- ICH GCP
- US Clinical Trials Registry
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Search clinical trials for: serotype Rh10 AAV
Total 443 results
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University College Hospital GalwayStewart R Walsh; Wael Tawfick; Thomas A Aherne; Mark Twyford; Marie O'ShaughnessyRecruiting
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Mridula George, MDNational Cancer Institute (NCI); Incyte Corporation; Oncolytics BiotechRecruitingAnatomic Stage IV Breast Cancer AJCC v8 | Prognostic Stage IV Breast Cancer AJCC v8 | Triple-negative Breast Cancer | Metastatic Triple-Negative Breast Carcinoma | Locally Advanced Breast CarcinomaUnited States
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Prevail TherapeuticsEli Lilly and CompanyRecruitingFrontotemporal DementiaUnited States, Australia, Belgium, Spain, United Kingdom, France
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Tianjin Anding HospitalRecruitingBPSD | Amisulpride | Olanzapine | Dementia of the Alzheimer TypeChina
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Prevail TherapeuticsEli Lilly and CompanyRecruitingParkinson DiseaseUnited States, Israel
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Aspa TherapeuticsRecruiting
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Brigham and Women's HospitalUnited States Department of Defense; Massachusetts Institute of Technology; Walter...Recruiting
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National Human Genome Research Institute (NHGRI)Sio Gene TherapiesRecruitingGangliosidosis | Lysosomal Diseases | GM1United States
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eyeDNA TherapeuticsRecruitingRetinitis PigmentosaFrance
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GenSight BiologicsRecruitingNon-syndromic Retinitis PigmentosaUnited States, France, United Kingdom
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University College, LondonMedical Research CouncilRecruiting
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Krzysztof BankiewiczNational Institute of Neurological Disorders and Stroke (NINDS); University...Recruiting
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Weill Medical College of Cornell UniversityNational Institute on Drug Abuse (NIDA)RecruitingCocaine DependenceUnited States
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Shirley Ryan AbilityLabCoapt, LLCActive, not recruitingLower Limb Amputation Below Knee (Injury) | Lower Limb Amputation Above Knee (Injury) | Amputation | Phantom Limb Pain | Phantom Pain | Phantom Sensation | Lower Limb Amputation Knee | Lower Limb Amputation at Ankle (Injury) | Upper Limb Amputation at the Hand | Upper Limb Amputation at the Wrist | Upper... and other conditionsUnited States
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Janssen Research & Development, LLCJanssen Research & Development, LLCActive, not recruitingX-Linked Retinitis PigmentosaBelgium, Canada, United States, Israel, United Kingdom, Denmark, France, Italy, Netherlands, Switzerland, Spain
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Janssen Research & Development, LLCJanssen Research & Development, LLCActive, not recruitingX-Linked Retinitis PigmentosaUnited States, Canada, Israel, United Kingdom, Denmark, France, Belgium, Italy, Netherlands, Switzerland, Spain
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PfizerActive, not recruiting
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Zuyderland Medisch CentrumCompletedBreast CancerNetherlands
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NightstaRx Ltd, a Biogen CompanyEnrolling by invitationChoroideremia | X-Linked Retinitis PigmentosaUnited States, United Kingdom, Netherlands, Germany, France, Brazil, Canada, Denmark, Finland
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BayerUltragenix pharmaceuticalActive, not recruitingHemophilia ANetherlands, United States, Germany, United Kingdom, France, Bulgaria
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Forge Biologics, IncActive, not recruiting
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Janssen Research & Development, LLCActive, not recruitingX-Linked Retinitis PigmentosaUnited States, United Kingdom
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CSL BehringEnrolling by invitation
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Novo Nordisk A/SEnrolling by invitationDiabetes Mellitus, Type 2Finland, France
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Janssen Research & Development, LLCSuspendedHealthyUnited States, United Kingdom
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Beacon TherapeuticsActive, not recruitingX-Linked Retinitis PigmentosaUnited States
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National Cancer Institute (NCI)CompletedAnemia | Refractory Multiple Myeloma | Recurrent Multiple MyelomaUnited States
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CSL BehringActive, not recruiting
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Excision BioTherapeuticsActive, not recruiting
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4D Molecular TherapeuticsActive, not recruitingChoroideremiaUnited States
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Sangamo TherapeuticsActive, not recruitingFabry DiseaseUnited States, United Kingdom, Taiwan, Australia, Germany, Italy, Canada
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University of California, San DiegoUnited States Department of DefenseCompleted
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Mayo ClinicGenentech, Inc.TerminatedMicroscopic Polyangiitis | Granulomatosis With Polyangiitis | ANCA Associated VasculitisUnited States
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National Institute of Neurological Disorders and...Completed
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MeiraGTx UK II LtdSyne Qua Non Limited; EMAS PharmaCompletedAchromatopsiaUnited Kingdom, United States
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Ultragenyx Pharmaceutical IncActive, not recruitingGlycogen Storage Disease Type IA | Von Gierke's Disease (GSD Type Ia)Netherlands, United States, Canada, Spain
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VegaVect, Inc.National Eye Institute (NEI)Active, not recruiting
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Janssen Pharmaceutical K.K.Terminated
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BioMarin PharmaceuticalActive, not recruitingHemophilia A | Gene Therapy | Blood Disorder | Clotting DisordersTaiwan, Korea, Republic of, United Kingdom, South Africa
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BioMarin PharmaceuticalCompleted
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National Cancer Institute (NCI)Active, not recruitingGanglioneuroblastoma | High Risk NeuroblastomaUnited States, New Zealand, Australia
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MeiraGTx, LLCActive, not recruitingRadiation-induced XerostomiaUnited States, Canada
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Spark Therapeutics, Inc.Children's Hospital of Philadelphia; University of IowaActive, not recruitingLeber Congenital Amaurosis | Inherited Retinal Dystrophy Due to RPE65 MutationsUnited States
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MeiraGTx UK II LtdSyne Qua Non LimitedCompletedEye Diseases | Retinal Diseases | Eye Diseases, Hereditary | Leber Congenital Amaurosis (LCA)United States, United Kingdom
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Beacon TherapeuticsActive, not recruitingX-Linked Retinitis PigmentosaUnited States
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Nanoscope Therapeutics Inc.CompletedEye Diseases | Retinal Degeneration | Retinal Diseases | Retinitis Pigmentosa | Retinitis | Eye Diseases, Hereditary | Retinal DystrophiesUnited States, Puerto Rico
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Beacon TherapeuticsEnrolling by invitationX-Linked Retinitis PigmentosaUnited States
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Prevail TherapeuticsEli Lilly and CompanyActive, not recruitingGaucher Disease, Type 2United States, United Kingdom
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AmgenCompletedMigraine HeadacheUnited States, Austria, Australia, Czechia, Finland, France, Hungary, Italy, Poland, Portugal, Spain, United Kingdom
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MeiraGTx, LLCActive, not recruitingParkinson DiseaseUnited States