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Search clinical trials for: autosomal dominant osteopetrosis type I
Total 495621 results
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Lisa Guay WoodfordNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)RecruitingNephronophthisis | Joubert Syndrome | Bardet Biedl Syndrome | Autosomal Recessive Polycystic Kidney Disease | Congenital Hepatic Fibrosis | Hepato/Renal Fibrocystic Disease | Meckel-Gruber Syndrome | Caroli Syndrome | Oro-Facial-Digital Syndrome Type I | Glomerulocystic Kidney DiseaseUnited States
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Washington University School of MedicineNational Institute on Aging (NIA)RecruitingAlzheimer's DiseaseUnited States, Argentina, Australia, Brazil, Canada, Colombia, Germany, Japan, Korea, Republic of, Mexico, United Kingdom, Spain
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Reata, a wholly owned subsidiary of BiogenTerminatedAutosomal Dominant Polycystic Kidney | ADPKDUnited States, Spain, United Kingdom, Australia, France, Japan, Germany, Belgium, Czechia, Italy
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National Human Genome Research Institute (NHGRI)CompletedGeneralized Arterial Calcification of Infancy | Autosomal Recessive Hypophosphatemic Rickets Type2United States
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Inozyme PharmaActive, not recruitingGeneralized Arterial Calcification of Infancy | Autosomal Recessive Hypophosphatemic Rickets | Ectonucleotide Pyrophosphatase/phosphodiesterase1 DeficiencyUnited States, Canada, Germany, France, United Kingdom
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University College, LondonCancer Research UK; Cancer Research UK & UCL Cancer Trials CentreCompleted
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Mayo ClinicUniversity of Kansas Medical CenterCompletedAutosomal Dominant Polycystic Kidney DiseaseUnited States
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Memorial Sloan Kettering Cancer CenterActive, not recruitingNeuroendocrine Tumors | Liver-Dominant Metastatic Pancreatic Neuroendocrine TumorsUnited States
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University of Southern CaliforniaEnrolling by invitationAutosomal Dominant Polycystic Kidney DiseaseUnited States
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ECOG-ACRIN Cancer Research GroupNational Cancer Institute (NCI)Active, not recruitingAnatomic Stage IV Breast Cancer AJCC v8 | Prognostic Stage IV Breast Cancer AJCC v8 | Hormone Receptor Positive Breast Carcinoma | Metastatic Breast CarcinomaUnited States, Puerto Rico, Ireland
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University of Colorado, DenverActive, not recruitingAutosomal Dominant Polycystic Kidney | ADPKDUnited States
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Mario Negri Institute for Pharmacological ResearchCompleted
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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Universidad Católica San Antonio de MurciaCompleted
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Reata, a wholly owned subsidiary of BiogenTerminatedChronic Kidney Diseases | Autosomal Dominant Polycystic Kidney | Alport SyndromeUnited States, France, Australia, Japan, Spain, Puerto Rico
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McMaster UniversityCompletedPolyuria | Autosomal Dominant Polycystic KidneyCanada
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Hoffmann-La RocheNational Institute on Aging (NIA); Banner Alzheimer's InstituteCompleted
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OHSU Knight Cancer InstituteOregon Health and Science UniversityActive, not recruitingStage III Intrahepatic Cholangiocarcinoma AJCC v8 | Stage IIIA Intrahepatic Cholangiocarcinoma AJCC v8 | Stage IIIB Intrahepatic Cholangiocarcinoma AJCC v8 | Liver and Intrahepatic Bile Duct Carcinoma | Stage IV Intrahepatic Cholangiocarcinoma AJCC v8 | Unresectable Intrahepatic CholangiocarcinomaUnited States
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Novartis PharmaceuticalsActive, not recruitingAlzheimer Disease | Mild Cognitive ImpairmentFrance, Spain, Sweden, Finland
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BiogenUniversity of Rochester; David BeardenCompletedKCNT1-Related EpilepsyUnited States
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European Organisation for Research and Treatment...UNICANCER; Lymphoma Study AssociationActive, not recruitingLymphomaFrance, Spain, Switzerland, Netherlands, Belgium, Poland, Slovenia, Italy, Slovakia, Portugal
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University of Texas Southwestern Medical CenterNational Institute of Neurological Disorders and Stroke (NINDS)Active, not recruitingGlucose Metabolism Disorders | Epilepsy | Glucose Transporter Type 1 Deficiency Syndrome | Glut1 Deficiency Syndrome 1, Autosomal Recessive | Glucose Transporter Protein Type 1 Deficiency Syndrome | Glucose Transport Defect | GLUT1DS1United States
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Otsuka Pharmaceutical Co., Ltd.CompletedPolycystic Kidney, Autosomal DominantJapan
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Delcath Systems Inc.IQVIA BiotechCompletedMelanoma, OcularUnited States, Spain, Italy, Germany, United Kingdom, Switzerland, Belgium, Austria, France
