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Search clinical trials for: Gain of function STAT1 defects
Total 434686 results
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Guy's and St Thomas' NHS Foundation TrustRecruitingNeurofibromatosis Type 1United Kingdom
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Government College University FaisalabadRecruitingQuality of Life | Parenting | Congenital Heart Disease | Psychological Intervention | Psychological DisturbancePakistan
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Shanghai 10th People's HospitalRecruitingHeart Failure | Atrial FibrillationChina
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Sohag UniversityNot yet recruitingValue of Thyroid Functions in Children With Congenital Heart DiseasesEgypt
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Fatebenefratelli HospitalMayo Clinic; University of Pisa; Universita di Verona; Careggi Hospital; University... and other collaboratorsRecruitingCoronary Artery Disease | Heart Failure | Heart Transplantation | Congenital Heart Disease | Valvular Heart Disease | Hypertrophic Cardiomyopathy | Post-chest Radio/ChemiotherapyItaly
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Sohag UniversityRecruitingEyelid Defects | Periocular TumorsEgypt
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Eunice Kennedy Shriver National Institute of Child...RecruitingTurner Syndrome | Galactosemia | Ovarian Disfunction | Post-menarcheal Adolescents | Variations in Sex Characteristics | Differences in Sex DevelopmentUnited States
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University of FloridaRecruitingCoronary Artery DiseaseUnited States
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University Hospital, ToulouseRecruiting
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University of MichiganRecruitingObesity | Metabolic Syndrome | Insulin Resistance | Weight Loss | Weight Gain | Metabolic DiseaseUnited States
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Instituto do Cancer do Estado de São PauloRecruiting
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Abiomed Inc.RecruitingCoronary Artery Disease | Left Ventricular DysfunctionUnited States, Switzerland, Germany, Canada, Italy, Netherlands, United Kingdom
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dr. Laura C. G. de Graaff-HerderRecruitingDisorders of Sex Development | Congenital Adrenal Hyperplasia | Tuberous Sclerosis | Kallmann Syndrome | Prader-Willi Syndrome | Neurofibromatosis | Rett Syndrome | 22q11 Deletion Syndrome | Turner Syndrome | Noonan Syndrome | Allan-Herndon-Dudley Syndrome | Saethre-Chotzen Syndrome | Congenital Hypopituitarism | Cornelia... and other conditionsNetherlands
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Merck Sharp & Dohme LLCEisai Inc.RecruitingSquamous Cell Carcinoma of Head and NeckUnited States, Australia, Canada, Denmark, France, Israel, Korea, Republic of, Norway, Portugal, Romania, Spain, Taiwan, United Kingdom, Colombia, Brazil
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Children's Hospital Medical Center, CincinnatiRecruitingNeurofibromatosis 1 | Noonan Syndrome | Legius Syndrome | Cardiofaciocutaneous Syndrome | Costello Syndrome | SYNGAP1-Related Intellectual Disability | DLG4 | RAS Mutation | Noonan Syndrome With Multiple Lentigines | Noonan Neurofibromatosis Syndrome | Smith-Kingsmore Syndrome | MTOR Gene Mutation | GATOR-1 Gene... and other conditionsUnited States
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University of FloridaU.S. Army Medical Research and Development CommandRecruitingDuchenne Muscular Dystrophy (DMD)United States
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dr. M.J.N.L. BendersUniversity Medical Center Groningen; Erasmus Medical Center; ZonMw: The Netherlands... and other collaboratorsRecruitingCongenital Heart Disease in Children | NeuroprotectionNetherlands
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University of South FloridaNational Institute on Aging (NIA); University of Florida; University of California... and other collaboratorsRecruitingDementia | Mild Cognitive Impairment | Age-related Cognitive DeclineUnited States
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University of FloridaRecruiting
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Columbia UniversityNational Heart, Lung, and Blood Institute (NHLBI)RecruitingCongenital Heart DiseaseUnited States, Colombia
