- ICH GCP
- US Clinical Trials Registry
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Search clinical trials for: Inborn Errors
Total 15937 results
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University of UtahCompleted
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Instituto de Cardiologia do Rio Grande do SulFundação de Amparo à Pesquisa do Estado do Rio Grande do Sul, Brazil; Conselho...CompletedAutologous Transplantation of Bone Marrow Mononuclear Stem-Cells for Dilated Cardiomyopathy (SDILCM)Dilated CardiomyopathyBrazil
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PharmaxisCompleted
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Azienda Ospedaliera V. CervelloCompletedBeta-Thalassemia | Thalassemia MajorItaly
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University Hospital, Strasbourg, FranceCompletedBardet-Biedl Syndrome | Orphan DiseasesFrance
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Universita di VeronaCompleted
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University of Medicine and Dentistry of New JerseyGenentech, Inc.Completed
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National Center for Complementary and Integrative...Completed
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PfizerCompletedGrowth Hormone Deficiency | Growth RetardationFrance
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Asan Medical CenterSamsung Medical Center; Seoul National University Hospital; Kyunghee University...UnknownNon-Infectious Uveitis | Ocular Behcet's Disease, | Refractory UveitisKorea, Republic of
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National Taiwan University HospitalNational Taiwan UniversityUnknownComputerized Physician Order EntryTaiwan
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Academisch Medisch Centrum - Universiteit van Amsterdam...CompletedCharcot-Marie-Tooth Disease | Hereditary Motor and Sensory NeuropathiesNetherlands
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University of California, Los AngelesScios, Inc.Completed
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St. Jude Children's Research HospitalCompletedOsteogenesis ImperfectaUnited States
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Tehran University of Medical SciencesCompletedBehcet's SyndromeIran, Islamic Republic of
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University of BernHoffmann-La Roche; Swiss National Science FoundationCompleted
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University of BialystokUnknown
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Genentech, Inc.Completed
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University of Sao PauloCompleted
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St. Jude Children's Research HospitalGlaxoSmithKline; National Institutes of Health (NIH)CompletedWilms TumorUnited States, Canada
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Sunnybrook Health Sciences CentreOrtho Biotech, Inc.Terminated
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Aerovance, Inc.CompletedAtopic EczemaUnited Kingdom
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Dartmouth-Hitchcock Medical CenterBEST research collaborativeCompletedBlood TransfusionNorway, United States, Australia, Canada, United Kingdom, Brazil
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Technische Universität DresdenCompleted
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Tehran University of Medical SciencesHoffmann-La RocheCompletedBehcet's SyndromeIran, Islamic Republic of
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Cardiff UniversityWyeth is now a wholly owned subsidiary of Pfizer; University of Nottingham; Royal... and other collaboratorsUnknownTuberous Sclerosis | LymphangioleiomyomatosisUnited Kingdom
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LEO PharmaCompletedAtopic DermatitisUnited Kingdom, Finland, Canada, Denmark
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NovartisCompleted
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Radboud University Medical CenterZonMw: The Netherlands Organisation for Health Research and DevelopmentUnknownColorectal Neoplasms | Hereditary Nonpolyposis Colorectal CancerNetherlands
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Wyeth is now a wholly owned subsidiary of PfizerCompleted
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Wyeth is now a wholly owned subsidiary of PfizerCompletedHemophilia A
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Wyeth is now a wholly owned subsidiary of PfizerCompletedHemophilia APoland, Belgium, France, Italy, Spain, United States, Australia, Netherlands, New Zealand, Sweden, Germany, Finland, Hungary
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Federal University of São PauloCSL BehringCompletedCommon Variable Immunodeficiency | AgammaglobulinemiaBrazil
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Far Eastern Memorial HospitalUnknown
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University of JenaCompletedAtopic DermatitisGermany
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Sheba Medical CenterUnknownFamilial Mediterranean FeverIsrael
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Institute of Child HealthGreat Ormond Street Hospital for Children NHS Foundation TrustCompletedAtaxia Telangiectasia (AT)United Kingdom
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PfizerTerminatedBrain Injuries | Growth Hormone Deficiency DwarfismUnited States
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Walter Reed Army Medical CenterUnited States Naval Medical Center, San DiegoCompleted
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Walter Reed Army Medical CenterCompleted
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Walter Reed Army Medical CenterCompleted
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Italian Society of CardiologyUnknownIschemic Heart Disease | Chronic Heart Failure | Dilated CardiomyopathyItaly
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IcagenMcNeil Consumer & Specialty Pharmaceuticals, a Division of McNeil-PPC, Inc.TerminatedSickle Cell DiseaseUnited States, France, United Kingdom, Brazil, Jamaica, Trinidad and Tobago
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State University of New York - Upstate Medical...Completed
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University of MelbourneCIBA VISIONCompletedMyopia | HyperopiaAustralia
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University Hospital Inselspital, BerneHaag-Streit AGCompletedCataract | Myopia | Hyperopia | Aphakia | PseudophakiaSwitzerland
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Samsung Medical CenterCompleted
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McGill University Health Centre/Research Institute...Unknown
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University of TurkuUnknownUnverricht-Lundborg SyndromeFinland
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Seattle Children's HospitalCystic Fibrosis FoundationCompletedCystic Fibrosis | Chronic BronchitisUnited States