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Search clinical trials for: PAH Deficiency
Total 19565 results
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Wake Forest University Health SciencesCompletedNausea | Vitamin D Deficiency | Orthostatic IntoleranceUnited States
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National Cancer Institute (NCI)CompletedHIV Infection | Advanced Malignant Solid Neoplasm | Recurrent Malignant Solid Neoplasm | Metastatic Malignant Solid Neoplasm | Unresectable Solid NeoplasmUnited States
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Joanne Kurtzberg, MDDuke University; Miltenyi Biotec, Inc.AvailableHematologic Malignancies | Immune Deficiencies | Inborn Errors of Metabolism DisordersUnited States
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National Cancer Institute (NCI)WithdrawnHematopoietic and Lymphoid Cell Neoplasm | Lynch Syndrome | Refractory Lymphoma | Refractory Malignant Solid Neoplasm | Recurrent Lymphoma | Recurrent Malignant Solid Neoplasm | Recurrent Neuroblastoma | Refractory Neuroblastoma | Recurrent Primary Central Nervous System Neoplasm | Refractory Primary Central... and other conditionsUnited States, Canada
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Bellicum PharmaceuticalsActive, not recruitingStudy of Gene Modified Donor T-cells Following TCR Alpha Beta Positive Depleted Stem Cell TransplantLymphoma, Non-Hodgkin | Myelodysplastic Syndromes | Acute Lymphoblastic Leukemia | Anemia, Aplastic | Primary Immune Deficiency Disorder | Cytopenia | Osteopetrosis | Leukemia, Acute Myeloid (AML), Child | Hemoglobinopathy in ChildrenUnited States
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Homology Medicines, IncEnrolling by invitationPhenylketonuria | PAH DeficiencyUnited States
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Centre Leon BerardWithdrawnMyelodysplastic Syndromes | Severe Combined Immunodeficiency | Acute Leukemia | Haematological Malignancy | Hemoglobinopathy in Children | Bone Marrow AplasiaFrance
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AIO-Studien-gGmbHProf. Hartmut Link; MMF GmbH; AIO AG Supportivtherapie; AGSMO (Arbeitsgemeinschaft...CompletedSolid Tumor | Anemia, Iron Deficiency | Malignant LymphomaGermany
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M.D. Anderson Cancer CenterThe University of Texas Health Science Center, Houston; Baylor College of MedicineCompletedHuman Immunodeficiency Virus | Malignant Neoplasms of Mesothelial and Soft TissueUnited States
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Incyte CorporationCompletedMelanoma | Renal Cell Carcinoma | Cervical Cancer | Stomach Cancer | Small Cell Lung Cancer | Hepatocellular Carcinoma | Gastric Cancer | Esophageal Cancer | Ovarian Cancer | NSCLC | Mesothelioma | Squamous Cell Carcinoma of the Head and Neck | Non-small Cell Lung Cancer | Gastroesophageal Junction Cancer | Urothelial... and other conditionsUnited States
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National Institute of Allergy and Infectious Diseases...Completed
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BioMarin PharmaceuticalActive, not recruiting
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University of California, San FranciscoCompletedSickle Cell Disease | Hemoglobinopathies | Thalassemia | Hematologic Malignancies | Immunodeficiencies | Fanconi's Anemia | Nonmalignant Diseases | Genetic Inborn Errors of MetabolismUnited States
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University of California, San FranciscoCompletedSickle Cell Disease | Hemoglobinopathies | Thalassemia | Hematologic Malignancies | Immunodeficiencies | Fanconi's Anemia | Nonmalignant Diseases | Genetic Inborn Errors of MetabolismUnited States
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University of California, San FranciscoThrasher Research FundCompletedSickle Cell Disease | Hemoglobinopathies | Fanconi Anemia | Thalassemia | Hematologic Malignancies | Immunodeficiencies | Nonmalignant Diseases | Genetic Inborn Errors of MetabolismUnited States
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University of EdinburghNHS LothianWithdrawnBronchiectasis | Immunoglobulin Subclass DeficiencyUnited Kingdom
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute... and other collaboratorsCompletedNon-Neoplastic Hematologic and Lymphocytic DisorderUnited States
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National Cancer Institute (NCI)CompletedHematopoietic and Lymphoid Cell Neoplasm | Advanced Lymphoma | Advanced Malignant Solid Neoplasm | Refractory Lymphoma | Refractory Malignant Solid Neoplasm | Refractory Plasma Cell MyelomaUnited States
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Gary Archer Ph.D.National Cancer Institute (NCI)CompletedMalignant Neoplasms BrainUnited States
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Diane GeorgeActive, not recruitingSickle Cell Disease | Hemoglobinopathies | Severe Congenital Neutropenia | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Macrophage Activation Syndrome | Bone Marrow Failure Syndrome | Amegakaryocytic Thrombocytopenia | Schwachman Diamond Syndrome | Primary Immunodeficiency Syndromes | Acquired Immunodeficiency... and other conditionsUnited States
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M.D. Anderson Cancer CenterAmerican Regent, Inc.TerminatedMalignant Neoplasms of Mesothelial and Soft Tissue | Gastrointestinal Stromal Tumor With Neurogenic DifferentiationUnited States
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Assiut UniversityCompletedIron Deficiency Anemia TreatmentEgypt
