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Search clinical trials for: SMA - Spinal Muscular Atrophy
Total 38841 results
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Centre Hospitalier Universitaire de LiegeQueen Fabiola Children's University Hospital; Erasme University Hospital; Centre... and other collaboratorsActive, not recruiting
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Scholar Rock, Inc.Active, not recruitingNeuromuscular Diseases | Neuromuscular Manifestations | Atrophy | Muscular Atrophy | Spinal Muscular Atrophy | Muscular Atrophy, Spinal | Spinal Muscular Atrophy Type 3 | SMA | Spinal Muscular Atrophy Type 2 | Anti-myostatinUnited States, Germany, Belgium, Spain, United Kingdom, Netherlands, France, Italy, Poland
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Hoffmann-La RocheCompletedMuscular Atrophy, SpinalBelgium, United States, China, Spain, Japan, Canada, France, Poland, Brazil, Croatia, Italy, Russian Federation, Turkey, Germany, Serbia, United Kingdom
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Synchron Medical, Inc.Active, not recruitingParalysis | Amyotrophic Lateral Sclerosis | Muscular Dystrophies | Spinal Cord Injuries | Neurologic Disorder | Spinal Muscular Atrophy | Cervical Spinal Cord Injury | Stroke, Lacunar | Paralysis; Stroke | Stroke Brainstem | Tetraplegic; Paralysis | Quadriplegia/TetraplegiaUnited States
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Scholar Rock, Inc.CompletedNeuromuscular Diseases | Neuromuscular Manifestations | Atrophy | Muscular Atrophy | Spinal Muscular Atrophy | Muscular Atrophy, Spinal | Spinal Muscular Atrophy Type 3 | SMA | Spinal Muscular Atrophy Type 2United States, Spain, Italy, Netherlands
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Ohio State UniversityCure SMAActive, not recruitingSpinal Muscular AtrophyUnited States
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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Hospital Israelita Albert EinsteinBiogenActive, not recruitingSpinal Muscular AtrophyBrazil, Argentina, Chile, Colombia, Mexico, Uruguay
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Hadassah Medical OrganizationActive, not recruitingNeurodegenerative DisordersIsrael
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Novartis PharmaceuticalsActive, not recruitingType 2 Spinal Muscular AtrophyUnited States, China, Saudi Arabia, Thailand, Singapore, Brazil, Malaysia, Taiwan, Colombia, Mexico, Denmark, Egypt, India, South Africa, Vietnam
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Novartis Gene TherapiesActive, not recruitingSMA | Spinal Muscular Atrophy Type II | Spinal Muscular Atrophy Type I | Spinal Muscular Atrophy Type IIIUnited States, Belgium, France, Japan, United Kingdom, Italy, Taiwan, Australia, Canada
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Centre Hospitalier Universitaire de NiceActive, not recruitingSpinal Muscular AtrophyFrance
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Columbia UniversityMuscular Dystrophy Association; Stevens Institute of TechnologyCompletedDuchenne Muscular Dystrophy | Spinal Muscular Atrophy Type 3United States
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University of AlbertaWithdrawnHealthy | Amyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Frontotemporal Dementia | Muscular Atrophy, ProgressiveCanada
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BiogenCompletedSpinal Muscular AtrophyGermany
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BiogenCompletedSpinal Muscular AtrophyUnited States, Spain, Germany, United Kingdom, Australia, Japan, Canada, Belgium, France, Hong Kong, Italy, Korea, Republic of, Sweden, Turkey
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Novartis PharmaceuticalsActive, not recruitingSpinal Muscular AtrophyJapan, Belgium, Spain, Canada, United States, Australia, Italy, France, Netherlands
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Novartis PharmaceuticalsCompletedSpinal Muscular AtrophyTaiwan, Belgium, Canada, United States, Australia, France, Italy, Portugal, United Kingdom
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Hospices Civils de LyonCompletedSpinal Muscular AtrophyFrance
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Novartis PharmaceuticalsCompleted
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Catalyst Pharmaceuticals, Inc.TerminatedSpinal Muscular Atrophy Type 3Italy
