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Search clinical trials for: genetic disorders
Total 154527 results
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University of RochesterNot yet recruitingAge-Related Macular Degeneration | Retinitis Pigmentosa | Retinal Dystrophies | Alcohol Use Disorder | Stargardt DiseaseUnited States
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Kathelijn FischerRadboud University Medical Center; University Medical Center Groningen; Maastricht... and other collaboratorsRecruitingAdolescent | Child | Hemophilia A With Inhibitor | Adult | Hemophilia A Without Inhibitor | Hemophilia A, SevereNetherlands
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Qilu Hospital of Shandong UniversityRecruitingChild | Williams Syndrome | Neurodevelopmental DelayChina
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Noema Pharma AGNot yet recruiting
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Suzhou Alphamab Co., Ltd.RecruitingHemophilia A With Inhibitor | Hemophilia B With InhibitorChina
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University of California, Los AngelesRecruitingTuberous SclerosisUnited States
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University of ValenciaAsociación de Fibrosis Quística - Comunidad ValencianaNot yet recruiting
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M.D. Anderson Cancer CenterNovartis PharmaceuticalsNot yet recruitingAcute Lymphoblastic Leukemia | Philadelphia Chromosome-PositiveUnited States
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Forge Biologics, IncNot yet recruitingKrabbe DiseaseUnited States
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Halic UniversityRecruitingCystic Fibrosis | Cystic Fibrosis in ChildrenTurkey
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Massachusetts General HospitalJohns Hopkins UniversityNot yet recruitingNeurofibromatosis 1 | Neurofibromas, CutaneousUnited States
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Inozyme PharmaGACI GlobalNot yet recruitingATP-Binding Cassette Subfamily C Member 6 Deficiency | Ectonucleotide Pyrophosphatase/Phosphodiesterase 1 Deficiency
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Marco CapogrossoRoche-GenentechNot yet recruitingSpinal Muscular Atrophy | Spinal Muscular Atrophy Type 3 | SMA | Spinal Muscular Atrophy Type II | Spinal Muscular Atrophy 4United States
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ARTHEx Biotech S.L.Not yet recruitingMyotonic Dystrophy 1
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metaX Institut fuer Diatetik GmbHGreat Ormond Street Hospital for Children NHS Foundation Trust; Birmingham...Not yet recruitingAlkaptonuria | Homocystine; Metabolic Disorder | Tyrosinemia, Type I | Tyrosinemia, Type II | Tyrosinemia, Type III | MSUD (Maple Syrup Urine Disease)
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Chia Tai Tianqing Pharmaceutical Group Nanjing...Not yet recruiting
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Spark Therapeutics, Inc.Recruiting
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John ElfarNot yet recruitingCarpal Tunnel Syndrome | Compression Neuropathy
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Lise AksglædeNot yet recruitingKlinefelter Syndrome
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Istituto Auxologico ItalianoRecruitingShort Stature | Short; Stature, PsychosocialItaly
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Istituto Auxologico ItalianoRecruitingPrader-Willi SyndromeItaly
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IRCCS Fondazione Stella MarisRecruitingFragile X SyndromeItaly
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University of ÉvoraUniversidade Nova de Lisboa; Comprehensive Health Research Centre; Unidade Local... and other collaboratorsRecruitingVitamin D Deficiency | PregnancyPortugal
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Suzhou Municipal HospitalNot yet recruitingFamilial Hypercholesterolemia | Refractory Hypercholesterolemia
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Halic UniversityRecruitingCystic Fibrosis | ParentsTurkey
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Steen Hvitfeldt PoulsenNovo Nordisk A/SRecruitingQuality of Life | Transthyretin Amyloidosis | Transthyretin Amyloid Cardiomyopathy | Wild-Type Transthyretin-Related (ATTR)AmyloidosisDenmark
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University of FloridaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)Not yet recruitingMuscular Dystrophy | Exercise | Duchenne Muscular Dystrophy | Vasodilation | DMD | Muscular Dystrophy in Children | Duchenne Disease
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Ondokuz Mayıs UniversityRecruitingQuality of Life | Urinary Incontinence | Menopause | Wolman Disease | Psychological Well-BeingTurkey
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Australasian Leukaemia and Lymphoma GroupNot yet recruitingHigh-grade B-cell Lymphoma | DLBCL - Diffuse Large B Cell Lymphoma | High Grade B-Cell Lymphoma With MYC and BCL2 or BCL6 Rearrangements | DLBCL, Nos Genetic Subtypes | High Grade B-Cell Lymphoma, Not Otherwise Specified | Follicular Large Cell Lymphoma, Relapsed | Follicular Large Cell Lymphoma
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Staidson (Beijing) Biopharmaceuticals Co., LtdRecruiting
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Assistance Publique - Hôpitaux de ParisNot yet recruiting
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Asklepios Biopharmaceutical, Inc.BayerNot yet recruiting
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Oslo University HospitalRecruitingCystic Fibrosis in ChildrenNorway
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Specila hospital for cerebral palsy and developmental...FRAXA Research FoundationRecruitingFragile X SyndromeSerbia
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BioMarin PharmaceuticalRecruitingDuchenne Muscular DystrophySpain, United Kingdom
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Perha PharmaceuticalsGöteborg University; Proteas BioanalyticsRecruiting
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Duke UniversityNational Human Genome Research Institute (NHGRI)Not yet recruitingLiver Diseases | Cardiovascular Diseases | Cancer | HyperthermiaUnited States
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University Hospital, ToulouseNot yet recruitingPrader-Willi SyndromeFrance
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The Affiliated Hospital of Xuzhou Medical UniversityRecruitingType 2 Diabetes Mellitus | Genetic Mutations | Gene Polymorphisms | Susceptibility, GeneticChina
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Radboud University Medical CenterEnzyre B.V.Not yet recruiting
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Novartis PharmaceuticalsRecruitingHypercholesterolaemia | Familial HypercholesterolaemiaJapan
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Xinhua Hospital, Shanghai Jiao Tong University...Shanghai Vitalgen BioPharma Co., Ltd.RecruitingType II Gaucher DiseaseChina
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Karolinska InstitutetRecruitingTourette Syndrome | Chronic Tic DisorderSweden
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Sarepta Therapeutics, Inc.RecruitingDuchenne Muscular DystrophyUnited States
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UniQure Biopharma B.V.RecruitingFabry DiseaseUnited States
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Investigación en Hemofilia y FisioterapiaRecruiting
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S.LAB (SOLOWAYS)Center of New Medical TechnologiesRecruiting
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Investigación en Hemofilia y FisioterapiaRecruiting
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Université de SherbrookeCanadian Institutes of Health Research (CIHR); Centre de recherche du Centre... and other collaboratorsNot yet recruiting
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Central Hospital, Nancy, FranceRecruiting