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Search clinical trials for: Mitochondrial depletion syndrome
Total 38153 results
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University of Kansas Medical CenterIn8bio Inc.RecruitingAcute Myeloid Leukemia | Myelodysplastic Syndromes | Acute Lymphoblastic Leukemia | Chronic Myeloid LeukemiaUnited States
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The University of Texas Health Science Center,...RecruitingLeigh Disease | Leigh Syndrome | Leigh's Necrotizing Encephalopathy | Subacute Necrotizing Encephalomyopathy | Subacute Necrotizing EncephalomyelopathyUnited States
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Children's Hospital of PhiladelphiaRecruitingParoxysmal Nocturnal Hemoglobinuria | Acquired Aplastic Anemia | Inherited Bone Marrow Failure SyndromesUnited States
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University Hospital, Strasbourg, FranceRecruiting
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MD Stem CellsRecruitingGlaucoma | Age-Related Macular Degeneration | Macular Degeneration | Retinitis Pigmentosa | Leber Hereditary Optic Neuropathy | Optic Atrophy | Blindness | Optic Neuropathy | Vision, Low | Retinal Disease | Stargardt Disease | Maculopathy | Retinopathy | Optic Nerve Disease | Nonarteritic Ischemic Optic Neuropathy | Vision... and other conditionsUnited States, United Arab Emirates
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Children's Hospital of PhiladelphiaUniversity of California, San FranciscoRecruitingImmunodeficiencies | Immune Dysregulation SyndromesUnited States
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Foundation Fighting BlindnessRecruitingRetinitis Pigmentosa | Choroideremia | Usher Syndrome | Batten Disease | Leber Congenital Amaurosis | Goldmann-Favre Syndrome | Kearns-Sayre Syndrome | Retinal Disease | Bardet-Biedl Syndrome | Stargardt Disease | Cone Dystrophy | Retinoschisis | Achromatopsia | Gyrate Atrophy | Eye Diseases Hereditary | Bassen-Kornzweig... and other conditionsUnited States
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Children's Hospital of PhiladelphiaRecruitingLeukemia | Bone Marrow Failure Syndromes | Immunodeficiencies | Inborn Errors of Metabolism | Immunodysregulation Polyendocrinopathy Enteropathy X-linked SyndromeUnited States
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Children's Hospital of PhiladelphiaRecruitingLymphoma | Leukemia | MyelodysplasiaUnited States
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Masonic Cancer Center, University of MinnesotaRecruitingHurler Syndrome | Sphingolipidoses | Peroxisomal Disorders | Metachromatic Leukodystrophy | Alpha-Mannosidosis | Hunter Syndrome | Mucopolysaccharidosis Disorders | Maroteaux Lamy Syndrome | Sly Syndrome | Fucosidosis | Aspartylglucosaminuria | Glycoprotein Metabolic Disorders | Recessive Leukodystrophies | Globoid... and other conditionsUnited States
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Sanford HealthNational Ataxia Foundation; Beyond Batten Disease Foundation; Pitt Hopkins Research... and other collaboratorsRecruitingMitochondrial Diseases | Retinitis Pigmentosa | Myasthenia Gravis | Eosinophilic Gastroenteritis | Multiple System Atrophy | Leiomyosarcoma | Leukodystrophy | Anal Fistula | Spinocerebellar Ataxia Type 3 | Friedreich Ataxia | Kennedy Disease | Lyme Disease | Hemophagocytic Lymphohistiocytosis | Spinocerebellar Ataxia... and other conditionsUnited States, Australia
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Duke UniversityWithdrawnCOVID-19 Acute Respiratory Distress SyndromeUnited States
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Khondrion BVJulius Clinical; ProPharma Group; Europees Fonds voor Regionale Ontwikkeling... and other collaboratorsActive, not recruitingMitochondrial Diseases | MELAS | Mitochondrial DNA tRNALeu(UUR) m.3243A<G Mutation | Subacute Necrotizing EncephalomyelopathyNetherlands
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Massachusetts Eye and Ear InfirmaryNational Eye Institute (NEI)Active, not recruitingStroke | Myasthenia Gravis | Traumatic Brain Injury | Chronic Progressive External Ophthalmoplegia | Ptosis, Eyelid | BlepharoptosisUnited States
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University College, LondonCancer Research UK; Cancer Research UK & UCL Cancer Trials CentreCompleted
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University of California, San DiegoDysautonomia InternationalActive, not recruitingPostural Tachycardia SyndromeUnited States
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PTC TherapeuticsEnrolling by invitationInherited Mitochondrial DiseaseUnited States, France, Spain, United Kingdom, Italy, Poland, Japan
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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Hoffmann-La RochePPD; Laboratory Corporation of America; Illingworth Research GroupActive, not recruitingMultiple Sclerosis | Clinically Isolated SyndromeUnited States, Spain, Switzerland, France, Germany
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute...CompletedRecurrent Adult Acute Myeloid Leukemia | Adult Acute Myeloid Leukemia in Remission | Childhood Acute Myeloid Leukemia in Remission | Adult Acute Lymphoblastic Leukemia in Remission | Childhood Acute Lymphoblastic Leukemia in Remission | Recurrent Adult Acute Lymphoblastic Leukemia | Recurrent... and other conditionsUnited States
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PTC TherapeuticsCompletedMitochondrial Diseases | Drug Resistant Epilepsy | Leigh Disease | Leigh Syndrome | Mitochondrial Encephalopathy (MELAS) | Pontocerebellar Hypoplasia Type 6 (PCH6) | Alpers Disease | Alpers SyndromeUnited States, Spain, United Kingdom, Canada, France, Italy, Poland, Sweden, Japan
