- ICH GCP
- US Clinical Trials Registry
- Search trials
Search clinical trials for: Hereditary Transthyretin-mediated (hATTR) Amyloidosis
Total 3458 results
-
Central Hospital, Nancy, FranceRecruiting
-
Medical University of GrazMedical University InnsbruckRecruitingAmyloid Cardiomyopathy | Wild Type ATTR AmyloidosisAustria
-
Massachusetts General HospitalPatient-Centered Outcomes Research InstituteNot yet recruitingNeurofibromatosis 1United States
-
University of MiamiFlorida lions eye bankNot yet recruitingCorneal Edema | Fuchs' Endothelial DystrophyUnited States
-
Cure HHTUniversity of Colorado, Denver; Massachusetts General Hospital; Mayo Clinic; Children... and other collaboratorsRecruitingArteriovenous Malformations | Epistaxis | Hereditary Hemorrhagic Telangiectasia | GastroIntestinal Bleeding | Telangiectasia | Vascular Malformation | Cerebral Arteriovenous MalformationsUnited States
-
Paolo MilaniRecruitingAmyloidosis | Amyloidosis Cardiac | ATTR Amyloidosis Wild TypeItaly
-
AmgenRecruiting
-
Assiut UniversityNot yet recruitingNephrolithiasis, Glomerulonephritis, Amyloidosis,AKI, CKD, Tubuli Interstitial | Urinary System Disorders in IBD Patients
-
Mahidol UniversityRecruitingRetinitis PigmentosaThailand
-
Rolfs Consulting und Verwaltungs-GmbH (RCV)Rhythm Pharmaceuticals, Inc.RecruitingCognitive Impairment | Hyperphagia | Obesity, Childhood | Bardet-Biedl Syndrome | Polydactyly | Retinopathy | Syndactyly | POMC DeficiencyGermany
-
Assiut UniversityNot yet recruiting
-
Assistance Publique - Hôpitaux de ParisRecruitingHereditary Spastic ParaparesisFrance
-
Swedish Orphan BiovitrumRecruitingHereditary Tyrosinemia, Type IChina
-
Nanjing University School of MedicineRecruiting
-
Lassen Therapeutics Inc.RecruitingEye Diseases | Endocrine System Diseases | Thyroid Eye Disease | Graves Ophthalmopathy | Orbital Diseases | Thyroid Associated Ophthalmopathy | Graves Orbitopathy | ProptosisUnited States, United Kingdom, Spain
-
bluebird bioCenter for International Blood and Marrow Transplant ResearchRecruitingCerebral Adrenoleukodystrophy (CALD)United States
-
University College, LondonNot yet recruiting
-
National Cancer Institute (NCI)Not yet recruitingNeurofibromatosis 1 | Nerve Sheath NeoplasmsUnited States
-
Samsung Medical CenterNot yet recruitingCharcot-Marie-Tooth Disease, Type 1
-
Tampere University HospitalTampere UniversityRecruitingLynch Syndrome | Urothelial CarcinomaCanada, Finland
-
Hospital Universitari Vall d'Hebron Research InstituteErasme University Hospital; Cyprus Institute of Neurology and Genetics; EuroBloodNet...RecruitingIron Metabolism Disorders | Sickle Cell Disease | Thalassemia | Hemolytic; Anemia, Hereditary, Due to Enzyme Disorder | Anemia Due to Membrane Defect | CDA | Sideroblastic Anemia | Constitutional Aplastic Anemia | Hereditary AnemiaSpain
-
Foundation For Rare Disease ResearchInstitute for Asthma & Allergy; Virant Diagnostics, Inc.; MedBio Reference Laboratories...Not yet recruitingAngioedema | Urticaria | C1 Inhibitor Deficiency | Angioedemas, Hereditary | Mastocytosis | Indolent Systemic Mastocytosis | Systemic Mastocytoses | ACE Inhibitor-Induced Angioedema
-