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Taipei Veterans General Hospital, TaiwanBioMarin PharmaceuticalUnknownPAH Deficiency | Pku Phenylketonuria
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Emory UniversityCompletedSickle Cell Disease | Fanconi Anemia | Hurler Syndrome | Chronic Granulomatous Disease | Severe Congenital Neutropenia | Hemophagocytic Lymphohistiocytosis | Wiskott-Aldrich Syndrome | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Glanzmann Thrombasthenia | Shwachman-Diamond Syndrome | Thalassemia Major | Leukocyte... and other conditionsUnited States
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University of ArkansasWithdrawnPancreatic Neoplasms | Colorectal Neoplasms, Hereditary Nonpolyposis | BRCA1 Gene Mutation | BRCA2 Gene Mutation | Hereditary Pancreatitis | Ataxia Telangiectasia | Peutz-Jegher's Syndrome | Familial Atypical Mole-Malignant Melanoma SyndromeUnited States
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Assiut UniversityUnknownIron Deficiency Anemia of Pregnancy
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Masonic Cancer Center, University of MinnesotaTerminatedHematologic Diseases | Hemophagocytic Lymphohistiocytosis | Immunologic Diseases | Chediak-Higashi Syndrome | X-Linked Lymphoproliferative Disorders | Griscelli Syndrome | Langerhans-Cell HistiocytosisUnited States
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Hamad Medical CorporationCompletedVitamin D Deficiency | AsthmaQatar
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Lucas Otieno Tina, MD MScGlaxoSmithKline; Strathmore UniversityCompletedSickle Cell Disease | Zinc Deficiency | Infection
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Joanne Kurtzberg, MDAldagenCompletedAnemia, Aplastic | MDS | Inborn Errors of Metabolism | Congenital Marrow Failure | Congenital Immunodeficiency SyndromeUnited States
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Galenic Research Institute LtdCompletedPeritoneal Neoplasms | Ascites | Yin Deficiency | Yang DeficiencyChina
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedChronic Myelomonocytic Leukemia | Fanconi Anemia | Childhood Acute Erythroleukemia (M6) | Childhood Acute Megakaryocytic Leukemia (M7) | Childhood Acute Monoblastic Leukemia (M5a) | Childhood Acute Monocytic Leukemia (M5b) | Childhood Acute Myeloblastic Leukemia With Maturation (M2) | Childhood Acute... and other conditionsUnited States
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University of Turin, ItalyCompletedVitamin D Deficiency | Asthma | Disease Exacerbation
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Vejle HospitalCompletedColorectal Cancer | Lynch Syndrome | HNPCCDenmark
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National Institute of Allergy and Infectious Diseases...CompletedHIV InfectionsUnited States
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Duke UniversityCompletedHemoglobinopathies | Thalassemia | Lysosomal Storage Disease | Immunodeficiencies | Inborn Errors of Metabolism | Sickle Cell | Non Malignant Disorders | Congenital Marrow FailuresUnited States
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National Cancer Institute (NCI)CompletedHIV Infection | Clear Cell Renal Cell Carcinoma | Primary Myelofibrosis | Polycythemia Vera | Essential Thrombocythemia | Chronic Myelomonocytic Leukemia | Recurrent Adult Acute Myeloid Leukemia | Extranodal Marginal Zone B-cell Lymphoma of Mucosa-associated Lymphoid Tissue | Nodal Marginal Zone B-cell... and other conditionsUnited States
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Sang-Heon ChoKorean Center for Disease Control and PreventionUnknownAsthma | AgedKorea, Republic of
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Enzon Pharmaceuticals, Inc.National Cancer Institute (NCI)WithdrawnLymphoma | Unspecified Childhood Solid Tumor, Protocol Specific | Myelodysplastic Syndromes | Leukemia | Neutropenia | Infection | Fever, Sweats, and Hot FlashesUnited States
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French National Agency for Research on AIDS and...Merck Sharp & Dohme LLC; Gilead Sciences; Institut de Médecine et d'Epidémiologie...CompletedHIV InfectionsSenegal, Cameroon
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Gilead SciencesCompleted
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National Institute of Nursing Research (NINR)Completed
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Solvay PharmaceuticalsCompletedHIV Infections | Highly Active Antiretroviral Therapy (HAART)-Related Nausea and VomitingUnited States
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University of California, San FranciscoMassachusetts General Hospital; Aga Khan University; University of Utah; Texas... and other collaboratorsCompletedAcquired Immunodeficiency Syndrome | HIVUnited States, Kenya, Puerto Rico, South Africa
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Chiron CorporationCompletedHIV Infections | Cytomegalovirus RetinitisUnited States
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ewimed GmbHLS medcap GmbHNot yet recruitingAscites | Pleural Effusion, Malignant | Pleural Effusion | Ascites, Malignant
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First Affiliated Hospital of Fujian Medical UniversityRecruiting
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First Affiliated Hospital of Fujian Medical UniversityRecruiting
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First Affiliated Hospital of Zhejiang UniversityCSPC Zhongnuo Pharmaceutical (Shijiazhuang) Co., Ltd.RecruitingMyeloid Malignancy | Relapsed/Refractory Acute Myeloid LeukaemiaChina
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University of TennesseeNot yet recruitingNutritional Deficiency | Very Low Birth Weight Infant