- ICH GCP
- US Clinical Trials Registry
- Search trials
Search clinical trials for: adeno associated virus
Total 44908 results
-
Sarepta Therapeutics, Inc.Active, not recruitingLimb-Girdle Muscular Dystrophy, Type 2EUnited States
-
Baxalta now part of ShireActive, not recruiting
-
Spark TherapeuticsCompletedChoroideremia | CHM (Choroideremia) Gene MutationsUnited States
-
Spark TherapeuticsCompletedHemophilia AUnited States, Australia, Canada, Israel, Thailand
-
Astellas Gene TherapiesActive, not recruitingX-Linked Myotubular MyopathyUnited States, Canada, France, Germany
-
Byron LamNational Eye Institute (NEI)Active, not recruitingLeber's Hereditary Optic NeuropathyUnited States
-
Daniel BenjaminEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedHeart Failure | Epilepsy | Pain | Pneumonia | Sepsis | Inflammation | Hypertension | Chronic Kidney Diseases | Hemophilia | Schizophrenia | Central Nervous System Infections | Nosocomial Pneumonia | Insomnia | Anxiety | Bipolar Disorder | Neutropenia | Staphylococcal Infections | Bradycardia | Seizures | Urinary Tract Infections | Pulmonary... and other conditionsUnited States, Canada, United Kingdom, Israel, Singapore
-
Homology Medicines, IncTerminated
-
Jonsson Comprehensive Cancer CenterNational Cancer Institute (NCI)TerminatedAnatomic Stage I Breast Cancer AJCC v8 | Anatomic Stage IA Breast Cancer AJCC v8 | Anatomic Stage IB Breast Cancer AJCC v8 | Anatomic Stage II Breast Cancer AJCC v8 | Anatomic Stage IIA Breast Cancer AJCC v8 | Anatomic Stage IIB Breast Cancer AJCC v8 | Anatomic Stage IIIA Breast Cancer AJCC v8 | Anatomic... and other conditionsUnited States
-
Shanghai Belief-Delivery BioMed Co., LtdActive, not recruiting
-
Brainvectis, a subsidiary of Asklepios BioPharmaceutical...Active, not recruitingHuntington DiseaseFrance
-
Sarepta Therapeutics, Inc.Nationwide Children's HospitalCompleted
-
Applied Genetic Technologies CorpCompletedX-linked RetinoschisisUnited States
-
Ultragenyx Pharmaceutical IncTerminatedWilson Disease | Ornithine Transcarbamylase Deficiency | Glycogen Storage Disease Type IASpain, United Kingdom, Canada, United States, Brazil
-
Baxalta now part of ShireTakeda Development Center Americas, Inc.; Baxalta Innovations GmbH, now part...Active, not recruitingHemophilia AUnited States, Spain, Hungary, Italy, Germany, Austria, France
-
Selecta Biosciences, Inc.National Human Genome Research Institute (NHGRI)SuspendedMethylmalonic Acidemia (MMA)United States
-
Novartis Gene TherapiesTerminatedSpinal Muscular AtrophyUnited States
-
BiocadTerminated
-
MeiraGTx UK II LtdJanssen Research & Development, LLCCompleted
-
Kunming Hope of Health HospitalTerminatedMenkes SyndromeChina
-
Sangamo TherapeuticsCeregeneCompletedIdiopathic Parkinson's DiseaseUnited States
-
Sangamo TherapeuticsCeregeneCompleted
-
National Cancer Institute (NCI)CompletedCervical Adenocarcinoma | Cervical Squamous Cell Carcinoma | Stage IVA Cervical Cancer AJCC v6 and v7 | Recurrent Cervical Carcinoma | Human Papillomavirus Infection | Stage IVB Cervical Cancer AJCC v6 and v7United States, Canada
-
Institute of Hematology & Blood Diseases HospitalEast China University of Science and TechnologyActive, not recruiting
-
Novartis Gene TherapiesCompletedSpinal Muscular Atrophy 1United States
-
AIDS Malignancy ConsortiumNational Cancer Institute (NCI); Montefiore Medical Center; University of Arkansas and other collaboratorsCompletedAcquired Immunodeficiency Syndrome | Cervical CancerSouth Africa, Zimbabwe
-
Homology Medicines, IncEnrolling by invitationPhenylketonuria | PAH DeficiencyUnited States
-
Audentes TherapeuticsTerminatedCrigler-Najjar SyndromeIsrael, United States, United Kingdom
-
University of FloridaLacerta TherapeuticsCompletedPompe DiseaseUnited States
-
ChimerixCompleted
-
King Khaled Eye Specialist HospitalKing Faisal Specialist Hospital & Research CenterCompletedRetinitis Pigmentosa | Retinal DiseaseSaudi Arabia
-
Eisai Inc.Completed
-
Gamaleya Research Institute of Epidemiology and...Government of the city of Moscow; Russian Direct Investment Fund; CRO: iPharmaUnknownCOVID-19 PreventionRussian Federation
-
Sangamo TherapeuticsAlzheimer's Disease Cooperative Study (ADCS)CompletedAlzheimer's DiseaseUnited States
-
Spark TherapeuticsCompleted
-
M.D. Anderson Cancer CenterVertex Pharmaceuticals IncorporatedTerminatedInfectionUnited States
-
Spark TherapeuticsChildren's Hospital of Philadelphia; Royal Prince Alfred Hospital, Sydney,... and other collaboratorsCompleted
-
Sangamo TherapeuticsCompletedIdiopathic Parkinson's DiseaseUnited States
-
Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)CompletedStage II Multiple Myeloma | Stage III Multiple Myeloma | Chronic Myelomonocytic Leukemia | Recurrent Adult Acute Myeloid Leukemia | Juvenile Myelomonocytic Leukemia | Extranodal Marginal Zone B-cell Lymphoma of Mucosa-associated Lymphoid Tissue | Nodal Marginal Zone B-cell Lymphoma | Recurrent Adult... and other conditionsUnited States, Italy
-
Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute...CompletedClear Cell Renal Cell Carcinoma | Chronic Myelomonocytic Leukemia | Recurrent Adult Acute Myeloid Leukemia | Juvenile Myelomonocytic Leukemia | Extranodal Marginal Zone B-cell Lymphoma of Mucosa-associated Lymphoid Tissue | Nodal Marginal Zone B-cell Lymphoma | Recurrent Adult Burkitt Lymphoma | Recurrent... and other conditionsUnited States, Germany, Italy
-
Institute of Liver and Biliary Sciences, IndiaCompleted
-
Jichi Medical UniversityTakara Bio Inc.; Gene Therapy Research Institution,Co.,Ltd.Terminated
-
Applied Genetic Technologies CorpNational Heart, Lung, and Blood Institute (NHLBI)CompletedAlpha-1 Antitrypsin DeficiencyUnited States, Ireland
-
Spark TherapeuticsChildren's Hospital of Philadelphia; University of Pittsburgh; St. James's Hospital... and other collaboratorsTerminated
-
Postgraduate Institute of Medical Education and...Completed
-
Tacere Therapeutics, Inc.TerminatedHepatitis CUnited States
-
University of FloridaNational Heart, Lung, and Blood Institute (NHLBI)CompletedPompe DiseaseUnited States
-
Applied Genetic Technologies CorpOregon Health and Science University; University of Massachusetts, WorcesterCompletedLeber Congenital AmaurosisUnited States
-
University of OxfordUniversity College, London; University of Southampton; Moorfields Eye Hospital... and other collaboratorsCompleted
-
LYSOGENECompletedMucopolysaccharidosis Type III A | Sanfilippo Disease Type AFrance