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Search clinical trials for: Late Onset Lysosomal Acid Lipase Deficiency (CESD)
Total 42347 results
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Amicus TherapeuticsActive, not recruitingPompe Disease (Late-onset)United States, Germany, Taiwan, Belgium, Australia, Slovenia, Spain, Netherlands, Hungary, Japan, Austria, United Kingdom, France, Argentina, Canada, Sweden, Denmark, New Zealand, Greece, Korea, Republic of, Bosnia and Herzegovina, Ita... and more
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Genzyme, a Sanofi CompanyActive, not recruiting
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Genzyme, a Sanofi CompanyActive, not recruitingTay-Sachs Disease | Sandhoff DiseaseUnited States, Argentina, Czechia, Portugal, Russian Federation, Turkey, United Kingdom, Brazil, France, Germany, Italy, Japan, Spain
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Genzyme, a Sanofi CompanyCompletedSphingomyelin LipidosisUnited States, Argentina, Australia, Belgium, Brazil, Bulgaria, Chile, France, Germany, Italy, Japan, Netherlands, Portugal, Spain, Tunisia, Turkey, United Kingdom
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Genzyme, a Sanofi CompanyCompletedSphingomyelin LipidosisUnited States, Belgium, Brazil, France, Germany, Italy, United Kingdom
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Amicus TherapeuticsCompletedPompe Disease (Late-onset)United States, Australia, Korea, Republic of, Japan, Taiwan, Belgium, Slovenia, New Zealand, United Kingdom, France, Argentina, Canada, Spain, Bosnia and Herzegovina, Germany, Sweden, Hungary, Austria, Bulgaria, Denmark, Greece, I... and more
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Daniel BenjaminEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedHeart Failure | Epilepsy | Pain | Pneumonia | Sepsis | Inflammation | Hypertension | Chronic Kidney Diseases | Hemophilia | Schizophrenia | Central Nervous System Infections | Nosocomial Pneumonia | Insomnia | Anxiety | Bipolar Disorder | Neutropenia | Staphylococcal Infections | Bradycardia | Seizures | Urinary Tract Infections | Pulmonary... and other conditionsUnited States, Canada, United Kingdom, Israel, Singapore
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SanofiCompletedSphingomyelin LipidosisItaly, Czechia, Belgium, France, Portugal, Turkey, United States, Argentina, Brazil, Chile, Germany, Romania, Spain
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Fundacion Clinic per a la Recerca BiomédicaHospital Clinic of BarcelonaActive, not recruitingInfant, Newborn, Diseases | Infant DevelopmentSpain
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Asklepios Biopharmaceutical, Inc.Active, not recruiting
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Jean-Pierre RoutyCanadian Foundation for AIDS Research (CANFAR); CIHR Canadian HIV Trials NetworkCompleted
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Peking Union Medical College HospitalGilead SciencesActive, not recruiting
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BioMarin PharmaceuticalTerminatedLate-onset Pompe DiseaseUnited States, United Kingdom
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Turkish Society of Pediatric Gastroenterology,...CompletedDuchenne Muscular Dystrophy | Pompe Disease (Late-onset)Turkey
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SanofiApproved for marketing
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II (GSD-II) | Acid Maltase Deficiency Disease | Pompe DiseaseUnited States
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LMU KlinikumCompletedHealthy | Myotonic Dystrophy Type 2 | Pompe Disease (Late-onset) | Spinal Muscular Atrophy Type 3 | Myotonic Dystrophy Type 1 (DM1) | Facioscapulohumeral Muscular Dystrophy 1 | Inclusion Body Myositis, SporadicGermany
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Duke UniversityWithdrawnPompe Disease (Late-onset)United States
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Genzyme, a Sanofi CompanyTerminatedGlycogen Storage Disease Type II (GSD-II) | Pompe Disease | Glycogenesis 2 Acid Maltase DeficiencyUnited States, Israel
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Genzyme, a Sanofi CompanyCompletedSphingomyelin LipidosisBrazil, France, Italy, United States, Germany, United Kingdom
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Mayo ClinicTakedaCompleted
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University of North Carolina, Chapel HillViiV HealthcareCompletedHIV | Acute HIV InfectionUnited States
