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Search clinical trials for: AAV vector
Total 3144 results
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University of Massachusetts, WorcesterNational Heart, Lung, and Blood Institute (NHLBI); University of Florida; National... and other collaboratorsCompletedAlpha 1-Antitrypsin DeficiencyUnited States
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Neurocrine BiosciencesOregon Health and Science University; University of California, San Francisco; Veristat, Inc... and other collaboratorsCompletedParkinson's DiseaseUnited States
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GenSight BiologicsCompletedOptic, Atrophy, Hereditary, LeberUnited Kingdom, United States, Germany, Italy, France
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Applied Genetic Technologies CorpNational Heart, Lung, and Blood Institute (NHLBI)CompletedAlpha-1 Antitrypsin DeficiencyUnited States, Ireland
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Spark TherapeuticsChildren's Hospital of Philadelphia; University of Pittsburgh; St. James's Hospital... and other collaboratorsTerminated
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St. Jude Children's Research HospitalNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Assisi...CompletedGalactosialidosisUnited States
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Tacere Therapeutics, Inc.TerminatedHepatitis CUnited States
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International AIDS Vaccine InitiativeNational Institute of Allergy and Infectious Diseases (NIAID); Children's Hospital...Unknown
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Applied Genetic Technologies CorpOregon Health and Science University; University of Massachusetts, WorcesterCompletedLeber Congenital AmaurosisUnited States
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National Institute of Diabetes and Digestive and...University of FloridaCompleted
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Tacere Therapeutics, Inc.CompletedHepatitis CUnited States
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Digna Biotech S.L.University of Navarra; Porphyria Centre Sweden; UniQure N.V.; Nationales Centrum...CompletedAcute Intermittent PorphyriaSpain
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Amsterdam Molecular TherapeuticsInternational Antiviral Therapy Evaluation CenterUnknownFamilial Lipoprotein Lipase DeficiencyCanada
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Amsterdam Molecular TherapeuticsThe Clinical Trial CompanyCompletedFamilial Lipoprotein Lipase DeficiencyCanada
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GenethonCompletedLimb Girdle Muscular Dystrophy Type 2C | Gamma-sarcoglycanopathyFrance
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Targeted Genetics CorporationCompletedArthritis, Rheumatoid | Arthritis, Psoriatic | Ankylosing SpondylitisUnited States
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National Institute of Allergy and Infectious Diseases...National Institutes of Health (NIH); University of WashingtonNot yet recruiting
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The Affiliated Nanjing Drum Tower Hospital of Nanjing...Not yet recruitingSystemic Lupus Erythematosus (SLE) | ANCA Associated Vasculitis (AAV) | Idiopathic Inflammatory Myopathy (IIM)China
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Canadian Blood ServicesNot yet recruitingBabesioses, Human
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National Institute of Allergy and Infectious Diseases...National Institutes of Health (NIH); University of Washington; Harvard School... and other collaboratorsNot yet recruiting
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BiocodexNot yet recruiting
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The University of Texas Health Science Center,...Not yet recruitingCerebellar AtaxiaUnited States
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Shanghai Vitalgen BioPharma Co., Ltd.Not yet recruitingAromatic L-amino Acid Decarboxylase Deficiency
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Hookipa Biotech GmbHNot yet recruitingHuman Immunodeficiency Virus (HIV) InfectionUnited States
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Kamuzu University of Health SciencesBoston University; Michigan State University; Ministry of Health, MalawiNot yet recruiting
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Mahidol UniversityNot yet recruitingVaccine Hesitancy
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BayerRecruitingSoil-transmitted Helminth Infection | Onchocerciasis (River Blindness)Germany
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Radboud University Medical CenterLondon School of Hygiene and Tropical Medicine; Malaria Research and Training...Not yet recruiting
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Bill & Melinda Gates Medical Research InstituteNot yet recruitingHealthy VolunteersKenya, Uganda
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Children's National Research InstituteSteven & Alexandra Cohen Foundation; Clinical Trials Network for Lyme and Other...RecruitingPregnancy Complications | Parenting | Tick-Borne Diseases | Lyme Disease | Chronic Lyme Disease | Tick-Borne Infections | Post Treatment Lyme DiseaseUnited States
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Essen BiotechNot yet recruitingSickle Cell Disease | Sickle-Cell Disease With CrisisChina
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Rigshospitalet, DenmarkRecruitingBorrelia Burgdorferi NeuroborreliosisDenmark
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TakedaNot yet recruiting
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Liaoning Chengda Biotechnology CO., LTDRecruitingJapanese EncephalitisChina
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IRCCS Sacro Cuore Don Calabria di NegrarRecruitingTick-Borne DiseasesItaly
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Technophage, SAVectorB2BNot yet recruitingPneumonia, Ventilator-AssociatedFrance
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Drugs for Neglected DiseasesInstitute of Tropical Medicine, Belgium; Institut National de Recherche Biomédicale... and other collaboratorsNot yet recruitingHuman African Trypanosomiasis
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Infectious Diseases Research Collaboration, UgandaLondon School of Hygiene and Tropical Medicine; Radboud University Medical...Not yet recruiting
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Evandro Chagas Institute of Clinical ResearchNot yet recruitingChronic Chagas DiseaseBrazil
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Malaria ConsortiumNot yet recruitingMalaria,Falciparum | Chemoprevention
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Valneva Austria GmbHRecruitingZika | Zika Virus InfectionUnited States
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Liaoning Chengda Biotechnology CO., LTDRecruitingJapanese Encephalitis | Measles | Rubella | MumpsChina
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Theravectys S.A.Not yet recruitingHPV-Related Cervical Carcinoma | HPV Positive Oropharyngeal Squamous Cell CarcinomaUnited States
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University of OxfordBill and Melinda Gates Foundation; University Hospitals Bristol and Weston...RecruitingMalaria,FalciparumUnited Kingdom
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IRCCS Sacro Cuore Don Calabria di NegrarRecruiting
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Lantu BiopharmaNot yet recruitingBeta-Thalassemia
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IRCCS Sacro Cuore Don Calabria di NegrarRecruiting