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Delcath Systems Inc.Active, not recruitingMetastatic Uveal Melanoma | Metastatic Ocular MelanomaUnited States
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Sound Pharmaceuticals, IncorporatedActive, not recruiting
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Zynerba Pharmaceuticals, Inc.Completed22Q Deletion SyndromeUnited States, Australia
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The Rogosin InstituteWeill Medical College of Cornell UniversityCompletedAutosomal Dominant Polycystic KidneyUnited States
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Bellicum PharmaceuticalsTerminatedLymphoma, Non-Hodgkin | Acute Lymphoblastic Leukemia | Primary Immunodeficiency | Anemia, Sickle Cell | Hemoglobinopathies | Fanconi Anemia | Anemia, Aplastic | Myelodysplastic Syndrome | Thalassemia | Cytopenia | Diamond Blackfan Anemia | Osteopetrosis | Leukemia, Acute Myeloid (AML), ChildUnited Kingdom, Italy
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Genentech, Inc.National Institute on Aging (NIA); Banner Alzheimer's InstituteCompleted
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Children's Oncology GroupNational Cancer Institute (NCI)Active, not recruitingAnn Arbor Stage I Childhood Hodgkin Lymphoma | Ann Arbor Stage II Childhood Hodgkin Lymphoma | Childhood Nodular Lymphocyte Predominant B-Cell LymphomaUnited States, Canada, Australia, New Zealand, Puerto Rico, Israel
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Weill Medical College of Cornell UniversityThe Rogosin InstituteEnrolling by invitationAutosomal Dominant Polycystic Kidney DiseaseUnited States
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AlexionCompleted
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AlexionCompleted
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IRCCS San Camillo, Venezia, ItalyUniversita di Verona; Fondazione IRCCS Ca' Granda, Ospedale Maggiore Policlinico and other collaboratorsEnrolling by invitationCalpain-3 Deficiency Limb Girdle Muscular Dystrophy Type 2AItaly
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National Cancer Institute (NCI)CompletedMetastatic Colorectal Cancer | Hepatocellular Carcinoma | Hepatocellular Cancer | Metastatic Pancreatic Cancer | Liver MetastasisUnited States
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Taipei Medical University Shuang Ho HospitalUniversity of Southern CaliforniaEnrolling by invitationChronic Kidney Diseases | Autosomal Dominant Polycystic Kidney DiseaseTaiwan
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Palladio BiosciencesCentessa Pharmaceuticals plcTerminatedPolycystic Kidney Disease, AdultUnited States
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Western Sydney Local Health DistrictWestmead Institute for Medical ResearchCompletedHypertension | Endothelial Dysfunction | Autosomal Dominant Polycystic KidneyAustralia
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Galapagos NVTerminatedAutosomal Dominant Polycystic Kidney DiseaseBelgium, Netherlands, Italy, Spain, Czechia, Germany, Poland
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University of Colorado, DenverPKD FoundationCompletedPolycystic Kidney, Autosomal DominantUnited States
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Palladio BiosciencesCentessa Pharmaceuticals plcTerminatedADPKD | Polycystic Kidney Disease, AdultUnited States
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Palladio BiosciencesCentessa Pharmaceuticals plcTerminatedAutosomal Dominant Polycystic Kidney | ADPKDUnited States, Spain, Hungary, United Kingdom, Australia, Bulgaria, Poland, Turkey
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Kadmon, a Sanofi CompanyCompletedAutosomal Dominant Polycystic Kidney | ADPKDUnited States
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University of Colorado, DenverCompletedPolycystic Kidney, Autosomal Dominant | Polycystic Kidney Disease, AdultUnited States
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Mayo ClinicNational Eye Institute (NEI)CompletedRetinal Disease | Best Vitelliform Macular Dystrophy | Bestrophinopathy | Adult Onset Vitelliform Macular Dystrophy | Autosomal Dominant VitreoretinalchoroidopathyUnited States
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Otsuka Pharmaceutical Development & Commercialization...CompletedAutosomal Dominant Polycystic Kidney Disease (ADPKD)Germany, Italy, Belgium, United Kingdom
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Juan PascualNational Institute of Neurological Disorders and Stroke (NINDS)CompletedGlucose Metabolism Disorders | Epilepsy | Glucose Transporter Type 1 Deficiency Syndrome | Glut1 Deficiency Syndrome 1, Autosomal Recessive | Glucose Transporter Protein Type 1 Deficiency Syndrome | Glucose Transport Defect | GLUT1DS1United States
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Palladio BiosciencesCompletedAutosomal Dominant Polycystic Kidney DiseaseUnited States
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Genzyme, a Sanofi CompanyTerminatedPolycystic Kidney, Autosomal DominantBelgium, Germany, Czechia, United States, Italy, Poland, Argentina, Australia, Austria, Canada, China, Denmark, France, Israel, Japan, Korea, Republic of, Netherlands, Portugal, Romania, Spain, Taiwan, Turkey, United Kingdom