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Search clinical trials for: Metabolic abnormality
Total 77291 results
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Novilla PharmaceuticalsNot yet recruitingAcute Pain | Gout Flare | Acute Gouty ArthritisAustralia
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Novartis PharmaceuticalsRecruitingHypercholesterolaemia | Familial HypercholesterolaemiaJapan
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Xinhua Hospital, Shanghai Jiao Tong University...Shanghai Vitalgen BioPharma Co., Ltd.RecruitingType II Gaucher DiseaseChina
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Nordlandssykehuset HFUniversity of Oslo; Norwegian University of Science and Technology; The University... and other collaboratorsRecruitingPorphyria, Acute IntermittentNorway
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Sunshine Guojian Pharmaceutical (Shanghai) Co.,...Recruiting
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UniQure Biopharma B.V.RecruitingFabry DiseaseUnited States
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Copenhagen Academy for Medical Education and SimulationRigshospitalet, Denmark; Slagelse Hospital; Technical University of DenmarkNot yet recruitingFetal Growth Retardation | Fetal Macrosomia | Fetal Growth
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S.LAB (SOLOWAYS)Center of New Medical TechnologiesRecruiting
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Ain Shams UniversityRecruitingWolf Parkinson White Syndrome | ArrythmiasEgypt
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Jiangsu Atom Bioscience and Pharmaceutical Co.,...Recruiting
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Brunel UniversityRoyal Free Hospital NHS Foundation TrustRecruiting
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Chung-Hsing WangSanofiNot yet recruiting
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Assistance Publique - Hôpitaux de ParisNot yet recruitingDexamethasone During Pregnancy
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iECURE, Inc.RecruitingUrea Cycle Disorders, Inborn | Ornithine Transcarbamylase Deficiency | Ornithine Transcarbamylase Deficiency Disease | Ornithine Carbamoyltransferase Deficiency (Disorder)United Kingdom
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Hospital Universitari Vall d'Hebron Research InstituteERN-EuroBloodNet (European Reference Network on Rare Hematological DiseasesRecruitingLeukemia | Anemia | Iron Metabolism Disorders | Anemia, Sickle Cell | Thalassemia | Bleeding Disorder | Myeloma | Lymphoid Neoplasm | Blood Cancer | Bone Marrow Failure | Red Cell Membrane and Enzyme Abnormalities | Myeloma, MalignantSpain
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Hospices Civils de LyonNot yet recruitingX-Linked Hypophosphatemic Rickets
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CAMP4 Therapeutics CorporationRecruiting
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Travere Therapeutics, Inc.Recruiting
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UNICANCERServierNot yet recruitingMetastatic Colorectal Cancer | Metastatic Gastroesophageal Adenocarcinoma | DPD Deficiency
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Rolfs Consulting und Verwaltungs-GmbH (RCV)Rhythm Pharmaceuticals, Inc.RecruitingCognitive Impairment | Hyperphagia | Obesity, Childhood | Bardet-Biedl Syndrome | Polydactyly | Retinopathy | Syndactyly | POMC DeficiencyGermany
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Maastricht University Medical CenterRecruitingArthritis | Musculoskeletal Diseases | Rheumatic Diseases | Rheumatoid Arthritis | Musculoskeletal Pain | Orthopedic Disorder | Musculoskeletal Diseases or Conditions | Gout | Arthrosis | Degenerative Joint Disease | PolyarthritisNetherlands
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Swedish Orphan BiovitrumRecruitingHereditary Tyrosinemia, Type IChina
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Hospices Civils de LyonRecruitingPatients With PH1 Treated With Lumasiran in FranceFrance
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University of CambridgeSanofiRecruiting
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bluebird bioCenter for International Blood and Marrow Transplant ResearchRecruitingCerebral Adrenoleukodystrophy (CALD)United States
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Shanghai Vitalgen BioPharma Co., Ltd.RecruitingGlutaric Acidemia Type I | Glutaric Aciduria Type IChina
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Tampere University HospitalTampere UniversityRecruitingLynch Syndrome | Urothelial CarcinomaCanada, Finland