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Khondrion BVJulius Clinical; ProPharma Group; CertaraCompletedMitochondrial Diseases | Mitochondrial DNA tRNALeu(UUR) m.3243A<G Mutation | Maternally Inherited Diabetes and Deafness (MIDD) | Mitochondrial Encephalomyopathy, Lactic Acidosis and Stroke Like Episodes (MELAS) | Chronic Progressive External Ophthalmoplegia (CPEO)Netherlands, Denmark, United Kingdom, Germany
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Haukeland University HospitalTerminatedChronic Fatigue Syndrome | Myalgic EncephalomyelitisNorway
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Celia BañulsInstituto de Salud Carlos IIIActive, not recruiting
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Wake Forest University Health SciencesNational Cancer Institute (NCI)CompletedPeripheral T-cell Lymphoma | Anaplastic Large Cell Lymphoma | Angioimmunoblastic T-cell Lymphoma | Adult Nasal Type Extranodal NK/T-cell Lymphoma | Hepatosplenic T-cell Lymphoma | Recurrent Adult Acute Lymphoblastic Leukemia | Recurrent Adult Hodgkin Lymphoma | Recurrent Adult T-cell Leukemia/Lymphoma and other conditionsUnited States
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute...Active, not recruitingLymphoblastic Lymphoma | Childhood Acute Myeloid Leukemia in Remission | Recurrent Acute Myeloid Leukemia | Refractory Acute Myeloid Leukemia | Myelodysplastic Syndrome With Excess Blasts | Childhood Acute Lymphoblastic Leukemia in Remission | Recurrent Childhood Acute Lymphoblastic Leukemia | Recurrent... and other conditionsUnited States
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PTC TherapeuticsNo longer available
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Children's Hospital of PhiladelphiaCompletedImmunodeficienciesUnited States
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Children's Hospital of PhiladelphiaAvailableLeukemia | Immunodeficiencies | Bone Marrow Failure SyndromeUnited States
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Stealth BioTherapeutics Inc.Active, not recruitingMitochondrial Diseases | Mitochondrial Myopathies | Mitochondrial Complex I Deficiency | Mitochondrial Pathology | Mitochondrial DNA Depletion | Mitochondrial DNA Mutation | Mitochondrial DNA Deletion | Mitochondrial Metabolism DefectSpain, United States, Italy, Netherlands, Australia, Germany, Hungary, New Zealand, Norway, United Kingdom
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PTC TherapeuticsCompletedLeigh SyndromeUnited States
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University of ArkansasThe University of Texas Health Science Center at San Antonio; Jane Botsford... and other collaboratorsActive, not recruitingAutism Spectrum Disorder | Mitochondrial Disease | Developmental Delay | AutismUnited States
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Tisento TherapeuticsChildren's Hospital of PhiladelphiaTerminated
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Centre Hospitalier Universitaire DijonTerminatedLung Diseases | Mechanical Ventilation | Bronchoalveolar LavageFrance
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Hospital Universitario 12 de OctubreActive, not recruiting
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Nationwide Children's HospitalActive, not recruitingHematologic Malignancy | MyelodysplasiaUnited States
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The University of QueenslandNational Health and Medical Research Council, AustraliaCompletedAtaxia TelangiectasiaAustralia
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Yale UniversityGenentech, Inc.TerminatedMultiple Sclerosis | Radiologically Isolated SyndromeUnited States
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St. Jude Children's Research HospitalActive, not recruitingSevere Combined ImmunodeficiencyUnited States
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Laval UniversityCompletedPulmonary Artery HypertensionCanada
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University of California, San DiegoNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Salk...Active, not recruitingMetabolic Syndrome | Pre-DiabetesUnited States
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University of California, San DiegoCompletedGulf War Syndrome | Persian Gulf Syndrome | Mitochondrial DisordersUnited States
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Stealth BioTherapeutics Inc.AvailableMitochondrial Diseases | Barth Syndrome
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Federal Research Institute of Pediatric Hematology...CompletedLymphoma | Myelodysplastic Syndromes | Leukemia | Opportunistic Infections | GvHD | Graft-versus-Host DiseaseRussian Federation
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Weill Medical College of Cornell UniversityNational Heart, Lung, and Blood Institute (NHLBI); New York Presbyterian Hospital and other collaboratorsCompletedSepsis | Septic Shock | Severe Sepsis | Infection | Sepsis SyndromeUnited States
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Burke Medical Research InstituteActive, not recruitingStroke | Multiple Sclerosis | Cerebral Palsy | Parkinson Disease | Spinal Cord Injuries | Neurologic Disorder | Hemiplegia | Hemiparesis | Friedreich Ataxia | Trauma, Brain | Transverse MyelitisUnited States
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Khondrion BVJulius ClinicalCompletedMitochondrial Diseases | Mitochondrial Myopathies | MELAS Syndrome | Mitochondrial Encephalomyopathies | MIDDNetherlands, Denmark, Germany, United Kingdom
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Taysha Gene Therapies, Inc.Withdrawn
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University of California, Los AngelesGilead SciencesCompletedHIV/AIDS | Mitochondrial Alteration | Antiviral Toxicity | Antiviral Drug Adverse ReactionUnited States
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Wake Forest University Health SciencesTerminatedAcute Myeloid Leukemia | Acute Lymphoblastic Leukemia | Chronic Myeloid Leukemia | Myelodysplastic Syndrome | Immune Deficiency | Lymphomas | Bone Marrow Failure | Osteopetrosis | HemoglobinopathyUnited States