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Search clinical trials for: Spinal muscular atrophy
Total 23211 results
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BiogenRecruitingHealthy Volunteer | Muscular Atrophy, SpinalKorea, Republic of, Germany, Belgium, Netherlands, France, Italy, Poland, Canada, United Kingdom, Israel
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Istanbul Medipol University HospitalIstanbul UniversityRecruitingNeuromuscular Diseases | Spinal Muscular Atrophy Type 3Turkey
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Columbia UniversityGenentech, Inc.RecruitingSpinal Muscular AtrophyUnited States
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University of OxfordHoffmann-La Roche; Oxford University Hospitals NHS Trust; Novartis Gene TherapiesRecruiting
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AbiliTech Medical Inc.Richard M. Schulze Family FoundationRecruitingCerebral Palsy | Muscular Dystrophies | Duchenne Muscular Dystrophy | Becker Muscular Dystrophy | Spinal Muscular Atrophy | Limb Girdle Muscular Dystrophy | FSHDUnited States
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Hospices Civils de LyonRecruitingSpinal Muscular AtrophyFrance
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BiogenRecruitingSpinal Muscular Atrophy (SMA)France
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Charles University, Czech RepublicRecruiting
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Novartis PharmaceuticalsRecruitingSpinal Muscular Atrophy (SMA)Spain, Canada, Taiwan, Belgium, Malaysia, China, Japan, Italy, Singapore, United Kingdom, France, Australia, Thailand, Denmark, United States
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LMU KlinikumRecruitingPompe Disease (Late-onset) | FSHD | Spinal Muscular Atrophy Type 3 | Inclusion Body MyositisGermany
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Genentech, Inc.RecruitingSpinal Muscular AtrophyUnited States, Puerto Rico
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Bakri ElsheikhGenentech, Inc.RecruitingSpinal Muscular AtrophyUnited States
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University of AlbertaMcGill University; University of Toronto; Laval University; Simon Fraser UniversityRecruitingAmyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Frontotemporal Degeneration | Progressive Muscular AtrophyCanada
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First Affiliated Hospital of Fujian Medical UniversityPeking Union Medical College Hospital; Fujian Medical University Union HospitalRecruiting
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Hoffmann-La RocheRecruitingSpinal Muscular Atrophy (SMA)Belgium, United States, Croatia, Japan, Netherlands, Spain, Canada, Poland, United Kingdom, Portugal, Italy, Australia
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Bahçeşehir UniversityNot yet recruitingDuchenne Muscular Dystrophy | Spinal Muscular Atrophy | Healthy Individuals
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Assistance Publique - Hôpitaux de ParisInstitut National de la Santé Et de la Recherche Médicale, France; Association...RecruitingAmyotrophic Lateral Sclerosis | Kennedy DiseaseFrance
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BiogenRecruitingSpinal Muscular AtrophyUnited States, Germany, Italy, Hungary, Japan
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BiogenRecruiting
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National Institute of Neurological Disorders and...RecruitingMotor Neuron Disease | Spinal and Bulbar Muscular Atrophy | Kennedys DiseaseUnited States
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University of MiamiNational Institute of Neurological Disorders and Stroke (NINDS); National Institutes...RecruitingAmyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Frontotemporal Dementia | Progressive Muscular Atrophy | Hereditary Spastic ParaplegiaUnited States, South Africa
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Mahidol UniversityRecruitingSpinal Muscular AtrophyThailand
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Assistance Publique - Hôpitaux de ParisRecruitingSpinal Muscular AtrophyFrance
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Seoul National University HospitalNot yet recruiting
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Thomas Jefferson UniversityRecruitingStroke | Cerebral Palsy | Amyotrophic Lateral Sclerosis | Muscular Dystrophies | Spinal Cord Injuries | Hemiparesis | Spinal Muscular Atrophy | Quadriplegia | Arthrogryposis | Neurologic Diseases | Charcot-Marie-Tooth | Weakness of Extremities as Sequela of Stroke | Weakness Due to Upper Motor Neuron Dysfunction | Arm ParalysisUnited States
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University of GiessenRecruitingSpinal Muscular AtrophyGermany