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Edwards LifesciencesRecruitingMitral Regurgitation | Mitral Insufficiency | Functional Mitral Regurgitation | Degenerative Mitral Valve DiseaseUnited States, Canada, Switzerland, Germany
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United TherapeuticsRecruitingCardiovascular Diseases | Vascular Diseases | Lung Diseases | Hypertension | Connective Tissue Diseases | Pulmonary Arterial Hypertension | Familial Primary Pulmonary Hypertension | Hypertension, Pulmonary | Pulmonary Hypertension | PAH | Respiratory Tract DiseaseUnited States, Australia, Austria, Italy, Taiwan, Spain, Korea, Republic of, Canada, United Kingdom, Singapore, Argentina, Germany, France, Belgium, Mexico, Brazil, Hungary, Bulgaria, Chile, Czechia, Denmark, Greece, Israel, Netherlands, Pola... and more
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Assiut UniversityRecruitingTetralogy of FallotEgypt
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Abbott Medical DevicesRecruitingCardiovascular Diseases | Heart Valve Diseases | Mitral Regurgitation | Mitral Valve Insufficiency | Valve Disease, Heart | Mitral Insufficiency | Functional Mitral Regurgitation | Degenerative Mitral Valve DiseaseUnited States, Canada
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Abbott Medical DevicesRecruitingStroke | Patent Foramen OvaleUnited States, Germany, Canada, Switzerland, Italy, Portugal, United Kingdom
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Vertos Medical, Inc.RecruitingLumbar Spinal StenosisUnited States
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Children's Oncology GroupNational Cancer Institute (NCI)RecruitingMalignant Germ Cell Tumor | Germ Cell Tumor | Childhood Extracranial Germ Cell Tumor | Extragonadal Embryonal Carcinoma | Malignant Ovarian Teratoma | Stage I Ovarian Choriocarcinoma | Stage I Ovarian Embryonal Carcinoma AJCC v6 and v7 | Stage I Ovarian Teratoma AJCC v6 and v7 | Stage I Ovarian Yolk... and other conditionsUnited States, Canada, Australia, Puerto Rico, New Zealand, Saudi Arabia, United Kingdom, India, Japan
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Fatebenefratelli HospitalFederico II University; Federal University of Rio Grande do Sul; Royal Brompton... and other collaboratorsRecruitingCoronary Artery Disease | Heart Failure | Aortic Valve Disease | Pulmonary Arterial Hypertension | Tetralogy of Fallot | Hypertrophic Cardiomyopathy | Athletes HeartItaly
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St. Jude Children's Research HospitalRecruitingPancreatic Cancer | Hodgkin Lymphoma | Lynch Syndrome | Tuberous Sclerosis | Fanconi Anemia | AML | Non Hodgkin Lymphoma | Familial Adenomatous Polyposis | Acute Leukemia | Nevoid Basal Cell Carcinoma Syndrome | Neurofibromatosis Type 1 | Neuroblastoma | Retinoblastoma | MDS | Rhabdomyosarcoma | Von Hippel-Lindau Disease | Adrenocortical Carcinoma and other conditionsUnited States
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Children's Hospital Medical Center, CincinnatiRecruitingHypoplastic Left Heart Syndrome (HLHS)United States, United Kingdom, Canada
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Metcela Inc.RecruitingHypoplastic Left Heart Syndrome | Single VentricleJapan
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University of FloridaRecruitingAlpha-1 Antitrypsin Deficiency | Cystic Fibrosis (CF) | AATD | AAT DeficiencyUnited States
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Sanford HealthNational Ataxia Foundation; Beyond Batten Disease Foundation; Pitt Hopkins Research... and other collaboratorsRecruitingMitochondrial Diseases | Retinitis Pigmentosa | Myasthenia Gravis | Eosinophilic Gastroenteritis | Multiple System Atrophy | Leiomyosarcoma | Leukodystrophy | Anal Fistula | Spinocerebellar Ataxia Type 3 | Friedreich Ataxia | Kennedy Disease | Lyme Disease | Hemophagocytic Lymphohistiocytosis | Spinocerebellar Ataxia... and other conditionsUnited States, Australia
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Center for International Blood and Marrow Transplant...National Marrow Donor ProgramRecruitingAutoimmune Diseases | Hodgkin Lymphoma | Hematologic Malignancies | Acute Lymphoblastic Leukemia (ALL) | Non-hodgkin Lymphoma | Severe Aplastic Anemia | Inherited Disorders of Metabolism | Inherited Abnormalities of Platelets | Histiocytic Disorders | Acute Myelogenous Leukemia (AML or ANLL) | Other Acute... and other conditionsUnited States
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University of FloridaBioMarin PharmaceuticalCompleted
