- ICH GCP
- US Clinical Trials Registry
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Search clinical trials for: gene therapy; lentiviral vector; KL003; β-thalassemia
Total 268949 results
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David WilliamsActive, not recruiting
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Memorial Sloan Kettering Cancer CenterActive, not recruitingConfirmed Diagnosis of ß-thalassemia MajorUnited States
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University of PennsylvaniaCompletedSubjects Entering Into This Protocol Will be Followed for up to 15 Years After Initial CART-EGFRvIII InfusionUnited States
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Great Ormond Street Hospital for Children NHS Foundation...Orchard TherapeuticsCompletedSevere Combined Immunodeficiency Due to ADA DeficiencyUnited Kingdom
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American Gene Technologies International Inc.Enrolling by invitation
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IRCCS San RaffaeleTelethon Institute for Gene Therapy (OSR-TIGET)Active, not recruiting
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Bioray LaboratoriesPLA 923 HospitalTerminated
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Prothya BiosolutionsTerminated
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University of California, Los AngelesOrchard Therapeutics; California Institute for Regenerative Medicine (CIRM)CompletedSevere Combined Immunodeficiency Due to ADA DeficiencyUnited States
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University of California, Los AngelesNational Institute of Allergy and Infectious Diseases (NIAID); National Heart... and other collaboratorsCompleted
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bluebird bioCompletedCerebral Adrenoleukodystrophy (CALD)United States, Germany, Argentina, Australia, France, United Kingdom
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Great Ormond Street Hospital for Children NHS Foundation...Orchard TherapeuticsCompletedAdenosine Deaminase Deficiency | Severe Combined Immunodeficiencies (SCID)United Kingdom
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IRCCS San RaffaeleFondazione TelethonActive, not recruiting
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Protagonist Therapeutics, Inc.CompletedChronic Anemia | β-thalassemia | Ineffective ErythropoiesisUnited States, Malaysia, Turkey, Thailand, United Kingdom, Italy, Lebanon, Tunisia, Greece
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Protagonist Therapeutics, Inc.Completedβ-thalassemia | Ineffective ErythropoiesisMalaysia, Thailand, United States, Greece, United Kingdom, Turkey, Lebanon, Tunisia
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CSL BehringTerminated
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GenethonInstitute of Child Health; Great Ormond Street Hospital for Children NHS Foundation...Completed
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GenethonActive, not recruitingWiskott-Aldrich SyndromeUnited Kingdom, France
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Novartis PharmaceuticalsCompletedTransfusional Iron Overload | β-thalassemiaItaly
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Hospital Universitari Vall d'Hebron Research InstituteCIEMAT; CIBERERCompleted
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National Institute of Allergy and Infectious Diseases...UnknownX-Linked Combined Immunodeficiency DiseasesUnited States
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Shenzhen Geno-Immune Medical InstituteUnknownAdenosine DeAminase Severe Combined ImmunoDeficiency (ADA-SCID)China
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Shenzhen Geno-Immune Medical InstituteUnknownSCID, X LinkedChina
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Shenzhen Geno-Immune Medical InstituteUnknown
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Shenzhen Geno-Immune Medical InstituteUnknown
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Shenzhen Geno-Immune Medical InstituteUnknown
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Shenzhen Geno-Immune Medical InstituteUnknown
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IRCCS San RaffaeleOrchard Therapeutics; Fondazione TelethonUnknown
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bluebird bioCompletedβ-thalassemia MajorUnited States, Australia, Thailand
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Theravectys S.A.Completed
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute...WithdrawnStage III Adult Hodgkin Lymphoma | Stage IV Adult Hodgkin Lymphoma | Human Immunodeficiency Virus 1 Positive | Stage I Adult Hodgkin Lymphoma | Stage II Adult Hodgkin Lymphoma | Stage I Adult Non-Hodgkin Lymphoma | Stage II Adult Non-Hodgkin Lymphoma | Stage III Adult Non-Hodgkin Lymphoma | Stage IV...United States
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GenethonHôpital Necker-Enfants MaladesCompleted
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Assiut UniversityUnknown
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Shenzhen Geno-Immune Medical InstituteUnknown
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National Human Genome Research Institute (NHGRI)National Institutes of Health Clinical Center (CC); National Cancer Institute... and other collaboratorsCompletedADA-SCID | Adenosine Deaminase DeficiencyUnited States
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Nanfang Hospital of Southern Medical UniversityGuangdong Yike Gene Science and Technology CO.,LtdUnknownBeta Thalassemia MajorChina
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Novartis PharmaceuticalsWithdrawn
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Novartis PharmaceuticalsCompletedTransfusional Iron Overload | β-thalassemia Major | Pediatric Rare AnemiaItaly, France
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Aghia Sophia Children's Hospital of AthensUnknownAsplenia | β-thalassemia MajorGreece
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Great Ormond Street Hospital for Children NHS Foundation...WithdrawnGranulomatous Disease, Chronic, X-linked, VariantUnited Kingdom
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Novartis PharmaceuticalsCompletedTransfusional Iron Overload in β-thalassemiaUnited States, Greece, Argentina, Germany, Belgium, Italy, United Kingdom, France, Tunisia, Canada, Turkey, Brazil
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Novartis PharmaceuticalsCompletedAnemia | HemosiderosisUnited States, Germany, Belgium, United Kingdom, Italy, Canada, France
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Shiraz University of Medical SciencesCompletedCombination Therapy of Hydroxyurea With L-Carnitine and Magnesium Chloride in Thalassemia Intermediaβ-Thalassemia IntermediaIran, Islamic Republic of
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Yeditepe UniversityNot yet recruitingDiabetes Mellitus, Type 2Turkey
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Hospital de Clinicas de Porto AlegreVifor PharmaNot yet recruitingHeart Failure, Systolic | Iron DeficienciesBrazil
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CellinCellsNot yet recruiting
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Istanbul Medipol University HospitalRecruiting
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Sun Yat-sen UniversityRecruiting