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Assistance Publique Hopitaux De MarseilleRecruitingSpinal Muscular AtrophyFrance
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CHU de ReimsRecruitingSpinal Muscular AtrophyFrance
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Oregon Health and Science UniversityRecruitingAmyotrophic Lateral Sclerosis | Muscular Dystrophies | Spinal Cord Injuries | Multiple System Atrophy | Parkinson's Disease and Parkinsonism | Brain Tumor Adult | Locked-in Syndrome | Brainstem StrokeUnited States
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Koç UniversityRecruitingMuscular Dystrophies | Telemedicine | Proximal MyopathyTurkey
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BiogenRecruitingObservational, Postmarketing Surveillance Study of Spinraza Injection (Nusinersen Sodium) (STANDARD)Muscular Atrophy, SpinalKorea, Republic of
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Dr. Rebecca SchuleGerman Research Foundation; German Center for Neurodegenerative Diseases (DZNE)RecruitingSpastic AtaxiaCanada, France, Germany, Italy, Netherlands, Turkey, United Kingdom
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Newcastle UniversityRoche Pharma AG; Biogen; Adult SMA REACH; SMA REACH UKRecruiting
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Assistance Publique - Hôpitaux de ParisRecruiting
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AveXis, Inc.United BioSource, LLCRecruitingSpinal Muscular Atrophy (SMA)Japan, United States, Korea, Republic of, Israel, Greece, Ireland, Portugal, Russian Federation, Taiwan
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Seoul National University HospitalNational Research Foundation of KoreaNot yet recruitingSarcopenia | Spinal Disease
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Merve KurtRecruitingDuchenne Muscular Dystrophy | Virtual Reality | Spinal Muscular Atrophy | Neuromuscular Disease | BiofeedbackTurkey
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TakedaRecruitingSpinal and Bulbar Muscular AtrophyJapan
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Great Ormond Street Hospital for Children NHS Foundation...RecruitingSpinal Muscular AtrophyUnited Kingdom
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University of MiamiNational Institute of Neurological Disorders and Stroke (NINDS); National Institutes... and other collaboratorsRecruitingAmyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Progressive Muscular Atrophy | ALS-Frontotemporal DementiaUnited States
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Kaohsiung Medical University Chung-Ho Memorial...The Chinese Foundation of Health; Taipei Institute of PathologyRecruiting
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Nemours Children's ClinicRecruitingCharcot-Marie-Tooth Disease | Motor Neuron Disease | Amyotrophic Lateral Sclerosis | Muscular Dystrophy | Spinal Muscular Atrophy | Neuromuscular Disease | Spinal Muscular Atrophy With Respiratory Distress 1 | Peroneal Muscular AtrophyUnited States
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Sanford HealthNational Ataxia Foundation; Beyond Batten Disease Foundation; Pitt Hopkins Research... and other collaboratorsRecruitingMitochondrial Diseases | Retinitis Pigmentosa | Myasthenia Gravis | Eosinophilic Gastroenteritis | Multiple System Atrophy | Leiomyosarcoma | Leukodystrophy | Anal Fistula | Spinocerebellar Ataxia Type 3 | Friedreich Ataxia | Kennedy Disease | Lyme Disease | Hemophagocytic Lymphohistiocytosis | Spinocerebellar Ataxia... and other conditionsUnited States, Australia
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BiogenActive, not recruiting
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Scholar Rock, Inc.CompletedNeuromuscular Diseases | Neuromuscular Manifestations | Atrophy | Muscular Atrophy | Spinal Muscular Atrophy | Muscular Atrophy, Spinal | Spinal Muscular Atrophy Type 3 | SMA | Spinal Muscular Atrophy Type 2United States, Spain, Italy, Netherlands
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Marco CapogrossoRoche-GenentechActive, not recruitingSpinal Muscular Atrophy Type 3 | Spinal Muscular Atrophy Type 4United States
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Hoffmann-La RocheActive, not recruitingSpinal Muscular AtrophyBelgium, United States, United Kingdom, France, Poland, Italy, Switzerland, Netherlands, Germany
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Hoffmann-La RocheActive, not recruitingMuscular Atrophy, SpinalUnited States, Belgium, Brazil, Russian Federation, Australia, Taiwan, Poland
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BiogenCompletedMuscular Atrophy, SpinalChina, United States, Netherlands, Spain, Korea, Republic of, Taiwan, Australia, Canada, Chile, Saudi Arabia, Poland, Israel, Brazil, Russian Federation, Hungary, Japan, United Kingdom, Italy, Germany, Estonia, Greece, Mexico, Colombia and more