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University of PennsylvaniaRecruitingLCAT DeficiencyUnited States
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Rocket Pharmaceuticals Inc.Recruiting
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Richard FryeAutism Discovery and Treatment FoundationRecruitingEpilepsy | Neurodevelopmental Disorders | Autism Spectrum Disorder | Down Syndrome | Mitochondrial Encephalomyopathies | Pediatric Acute-Onset Neuropsychiatric Syndrome | Cerebral Folate Deficiency | Pediatric Autoimmune Neuropsychiatric Disorder Associated With Streptococcal InfectionUnited States
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BioMarin PharmaceuticalRecruitingHypochondroplasiaUnited States, Spain, Canada, France, Japan, Australia, Italy, Argentina, Brazil, Germany, United Kingdom
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Hospital Universitari Vall d'Hebron Research InstituteErasme University Hospital; Cyprus Institute of Neurology and Genetics; EuroBloodNet...RecruitingIron Metabolism Disorders | Sickle Cell Disease | Thalassemia | Hemolytic; Anemia, Hereditary, Due to Enzyme Disorder | Anemia Due to Membrane Defect | CDA | Sideroblastic Anemia | Constitutional Aplastic Anemia | Hereditary AnemiaSpain
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Foundation For Rare Disease ResearchInstitute for Asthma & Allergy; Virant Diagnostics, Inc.; MedBio Reference Laboratories...Not yet recruitingAngioedema | Urticaria | C1 Inhibitor Deficiency | Angioedemas, Hereditary | Mastocytosis | Indolent Systemic Mastocytosis | Systemic Mastocytoses | ACE Inhibitor-Induced Angioedema
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Diakonhjemmet HospitalRecruiting
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Children's Hospital of Fudan UniversityNot yet recruiting
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RezoluteRecruitingCongenital HyperinsulinismBulgaria, Canada, Denmark, France, Georgia, Germany, Greece, Israel, Oman, Qatar, Saudi Arabia, Spain, Turkey, United Arab Emirates, United Kingdom, Vietnam
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University of Alabama at BirminghamMead Johnson NutritionRecruitingEarly DHA/ARA Supplementation in Growth-restricted Very Preterm Infants: A Randomized Clinical TrialPremature | Infant Malnutrition | Nutrition Disorder, Infant | Light-For-Dates With Signs of Fetal MalnutritionUnited States
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Thammasat UniversityNot yet recruiting
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New York Stem Cell Foundation Research InstituteRecruitingPTSD | Multiple Sclerosis | Cervical Cancer | Diabetes Mellitus, Type 2 | Diabetes Mellitus | Diabetes | Macular Degeneration | Diabetes Mellitus, Type 1 | Parkinson Disease | Amyotrophic Lateral Sclerosis | Dementia | Ovarian Cancer | Alzheimer Disease | ALS | Vulvar Cancer | Post Traumatic Stress Disorder | Lewy Body Disease and other conditionsUnited States
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University College CorkNot yet recruitingGestational Diabetes | Neonatal Encephalopathy | Diastolic Dysfunction | Trisomy 21 | Transient Tachypnea of the Newborn | Small for Gestational Age at DeliveryIreland
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Kyowa Kirin Korea Co., Ltd.RecruitingFGF23-related Hypophosphataemic Rickets and OsteomalaciaKorea, Republic of
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Princess Anna Mazowiecka Hospital, Warsaw, PolandMedical University of WarsawNot yet recruitingNephrolithiasis | Vitamin D Deficiency | Metabolic Bone Disease | Osteopenia of Prematurity | Late-Onset Neonatal SepsisPoland
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Grace Science, LLCRecruitingNGLY1 DeficiencyUnited States
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Hospices Civils de LyonRecruiting
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Hospital Affiliated to the Institute of Neurology...Not yet recruitingHepatolenticular Degeneration; WilsonChina
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Sonavex, Inc.RecruitingDiabetes | End Stage Renal DiseaseUnited States
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SanofiPulse Infoframe Ltd.RecruitingNiemann-Pick Diseases | Acid Sphingomyelinase DeficiencyUnited States
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Quince Therapeutics S.p.A.BiotrialRecruitingAtaxia TelangiectasiaBelgium, United States, Denmark, Germany, Italy, Norway, Poland, Spain, United Kingdom
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McGill University Health Centre/Research Institute...Canadian Institutes of Health Research (CIHR)RecruitingZellweger Spectrum DisorderCanada