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Search clinical trials for: Autosomal recessive congenital ichthyosis
Total 9321 results
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The Rogosin InstituteWeill Medical College of Cornell UniversityCompletedAutosomal Dominant Polycystic KidneyUnited States
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Abeona Therapeutics, IncNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedEpidermolysis Bullosa | Epidermolysis Bullosa DystrophicaUnited States
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Weill Medical College of Cornell UniversityThe Rogosin InstituteEnrolling by invitationAutosomal Dominant Polycystic Kidney DiseaseUnited States
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Mayne Pharma International Pty LtdTerminatedLamellar IchthyosisUnited States, Spain, Canada, Germany, France, Australia, Israel, Ukraine, United Kingdom
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Élise DuchesneMuscular Dystrophy CanadaCompletedAutosomal Recessive Spastic Ataxia of Charlevoix-SaguenayCanada
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Taipei Medical University Shuang Ho HospitalUniversity of Southern CaliforniaEnrolling by invitationChronic Kidney Diseases | Autosomal Dominant Polycystic Kidney DiseaseTaiwan
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Daiichi Sankyo, Inc.CompletedNetherton SyndromeUnited States
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Palladio BiosciencesCentessa Pharmaceuticals plcTerminatedPolycystic Kidney Disease, AdultUnited States
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Western Sydney Local Health DistrictWestmead Institute for Medical ResearchCompletedHypertension | Endothelial Dysfunction | Autosomal Dominant Polycystic KidneyAustralia
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Galapagos NVTerminatedAutosomal Dominant Polycystic Kidney DiseaseBelgium, Netherlands, Italy, Spain, Czechia, Germany, Poland
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University of Colorado, DenverPKD FoundationCompletedPolycystic Kidney, Autosomal DominantUnited States
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Palladio BiosciencesCentessa Pharmaceuticals plcTerminatedADPKD | Polycystic Kidney Disease, AdultUnited States
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Daiichi Sankyo, Inc.Completed
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AnaptysBio, Inc.Terminated
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Krystal Biotech, Inc.CompletedDystrophic Epidermolysis Bullosa | Recessive Dystrophic Epidermolysis Bullosa | Dominant Dystrophic Epidermolysis BullosaUnited States
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CHU de Quebec-Universite LavalThe Hospital for Sick ChildrenActive, not recruitingEpidermolysis Bullosa DystrophicaCanada
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Aldeyra Therapeutics, Inc.CompletedSjogren-Larsson SyndromeUnited States
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Castle Creek Biosciences, LLC.TerminatedEpidermolysis Bullosa Dystrophica, RecessiveUnited States
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Palladio BiosciencesCentessa Pharmaceuticals plcTerminatedAutosomal Dominant Polycystic Kidney | ADPKDUnited States, Spain, Hungary, United Kingdom, Australia, Bulgaria, Poland, Turkey
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Kadmon, a Sanofi CompanyCompletedAutosomal Dominant Polycystic Kidney | ADPKDUnited States
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University of Colorado, DenverCompletedPolycystic Kidney, Autosomal Dominant | Polycystic Kidney Disease, AdultUnited States
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Otsuka Pharmaceutical Development & Commercialization...CompletedAutosomal Dominant Polycystic Kidney Disease (ADPKD)Germany, Italy, Belgium, United Kingdom
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Juan PascualNational Institute of Neurological Disorders and Stroke (NINDS)CompletedGlucose Metabolism Disorders | Epilepsy | Glucose Transporter Type 1 Deficiency Syndrome | Glut1 Deficiency Syndrome 1, Autosomal Recessive | Glucose Transporter Protein Type 1 Deficiency Syndrome | Glucose Transport Defect | GLUT1DS1United States
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Aldeyra Therapeutics, Inc.CompletedSjögren-Larsson SyndromeUnited States
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Abeona Therapeutics, IncCompletedEpidermolysis Bullosa | Recessive Dystrophic Epidermolysis BullosaUnited States
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Palladio BiosciencesCompletedAutosomal Dominant Polycystic Kidney DiseaseUnited States
