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Search clinical trials for: Errors
Total 4715 results
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Alcon ResearchRecruitingPresbyopia | Astigmatism | AphakiaSpain
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Verve Therapeutics, Inc.RecruitingHeterozygous Familial Hypercholesterolemia | Premature Coronary Heart DiseaseUnited Kingdom, Canada
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He HuangLingyi Biotech Co., Ltd.Recruiting
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National Institute for Mother and Child Health...Marie Curie Emergency Children's Hospital, Bucharest; Victor Gomoiu Children...RecruitingChronic Granulomatous DiseaseRomania
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The Hong Kong Polytechnic UniversityHOYA Lamphun Ltd; Centre for Eye and Vision ResearchRecruiting
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University of BonnRecruitingHypophosphatasiaGermany
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Qilu Pharmaceutical Co., Ltd.Recruiting
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Astellas Gene TherapiesRecruitingPompe Disease (Late-onset)United States, Spain, France, Taiwan, Italy, Australia
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Orchard TherapeuticsRecruitingMPS-IH (Hurler Syndrome)Netherlands, United States, Italy, United Kingdom
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Ionis Pharmaceuticals, Inc.RecruitingPelizaeus-Merzbacher DiseaseFrance, Netherlands, United States, Germany
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ModernaTX, Inc.RecruitingPhenylketonuriaUnited States, Australia
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Peking University Third HospitalNot yet recruiting
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Jiangsu HengRui Medicine Co., Ltd.Not yet recruitingGout With Hyperuricemia in Adults
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Assistance Publique - Hôpitaux de ParisRecruiting
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nthalmic Pty LtdZhong Jing Wei Shi (Suzhou) Optical Technology Ltd.Recruiting
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Azienda Ospedaliero-Universitaria di ModenaRecruitingIron Overload | Hemochromatosis | Thalassemia Major | Thalassemia Intermedia | EndocrinopathyItaly
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McMaster UniversityNot yet recruitingObesity | Lysosomal Storage Diseases | Muscle Loss | Glycogen Storage Disease Type II | Pompe Disease | Nutrition Poor | Glycogen Storage Disease Type II, Adult | Glycogen Storage Disease Type II Late Onset
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Intellia TherapeuticsRegeneron PharmaceuticalsRecruitingTransthyretin Amyloidosis (ATTR) With CardiomyopathyUnited States, Australia, United Kingdom, New Zealand, Canada
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Martin DichgansRecruitingCerebral Amyloid AngiopathyGermany
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First Affiliated Hospital Xi'an Jiaotong UniversityRecruitingHomozygous Familial HypercholesterolemiaChina
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The University of New South WalesUniversity of California, Berkeley; State University of New York College of... and other collaboratorsNot yet recruitingMyopiaUnited States, Australia
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Amicus TherapeuticsRecruitingPompe DiseaseUnited States, United Kingdom, Germany
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Lysosomal and Rare Disorders Research and Treatment...RecruitingBone Diseases | Gaucher DiseaseUnited States
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AceLink Therapeutics, Inc.Tigermed Consulting Co., LtdRecruiting
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Verve Therapeutics, Inc.Not yet recruitingHypercholesterolemia | Atherosclerotic Cardiovascular Disease | Heterozygous Familial HypercholesterolemiaNew Zealand, United Kingdom
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Children's Hospital Medical Center, CincinnatiRecruiting
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Novozymes A/SAnalyze & RealizeNot yet recruiting
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Centre Hospitalier Universitaire de la RéunionRecruitingLipodystrophy | Dunnigan SyndromeRéunion
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National Human Genome Research Institute (NHGRI)RecruitingMetabolic Disease | Purine-Pyrimidine Metabolism | AICDA, OMIM *605257, Immunodeficiency With Hyper-IgM, Type 2; HIGM2 | UNG, OMIM *191525, Hyper-IgM Syndrome 5 | NT5C3A<TAB>, OMIM *606224, Anemia, Hemolytic, Due to UMPH1 Deficiency | UMPS, OMIM *613891, Orotic Aciduria | DHODH, OMIM *126064,... and other conditionsUnited States
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Rocket Pharmaceuticals Inc.RecruitingDanon DiseaseUnited States
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Westfälische Wilhelms-Universität MünsterChiesi GmbHRecruiting
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JCR Pharmaceuticals Co., Ltd.RecruitingMucopolysaccharidosis III-AGermany
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University Hospital PadovaRecruitingHypertension | Essential Hypertension | Hyperaldosteronism | Aldosteronism | Conn Adenoma | Aldosterone Disorder | Aldosterone-producing Adenoma | Bilateral Adrenal HyperplasiaItaly
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Beijing Airdoc Technology Co., Ltd.Recruiting
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Kubota Vision Inc.Not yet recruitingMyopia | Vision Disorders | Myopia, Progressive
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Alexion Pharmaceuticals, Inc.RecruitingHypophosphatasiaAustralia, United States, Japan, Germany, Turkey, Italy, India, France, United Kingdom, Argentina, Canada
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ISU Abxis Co., Ltd.RecruitingFabry DiseaseKorea, Republic of
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Alexion Pharmaceuticals, Inc.RecruitingHypophosphatasiaIsrael, Korea, Republic of, Taiwan, Sweden, Germany, Italy, Turkey, China, Poland, United States, France, Australia, Thailand, United Kingdom, Mexico, Vietnam, Argentina, Belgium, Brazil, Canada, Spain
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Alexion Pharmaceuticals, Inc.RecruitingHypophosphatasiaItaly, Spain, Israel, Korea, Republic of, Belgium, Germany, United States, China, France, Taiwan, Austria, Japan, India, Australia, Argentina, Poland, Turkey, Brazil, Canada, Thailand, United Kingdom, Slovakia, Czechia
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Islamic Hospital, JordanJordan University of Science and Technology; Yarmouk UniversityRecruitingRefractive Errors | Vision Disorders | Esotropia | CycloplegiaJordan, Qatar
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Johnson & Johnson Vision Care, Inc.Recruiting
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He Eye HospitalNot yet recruiting
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Jerry Vockley, MD, PhDUltragenyx Pharmaceutical IncRecruitingMedium-chain Acyl-CoA Dehydrogenase DeficiencyUnited States
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Jerry Vockley, MD, PhDAcer Therapeutics Inc.RecruitingMedium-chain Acyl-CoA Dehydrogenase DeficiencyUnited States
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Tasly Pharmaceutical Group Co., LtdNot yet recruiting
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UK Kidney AssociationRecruitingVasculitis | AL Amyloidosis | Tuberous Sclerosis | Fabry Disease | Cystinuria | Focal Segmental Glomerulosclerosis | IgA Nephropathy | Bartter Syndrome | Pure Red Cell Aplasia | Membranous Nephropathy | Atypical Hemolytic Uremic Syndrome | Autosomal Dominant Polycystic Kidney Disease | Cystinosis | Nephronophthisis | BK Nephropathy and other conditionsUnited Kingdom
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University of MinnesotaInnovations for Poverty Action; Peek Vision; Vision ActionRecruiting
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Lysosomal and Rare Disorders Research and Treatment...Recruiting