee | Lower Limb Amputation at Ankle (Injury) | Upper Limb Amputation at the Hand | Upper Limb Amputation at the Wrist | Upper... and other conditionsUnited States
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Janssen Research & Development, LLCJanssen Research & Development, LLCActive, not recruitingX-Linked Retinitis PigmentosaBelgium, Canada, United States, Israel, United Kingdom, Denmark, France, Italy, Netherlands, Switzerland, Spain
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Janssen Research & Development, LLCJanssen Research & Development, LLCActive, not recruitingX-Linked Retinitis PigmentosaUnited States, Canada, Israel, United Kingdom, Denmark, France, Belgium, Italy, Netherlands, Switzerland, Spain
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PfizerActive, not recruiting
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Zuyderland Medisch CentrumCompletedBreast CancerNetherlands
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NightstaRx Ltd, a Biogen CompanyEnrolling by invitationChoroideremia | X-Linked Retinitis PigmentosaUnited States, United Kingdom, Netherlands, Germany, France, Brazil, Canada, Denmark, Finland
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BayerUltragenix pharmaceuticalActive, not recruitingHemophilia ANetherlands, United States, Germany, United Kingdom, France, Bulgaria
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Forge Biologics, IncActive, not recruiting
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Janssen Research & Development, LLCActive, not recruitingX-Linked Retinitis PigmentosaUnited States, United Kingdom
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CSL BehringEnrolling by invitation
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Novo Nordisk A/SEnrolling by invitationDiabetes Mellitus, Type 2Finland, France