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Phoenix Tissue Repair, Inc.Phoenix Tissue Repair, a BridgeBio companyCompletedRecessive Dystrophic Epidermolysis BullosaUnited States
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Genzyme, a Sanofi CompanyTerminatedPolycystic Kidney, Autosomal DominantBelgium, Germany, Czechia, United States, Italy, Poland, Argentina, Australia, Austria, Canada, China, Denmark, France, Israel, Japan, Korea, Republic of, Netherlands, Portugal, Romania, Spain, Taiwan, Turkey, United Kingdom
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Kadmon, a Sanofi CompanyCompletedPolycystic Kidney, Autosomal DominantUnited States
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Mario Negri Institute for Pharmacological ResearchOtsuka Pharmaceutical Italy S.r.l.CompletedAutosomal Dominant Polycystic Kidney DiseaseItaly
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AceLink Therapeutics, Inc.Novotech (Australia) Pty LimitedCompletedAutosomal Dominant Polycystic KidneyAustralia
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RHEACELL GmbH & Co. KGFGK Clinical Research GmbH; Ticeba GmbH; Granzer Regulatory Consulting & ServicesCompletedRecessive Dystrophic Epidermolysis BullosaUnited States, Austria, France, Germany, United Kingdom
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SanofiTerminatedCongenital Cystic Kidney DiseaseGermany, Spain, United States, Australia, Belgium, Japan, Korea, Republic of, Netherlands
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National Institute of Arthritis and Musculoskeletal...CompletedIchthyosis | Ichthyosis, X-Linked | Ichthyosis, Lamellar | Darier Disease | Hailey-Hailey Disease | Hyperkeratosis, Epidermolytic | KeratodermaUnited States
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National Cancer Institute (NCI)WithdrawnHematopoietic and Lymphoid Cell Neoplasm | Lynch Syndrome | Refractory Lymphoma | Refractory Malignant Solid Neoplasm | Recurrent Lymphoma | Recurrent Malignant Solid Neoplasm | Recurrent Neuroblastoma | Refractory Neuroblastoma | Recurrent Primary Central Nervous System Neoplasm | Refractory Primary Central... and other conditionsUnited States, Canada
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Timber Pharmceuticals LLCCompletedCongenital IchthyosisUnited States, Australia
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University of CologneCompleted
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Kyongtae Ty Bae, M.D., Ph.D.University of Maryland, Baltimore; United States Department of Defense; University... and other collaboratorsCompletedPolycystic Kidney, Autosomal DominantUnited States
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Azienda Ospedaliero-Universitaria Consorziale Policlinico...Institute of Biomembranes, Bioenergetics and Molecular Biotechnologies; Istituti... and other collaboratorsCompletedAutosomal Dominant Polycystic Kidney Disease (ADPKD) | IgA Nephropathy (IgAN) | Diabetic Kidney Disease (DKD) | Advanced-Chronic Kidney Disease (CKD)Italy
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Rocket Pharmaceuticals Inc.California Institute for Regenerative Medicine (CIRM)TerminatedInfantile Malignant OsteopetrosisUnited States
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Kerecis Ltd.MedStar HealthCompleted
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Kerecis Ltd.Active, not recruiting
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Korea Otsuka Pharmaceutical Co., Ltd.CompletedAutosomal Dominant Polycystic Kidney Disease (ADPKD)Korea, Republic of
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Kadmon Corporation, LLCTerminatedAutosomal Dominant Polycystic Kidney Disease (ADPKD)United States
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ProQR TherapeuticsActive, not recruitingEye Diseases | Retinitis | Eye Diseases, Hereditary | Retinal Dystrophies | Vision Disorders | Retinal Disease | Autosomal Dominant Retinitis Pigmentosa | Vision TunnelUnited States
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Genzyme, a Sanofi CompanyCompletedHealthy Volunteers | Polycystic Kidney, Autosomal DominantUnited States
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University of Colorado, DenverCompletedPolycystic Kidney, Autosomal DominantUnited States
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University of Colorado, DenverNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)CompletedPolycystic Kidney, Autosomal DominantUnited States
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Holostem Terapie Avanzate s.r.l.Paracelsus Medical UniversityTerminatedRecessive Dystrophic Epidermolysis BullosaAustria
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Regulus Therapeutics Inc.CompletedPolycystic Kidney Disease, Autosomal DominantUnited States