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Search clinical trials for: alpha-1 antitrypsin deficiency
Total 60675 results
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OctapharmaWithdrawn
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Arrowhead PharmaceuticalsWithdrawnAlpha-1 Antitrypsin DeficiencyIreland, Canada, Italy, Sweden
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University of Massachusetts, WorcesterNational Heart, Lung, and Blood Institute (NHLBI); University of Florida; National... and other collaboratorsCompletedAlpha 1-Antitrypsin DeficiencyUnited States
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Applied Genetic Technologies CorpNational Heart, Lung, and Blood Institute (NHLBI)CompletedAlpha-1 Antitrypsin DeficiencyUnited States, Ireland
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University of Alabama at BirminghamNational Institutes of Health (NIH); Mereo BioPharmaCompletedEmphysema or COPD | Alpha-1 Antitrypsin Deficiency (AATD) | Pi*ZZ, Pi*SZ, Pi*Null, Another Rare Phenotype/Genotype Known to be Associated With Either Low or Functionally Impaired AAT Including F or I MutationsUnited States
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Krystal Biotech, Inc.RecruitingAlpha 1-Antitrypsin DeficiencyUnited States
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Hospital Universitari Vall d'Hebron Research InstituteEuropean Respiratory SocietyRecruitingAlpha 1-Antitrypsin DeficiencySpain
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Dicerna Pharmaceuticals, Inc., a Novo Nordisk companyActive, not recruitingAlpha 1-Antitrypsin DeficiencyUnited Kingdom, United States, Ireland, Belgium, New Zealand, Spain, Netherlands, Portugal, Canada, Australia, France, Austria, Germany, Sweden
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St. Louis UniversityBoston University; University College, London; University of Massachusetts, Worcester and other collaboratorsActive, not recruiting
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Arrowhead PharmaceuticalsCompleted
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Arrowhead PharmaceuticalsTerminatedAlpha-1 Antitrypsin DeficiencyAustralia, Netherlands, Germany, United Kingdom
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Kamada, Ltd.CompletedAlpha 1-Antitrypsin DeficiencyUnited States
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Columbia UniversityNational Heart, Lung, and Blood Institute (NHLBI); Alpha-1 FoundationActive, not recruitingAlpha 1-Antitrypsin Deficiency | Genetic DiseaseUnited States
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Adverum Biotechnologies, Inc.CompletedAlpha 1-Antitrypsin DeficiencyUnited States
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Inhibrx, Inc.CompletedAlpha-1 Antitrypsin Deficiency | AATDUnited States, New Zealand, United Kingdom
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Arrowhead PharmaceuticalsActive, not recruitingAlpha 1-Antitrypsin DeficiencyAustria, Germany, United Kingdom
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Dicerna Pharmaceuticals, Inc.WithdrawnAlpha 1-Antitrypsin DeficiencyNew Zealand
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Mereo BioPharmaSyneos HealthCompletedEmphysema | Alpha 1-Antitrypsin Deficiency | COPDUnited Kingdom, Belgium, United States, Denmark, Canada, Sweden, Poland, Spain
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Grifols Therapeutics LLCGrifols Japan K.K.CompletedAlpha1-Antitrypsin DeficiencyJapan
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University of Massachusetts, WorcesterNational Heart, Lung, and Blood Institute (NHLBI); University of Florida; National... and other collaboratorsCompletedAlpha 1-Antitrypsin DeficiencyUnited States
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Baxalta now part of ShireArriva Pharmaceuticals, Inc.CompletedAlpha1-antitrypsin DeficiencyUnited States
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RWTH Aachen UniversityUnknown
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Grifols Therapeutics LLCRecruiting
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Vertex Pharmaceuticals IncorporatedCompletedAlpha1-Antitrypsin DeficiencyUnited States, Germany, Canada, Ireland, Sweden, United Kingdom
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Grifols Therapeutics LLCGrifols Japan K.K.Completed
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Schön Klinik Berchtesgadener LandUnknownChronic Obstructive Pulmonary Disease | Alpha 1-Antitrypsin DeficiencyGermany
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TakedaEnrolling by invitationAlpha1-Antitrypsin DeficiencyUnited Kingdom, Germany, United States, Austria, Portugal
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Baxalta now part of ShireArriva Pharmaceuticals, Inc.CompletedAlpha1-antitrypsin DeficiencyUnited States
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Z Factor LimitedHammersmith Medicines Research; Centessa Pharmaceuticals plcTerminatedAlpha1 Anti-Trypsin DeficiencyUnited Kingdom
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Kamada, Ltd.Completed
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Baxalta now part of ShireCompletedAlpha1-antitrypsin DeficiencyUnited States, Canada
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Baxalta now part of ShireTerminated
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TakedaRecruitingAlpha1-Antitrypsin DeficiencyItaly, United States, Poland, Portugal
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TakedaTakeda Development Center Americas, Inc.RecruitingAlpha1-Antitrypsin DeficiencyUnited States, Belgium, Switzerland, Canada, Australia, Germany, United Kingdom, Austria, France, Spain, Portugal, Italy, Poland, Brazil
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Soroka University Medical CenterUnknownPost Cardiac Surgery Systemic Inflammatory Response
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University of FloridaCompletedAlpha-1 Antitrypsin Deficiency | Liver Fibrosis | AATD | AAT DeficiencyUnited States
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Baxalta now part of ShireCompleted
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Gerard TurinoCompletedEmphysema | Alpha 1-Antitrypsin DeficiencyUnited States, Canada
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Alnylam PharmaceuticalsTerminatedAntitrypsin Deficiency Liver DiseaseUnited Kingdom
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University of Michigan Rogel Cancer CenterCSL Behring; The Leukemia and Lymphoma SocietyCompletedGraft vs Host DiseaseUnited States
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Medical University of South CarolinaCSL BehringCompletedSmoking | Emphysema | Alpha-1 Antitrypsin Deficiency | COPDUnited States
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Medical University of South CarolinaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)CompletedChronic PancreatitisUnited States
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Grifols Therapeutics LLCCompletedAlpha 1-Antitrypsin DeficiencyDenmark, Sweden, United Kingdom
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Kamada, Ltd.CompletedType 1 Diabetes MellitusIsrael
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John LevineNational Cancer Institute (NCI)CompletedGVHD | Graft-versus-host-diseaseUnited States
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Assistance Publique - Hôpitaux de ParisUnknownEmphysema | Alpha 1-Antitrypsin DeficiencyFrance
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University of California, Los AngelesCompleted
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National Heart, Lung, and Blood Institute (NHLBI)CompletedLung Diseases, Obstructive | Emphysema | Alpha 1-Antitrypsin DeficiencyUnited States
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Columbia UniversityAlpha-1 Foundation; Stony Wold-Herbert Fund, Inc.CompletedChronic Obstructive Pulmonary Disease | Emphysema | Alpha-1 Antitrypsin DeficiencyUnited States
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Inhibrx, Inc.Not yet recruitingEmphysema | Alpha 1-Antitrypsin Deficiency