- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials Sponsored by Office of Rare Diseases (ORD)
Total 457 results
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); Rare Diseases... and other collaboratorsTerminatedAndersen-Tawil SyndromeUnited States
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National Center for Research Resources (NCRR)Ohio State UniversityCompletedPolyradiculoneuropathy, Chronic Inflammatory Demyelinating
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National Institute on Drug Abuse (NIDA)Johns Hopkins UniversityUnknown
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National Center for Research Resources (NCRR)Children's Hospital ColoradoUnknownLiver Cirrhosis | Cirrhosis
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National Center for Research Resources (NCRR)Johns Hopkins UniversityCompletedAmino Acid Metabolism, Inborn Errors
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National Center for Research Resources (NCRR)Ohio State UniversityCompletedAmyotrophic Lateral Sclerosis | Spinal Muscular Atrophy | Spinobulbar Muscular Atrophy
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National Center for Research Resources (NCRR)Virginia Commonwealth UniversityCompletedSystemic Lupus Erythematosus
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National Institute of Diabetes and Digestive and...University of PittsburghCompletedVulvar Diseases | Interstitial Cystitis
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Emory UniversityNational Institute of Neurological Disorders and Stroke (NINDS); Office of...WithdrawnSpasmodic Dysphonia | Laryngeal DystoniaUnited States
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National Center for Research Resources (NCRR)Baylor College of MedicineCompleted
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National Center for Research Resources (NCRR)Baylor College of MedicineCompleted
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National Institute of Neurological Disorders and...Mayo ClinicUnknownAcute Disseminated Encephalomyelitis | Devic's Syndrome | Marburg's Variant of Multiple Sclerosis | Balo's Concentric Sclerosis | Acute Transverse Myelitis
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National Center for Research Resources (NCRR)Children's Hospital of PhiladelphiaCompletedOsteoporosis | Osteopenia | Thalassemia Major
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National Institute of Allergy and Infectious Diseases...University of Alabama at BirminghamCompleted
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National Institute of Neurological Disorders and...Yale UniversityCompleted
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National Institute of Dental and Craniofacial Research...Columbia UniversityCompletedHIV Infections | Candidiasis, Oral
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National Center for Research Resources (NCRR)University of North CarolinaCompletedCystic Fibrosis | Atypical Mycobacterium Infection
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National Institute of Arthritis and Musculoskeletal...The Cleveland Clinic; Rare Diseases Clinical Research Network; Office of Rare...CompletedGiant Cell Arteritis | Takayasu's ArteritisUnited States, Canada
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National Institute of Neurological Disorders and...Mayo ClinicCompleted
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National Center for Research Resources (NCRR)Baylor College of MedicineCompletedHypertension, Pulmonary
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National Center for Research Resources (NCRR)University of North CarolinaCompleted
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National Center for Research Resources (NCRR)Baylor College of MedicineCompleted
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National Center for Research Resources (NCRR)University of North CarolinaCompletedHemophilia B | Factor IX Deficiency
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National Center for Research Resources (NCRR)University of North CarolinaCompletedVon Willebrand's Disease
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National Institute of Neurological Disorders and...University of PittsburghUnknown
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National Center for Research Resources (NCRR)Vanderbilt University Medical CenterCompleted
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National Institute of Allergy and Infectious Diseases...Harvard School of Public Health (HSPH)Completed
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Peter MerkelNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedTakayasu ArteritisUnited States, Canada
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University of CincinnatiNational Center for Research Resources (NCRR); Office of Rare Diseases (ORD); FDA Office of Orphan Products DevelopmentCompletedLymphangioleiomyomatosisUnited States, Canada, Japan
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National Center for Research Resources (NCRR)University of California, Los AngelesCompleted
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National Institute of Neurological Disorders and...Massachusetts General HospitalUnknownAmyotrophic Lateral Sclerosis
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National Center for Research Resources (NCRR)University of California, San DiegoCompletedFanconi Syndrome | Cystinosis
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National Center for Research Resources (NCRR)University of California, Los AngelesCompletedPulmonary Hypertension | Respiratory Distress Syndrome | Bronchopulmonary Dysplasia
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National Center for Research Resources (NCRR)University of California, San DiegoCompleted
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National Center for Research Resources (NCRR)Indiana University School of MedicineCompleted
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National Center for Research Resources (NCRR)University of California, San DiegoCompleted
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National Institute of Neurological Disorders and...Seattle Children's HospitalUnknown
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National Center for Research Resources (NCRR)University of California, Los AngelesCompletedPseudohypoparathyroidism
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National Center for Research Resources (NCRR)Tulane University School of MedicineCompleted
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National Center for Research Resources (NCRR)University of California, San DiegoCompletedHomocystinuria
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National Center for Research Resources (NCRR)University of California, Los AngelesCompleted
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National Center for Research Resources (NCRR)National Institute of Allergy and Infectious Diseases (NIAID)Completed
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National Center for Research Resources (NCRR)National Institute of Allergy and Infectious Diseases (NIAID)CompletedCytomegalovirus Infections
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National Center for Research Resources (NCRR)National Institute of Allergy and Infectious Diseases (NIAID)Completed
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National Center for Research Resources (NCRR)National Institute of Allergy and Infectious Diseases (NIAID)Completed
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National Institute of Neurological Disorders and...University of Colorado, DenverUnknown
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Andrea GropmanNational Center for Research Resources (NCRR); Rare Diseases Clinical Research... and other collaboratorsCompletedBrain Diseases, Metabolic, Inborn | Ornithine Transcarbamylase Deficiency | Urea Cycle DisorderUnited States
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National Institute of Neurological Disorders and...Baylor College of MedicineCompletedPrader-Willi Syndrome | DiGeorge Syndrome | Williams Syndrome | Angelman Syndrome | Smith-Magenis Syndrome | Chromosome Abnormalities | Shprintzen SyndromeUnited States
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National Center for Research Resources (NCRR)Oregon Health and Science UniversityCompletedPrecocious Puberty
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National Center for Research Resources (NCRR)UNC Lineberger Comprehensive Cancer CenterCompletedMetabolism, Inborn Errors | Methionine Adenosyltransferase Deficiency