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National Cancer Institute (NCI)Active, not recruitingNeurofibromatosis 1 | Neurofibroma, Plexiform | Neurofibromatosis Type 1 | NF1United States
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University of FloridaCompletedHeart FailureUnited States
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University of PittsburghNational Institutes of Health (NIH); National Institute on Aging (NIA)CompletedHealthy | Cognitive Function 1, SocialUnited States
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Boehringer IngelheimActive, not recruitingIdiopathic Pulmonary FibrosisUnited States, Spain, China, Canada, Norway, Korea, Republic of, Taiwan, Belgium, Australia, Germany, Denmark, Singapore, Thailand, Italy, Japan, United Kingdom, Switzerland, Croatia, France, Netherlands, Malaysia, New Zealand, Arge... and more
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Boehringer IngelheimActive, not recruitingLung Diseases, InterstitialUnited States, Spain, China, United Kingdom, Canada, Norway, Korea, Republic of, Belgium, Australia, Germany, Denmark, Singapore, Taiwan, Thailand, Italy, Japan, Finland, Turkey, Croatia, Switzerland, France, Serbia, Netherlands, Mala... and more
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisUnited States, Spain, United Kingdom, New Zealand, Israel, Australia, Ireland, Germany, Sweden, Czechia, Portugal, Hungary
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Universiteit AntwerpenUniversity Hospital, Antwerp; Cliniques universitaires Saint-Luc- Université...CompletedHemophilia A | Hemophilia BBelgium
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University of FloridaEnrolling by invitationCleft Palate | Mouth Abnormalities | Birth DefectUnited States
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United TherapeuticsEnrolling by invitationCardiovascular Diseases | Vascular Diseases | Lung Diseases | Hypertension | Connective Tissue Diseases | Pulmonary Arterial Hypertension | Familial Primary Pulmonary Hypertension | Hypertension, Pulmonary | Pulmonary Hypertension | PAH | Respiratory Tract DiseaseUnited States, Spain, Australia, Taiwan, Canada, Singapore, United Kingdom, Italy, Germany, China, Mexico, Argentina, Korea, Republic of, Austria, Greece, Sweden, Portugal, Belgium, Brazil, Bulgaria, Chile, Croatia, Czechia, Denmark, Fr... and more
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National Cancer Institute (NCI)NRG OncologyActive, not recruitingPancreatic Adenocarcinoma | Pancreatic Ductal Adenocarcinoma | Pancreatic Intraductal Papillary-Mucinous Neoplasm | Stage I Pancreatic Cancer AJCC v6 and v7 | Stage II Pancreatic Cancer AJCC v6 and v7United States, Canada, Israel, Belgium
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National Cancer Institute (NCI)Active, not recruitingMalignant Glioma | Recurrent Childhood Ependymoma | Rhabdoid Tumor | Advanced Malignant Solid Neoplasm | Refractory Malignant Solid Neoplasm | Recurrent Hepatoblastoma | Recurrent Langerhans Cell Histiocytosis | Recurrent Malignant Solid Neoplasm | Recurrent Medulloblastoma | Recurrent Neuroblastoma | Recurrent... and other conditionsUnited States, Puerto Rico
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National Cancer Institute (NCI)Active, not recruitingMale Breast Carcinoma | Stage IIA Breast Cancer AJCC v6 and v7 | Stage IIB Breast Cancer AJCC v6 and v7 | Stage IIIA Breast Cancer AJCC v7 | Stage IIIB Breast Cancer AJCC v7 | Stage IIIC Breast Cancer AJCC v7United States, Puerto Rico
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National Cancer Institute (NCI)NRG OncologyActive, not recruitingRecurrent Fallopian Tube Carcinoma | Recurrent Ovarian Carcinoma | Stage IA Fallopian Tube Cancer AJCC v6 and v7 | Stage IA Ovarian Cancer AJCC v6 and v7 | Stage IB Fallopian Tube Cancer AJCC v6 and v7 | Stage IB Ovarian Cancer AJCC v6 and v7 | Stage IC Fallopian Tube Cancer AJCC v6 and v7 | Stage... and other conditionsUnited States
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KU LeuvenCompletedCongenital Heart DiseaseBotswana, United States, Korea, Republic of, Belgium, Sweden, France, Switzerland, Denmark, Pakistan, Norway, Taiwan, Malta, Brazil, Bulgaria, India, Austria, Argentina, Australia, Cameroon, Canada, Chile, Colombia, Ethiopia, Greece, Italy and more
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University of FloridaTerminatedFrailty | Spinal Fusion | Prehabilitation | Lumbar Spine Injury | Nutritional Supplementation | Functional OutcomeUnited States