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University Hospital, Basel, SwitzerlandEnrolling by invitationSpinal Muscular Atrophy Type II | Spinal Muscular Atrophy Type IIISwitzerland
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Biohaven Pharmaceuticals, Inc.Active, not recruitingNeuromuscular Diseases | Spinal Muscular Atrophy | SMAUnited States, Netherlands, United Kingdom, Spain, Czechia, Belgium, Germany, Italy, Poland
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University of UtahAbbott; Leadiant Biosciences, Inc.; Families of Spinal Muscular AtrophyCompletedSpinal Muscular AtrophyUnited States
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Novartis PharmaceuticalsCompletedSpinal Muscular AtrophyBelgium, Germany, Italy, Russian Federation, Poland, Bulgaria, Denmark
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Columbia UniversityThe Spinal Muscular Atrophy FoundationCompleted
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Synchron Medical, Inc.WithdrawnParalysis | Amyotrophic Lateral Sclerosis | Muscular Dystrophies | Neurologic Disorder | Spinal Muscular Atrophy | Spinal Cord Injury | Stroke, Lacunar | Upper Limb Injury | Paralysis; Stroke | Stroke, BrainstemAustralia
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UMC UtrechtPrincess Beatrix Muscle FoundationActive, not recruitingSpinal Muscular AtrophyNetherlands
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University Medical Centre LjubljanaCompleted
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Novartis Gene TherapiesPRA Health SciencesCompletedSpinal Muscular AtrophyUnited States, United Kingdom, Australia, Belgium, Canada, Japan
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Novartis Gene TherapiesCompletedGene Therapy | SMA - Spinal Muscular AtrophyUnited States
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Novartis Gene TherapiesCompletedSMAFrance, United Kingdom, Italy, Belgium
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Columbia UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedSpinal Muscular Atrophy Type 3 | Mitochondrial MyopathyUnited States
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Great Ormond Street Hospital for Children NHS Foundation...CompletedSpinal Muscular AtrophyUnited Kingdom
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Ohio State UniversityBiogen; Cure SMACompleted
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Institut de Myologie, FranceCompletedSpinal Muscular AtrophyFrance
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Catalyst Pharmaceuticals, Inc.CompletedMuscular Atrophy, SpinalItaly
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Assistance Publique - Hôpitaux de ParisCompletedInfantile Spinal Muscular Atrophy of Type 2 or 3France
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Hospital Israelita Albert EinsteinMinistry of Health, BrazilCompletedSpinal Muscular AtrophyBrazil
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BiogenCompleted
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BiogenNo longer availableInfantile-onset Spinal Muscular AtrophyNew Zealand, Colombia, Turkey
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Centre Hospitalier Régional de la CitadelleRoche Pharma AG; Biogen; AveXis, Inc.; Association Belge contre les Maladies neuro...CompletedSpinal Muscular AtrophyBelgium
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BiogenCompletedSpinal Muscular AtrophyUnited States
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BiogenCompletedSpinal Muscular AtrophyUnited States, Canada
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BiogenTerminatedSpinal Muscular AtrophyKorea, Republic of, United States, Spain, Canada, Germany, Australia, Japan, Sweden, Belgium, France, Italy, Turkey, United Kingdom
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BiogenTerminatedSpinal Muscular AtrophyUnited States, Germany
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Gillette Children's Specialty HealthcareUniversity of MinnesotaCompletedSpinal Muscular Dystrophy | Neuromuscular DisabilityUnited States
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BiogenCompletedSpinal Muscular AtrophyUnited States, Germany, Spain, Canada, France, Hong Kong, Italy, Japan, Korea, Republic of, Sweden
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BiogenCompleted
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BiogenCompleted