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National Institute of Allergy and Infectious Diseases...CompletedHIV Infections | TuberculosisUnited States
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National Institute of Allergy and Infectious Diseases...Lederle Laboratories; Hoechst Marion RousselCompletedHIV Infections | TuberculosisUnited States, Puerto Rico
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National Institute of Allergy and Infectious Diseases...CompletedHIV Infections | TuberculosisUnited States
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National Institute of Allergy and Infectious Diseases...AIDS Clinical Trials GroupCompletedHIV InfectionsUnited States, Puerto Rico
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Institut de Recherche pour le DeveloppementEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedHIV InfectionsThailand
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Duke UniversityCompleted
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Duke UniversityGenzyme, a Sanofi CompanyCompletedNeuropathy | Myopathy | Glycogen Storage Disease Type II (Late-onset Pompe Disease)United States
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University of FloridaBioMarin PharmaceuticalCompleted
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ShirePharmaNet; Nextrials, Inc.WithdrawnLeukodystrophy, Globoid Cell
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LMU KlinikumGenzyme, a Sanofi CompanyCompletedPompe DiseaseGermany, Taiwan, Italy
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Fred Hutchinson Cancer CenterUniversity of WashingtonCompleted
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Zymenex A/SEuropean CommissionCompletedA Placebo-Controlled Phase 3 Trial of Repeated Lamazym Treatment of Subjects With Alpha-MannosidosisAlpha-MannosidosisDenmark, United Kingdom, France, Germany, Poland
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Valerion Therapeutics, LLCTerminatedPompe DiseaseUnited States, United Kingdom
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University of British ColumbiaMedical University of Graz; Hospital de Clinicas de Porto AlegreUnknownMorquio B Disease | GM1 Gangliosidosis Type IIICanada
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Walter K. KraftMerck Sharp & Dohme LLCCompletedLatent Tuberculosis | Human Immunodeficiency Virus | Drug Interaction Potentiation | Rifamycins Causing Adverse Effects in Therapeutic UseUnited States
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Germans Trias i Pujol HospitalCompleted
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Enzyvant Therapeutics GmBHCompletedFarber Disease | Farber's Disease | Farber Lipogranulomatosis | Acid Ceramidase Deficiency | Ceramidase Deficiency | N-Laurylsphingosine Deacylase Deficiency | ASAH1 MutationUnited States, Egypt, Canada, Italy, Turkey, Argentina, Germany, India, Sweden
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Rigshospitalet, DenmarkUnknownCarbohydrate Metabolism, Inborn Errors | Metabolism, Inborn Errors | Lipid Metabolism, Inborn Errors | Glycogen Storage Disease Type II | Glycogen Storage Disease Type V | VLCAD Deficiency | Glycogen Storage Disease Type III | Phosphoglycerate Kinase Deficiency | Neutral Lipid Storage Disease | Carnitine... and other conditionsDenmark
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National Human Genome Research Institute (NHGRI)CompletedCancer | Myelofibrosis | Pulmonary Fibrosis | Gaucher Disease | Hermansky-Pudlak Syndrome (HPS)United States
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Duke UniversityCompletedPompe DiseaseUnited States
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Duke UniversityCompleted
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Duke UniversityCompleted
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Dwight Koeberl, M.D., Ph.D.Completed
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University of Modena and Reggio EmiliaCompleted
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Amicus TherapeuticsTerminatedLate-onset Pompe DiseaseUnited States, Canada, Australia, Belgium
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University of LausanneUniversity of Modena and Reggio EmiliaCompletedN-Acetylneuraminic Acid Storage DiseaseSwitzerland, Italy
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Pharmacosmos A/SLaboratory Corporation of America; BioStata; ClinStar, LLCCompletedIron Deficiency AnaemiaUnited States
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Grifols Therapeutics LLCTerminatedType 1 Diabetes MellitusUnited States