- ICH GCP
- US Clinical Trials Registry
- Search trials
Search clinical trials for: Inborn Amino Acid Metabolism, Inborn Errors
Total 43230 results
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Vitaflo International, LtdCompleted
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Vitaflo International, LtdJohannes Gutenberg University Mainz; Kreiskliniken ReutlingenCompleted
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Vitaflo International, LtdCompletedAlkaptonuria | Tyrosinemias | Tyrosinemia, Type I | Tyrosinemia, Type II | Tyrosinemia, Type IIIUnited Kingdom
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Vitaflo International, LtdOregon Health and Science UniversityCompleted
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Vitaflo International, LtdArla FoodsCompletedPhenylketonuriasUnited Kingdom, Denmark
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Vitaflo International, LtdBirmingham Women's and Children's NHS Foundation TrustCompletedPhenylketonuria | Inborn Errors of MetabolismUnited Kingdom
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Vitaflo International, LtdCompleted
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Vitaflo International, LtdActive, not recruiting
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Vitaflo International, LtdActive, not recruiting
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Fondation Ophtalmologique Adolphe de RothschildCompletedAlbinism | Fovea PlanaFrance
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Instituto de Seguridad y Servicios Sociales de...CompletedHypercholesterolemia, FamilialMexico
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BioMarin PharmaceuticalActive, not recruitingPhenylketonuria (PKU)United States, Germany
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Travere Therapeutics, Inc.Active, not recruiting
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PTC TherapeuticsCompletedPhenylketonuriaSpain, United States, Australia, Germany, United Kingdom, Brazil, Denmark, Canada, France, Georgia, Italy, Mexico, Netherlands, Portugal, Turkey
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HemoShear TherapeuticsTerminatedPropionic Acidemia | Methylmalonic AcidemiaUnited States, Saudi Arabia, Australia
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HemoShear TherapeuticsPrometrika, LLC; AllStripes Research Inc.; Genome MedicalTerminatedPropionic Acidemia | Methylmalonic AcidemiaUnited States, Canada, United Kingdom
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CoA Therapeutics, Inc., a BridgeBio companyTerminatedHealthy Volunteers | Propionic Acidemia | Methylmalonic Acidemia | Organic AcidemiaUnited States
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Thomas Chi, MDNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)Active, not recruiting
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University of Massachusetts, AmherstWithdrawnOxidative Stress | COPD | Tetrahydrobiopterin DeficiencyUnited States
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S.LAB (SOLOWAYS)Center of New Medical Technologies; Triangel ScientificCompletedHyperlipoproteinemias | HyperhomocysteinemiaRussian Federation
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Klaus ParhoferTerminated
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LogicBio Therapeutics, IncAlexion Pharmaceuticals, Inc.Active, not recruitingMethylmalonic AcidemiaUnited States
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University of Southern CaliforniaNational PKU AllianceActive, not recruitingPhenylketonuriasUnited States
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IntraBio IncCompletedNiemann-Pick Disease, Type CUnited States, United Kingdom, Germany, Slovakia, Spain
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Nutricia UK LtdCompletedPKU | TyrosinemiasUnited Kingdom
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Boston Children's HospitalBioMarin PharmaceuticalCompletedPhenylketonuriasUnited States
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PTC TherapeuticsCompletedBH4 Deficiency | HyperphenylalaninemiaUnited States
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Arcturus Therapeutics, Inc.CompletedOrnithine Transcarbamylase DeficiencyNew Zealand
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Homology Medicines, IncTerminatedPhenylketonuria | Phenylketonurias | PAH DeficiencyUnited States
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Istanbul University - Cerrahpasa (IUC)CompletedUrea Cycle Disorder | Lysinuric Protein IntoleranceTurkey
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Hospital Universitario 12 de OctubreActive, not recruiting
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IntraBio IncActive, not recruitingNiemann-Pick Disease, Type CUnited States, Australia, United Kingdom, Germany, Slovakia, Netherlands, Czechia, Switzerland
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University of NebraskaCompleted
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Homology Medicines, IncTerminated
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Homology Medicines, IncTerminated
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Tulane University School of MedicineBioMarin PharmaceuticalCompletedPhenylketonuria | Behavior and Behavior Mechanisms | PAH Gene ExpressionUnited States
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University of Missouri-ColumbiaBioMarin PharmaceuticalEnrolling by invitationPhenylketonuriasUnited States
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Birmingham Women's and Children's NHS Foundation...Active, not recruiting
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Aeglea BiotherapeuticsTerminatedHomocystinuria Due to Cystathionine Beta-Synthase DeficiencyUnited States, United Kingdom, Australia
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Horizon Therapeutics, LLCCompletedUrea Cycle DisorderUnited States, Spain, Italy, Switzerland
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Aeglea BiotherapeuticsTerminatedArginase I Deficiency | HyperargininemiaCanada
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Aeglea BiotherapeuticsCompletedArginase I Deficiency | HyperargininemiaUnited States, Canada, United Kingdom, Portugal
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Aeglea BiotherapeuticsCompletedArginase I Deficiency | HyperargininemiaUnited States, Italy, Canada, France, United Kingdom, Austria, Germany
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APR Applied Pharma Research s.a.Terminated
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Ultragenyx Pharmaceutical IncTerminatedWilson Disease | Ornithine Transcarbamylase Deficiency | Glycogen Storage Disease Type IASpain, United Kingdom, Canada, United States, Brazil
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LYSOGENETerminatedGM1 GangliosidosisUnited Kingdom, United States, France
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Nutricia ResearchCompleted