IRCCS Policlinico S. MatteoRecruitingAL AmyloidosisGermany, Italy, Spain, Switzerland, Netherlands
-
New York Stem Cell Foundation Research InstituteCharcot-Marie-Tooth AssociationRecruitingHealthy | Charcot-Marie-Tooth DiseaseUnited States
-
Johns Hopkins UniversityRecruitingGranular Dystrophy, CornealUnited States
-
University Tunis El ManarRecruitingPrevalence | Heart Failure With Preserved Ejection Fraction | Diagnosis | Cardiac Amyloidosis | Echocardiography | CMR | Bone ScintigraphyTunisia
-
Baylor College of MedicineCenter for Cell and Gene Therapy, Baylor College of MedicineNot yet recruitingHepatocellular Carcinoma | Liposarcoma | Rhabdomyosarcoma | Wilms Tumor | Hepatoblastoma | Malignant Rhabdoid Tumor | Yolk Sac Tumor | Embryonal Sarcoma of LiverUnited States
-
Assistance Publique - Hôpitaux de ParisAssociation Française Contre l'Amylose (association of patients and families...Not yet recruitingCardiac Amyloidosis
-
AstraZenecaRecruiting
-
Jin Lu, MDRecruitingAL Amyloidosis | Amyloidosis; SystemicChina
-
University of Alabama at BirminghamChildren's Hospital of Philadelphia; Congressionally Directed Medical Research...Not yet recruitingNeurofibromatosis 1 | Plexiform Neurofibroma
-
Midwest Heart & Vascular SpecialistsRecruitingAL Amyloidosis | Amyloid | Cardiac Amyloidosis | Amyloidosis Cardiac | Systemic Amyloidosis | ATTR Amyloidosis Wild Type | Infiltrative Cardiomyopathy, AmyloidUnited States
-
Centre Hospitalier National d'Ophtalmologie des...Street LabNot yet recruitingRetinal Degeneration
-
Rutgers, The State University of New JerseyRecruitingBreast Cancer | Colorectal Cancer | Ovarian Cancer | Fallopian Tube Cancer | Prostate Cancer | Endometrial Cancer | Pancreas Cancer | Peritoneal CancerUnited States
-
Alexion Pharmaceuticals, Inc.RecruitingTransthyretin Amyloid CardiomyopathyUnited States, Spain, United Kingdom, Norway, Israel, China, Korea, Republic of, Belgium, France, Germany, Italy, Japan, Australia, Argentina, Austria, Taiwan, Switzerland, Canada, Sweden, Poland, Denmark, Turkey, Brazil, Netherlands, G... and more
-
Sixth Affiliated Hospital, Sun Yat-sen UniversityRecruitingHereditary DiseasesChina
-
Oscar Gerardo Arrieta RodríguezRecruiting
-
Viridian Therapeutics, Inc.Recruiting
-
St. Joseph's Hospital and Medical Center, PhoenixTexas Tech UniversityNot yet recruitingCognitive Dysfunction | Neurodegenerative Disease, Hereditary | Cognitive Impairment, Mild | Amyloid Plaque | Inflammation, Brain
-
Minoryx Therapeutics, S.L.RecruitingX-linked AdrenoleukodystrophyFrance
-
Assiut UniversityNot yet recruiting
-
AstraZenecaRecruitingNeurofibroma, PlexiformChina
-
Royal Marsden NHS Foundation TrustRecruitingLynch Syndrome | Familial Adenomatous Polyposis | Hereditary Diffuse Gastric Cancer | Peutz-Jeghers Syndrome | Cowden Syndrome | Li Fraumeni Syndrome | MutYH-associated Polyposis | SMAD4 Gene MutationUnited Kingdom
-
David M. RitterRecruitingTuberous Sclerosis Complex | LymphangioleiomyomatosisUnited States
-
Karolinska InstitutetRecruitingCardiovascular Diseases | Dyslipidemias | Hereditary DiseasesSweden
-
M.D. Anderson Cancer CenterRecruiting
-
Johns Hopkins UniversityNeurofibromatosis Therapeutic Acceleration ProgramRecruitingCutaneous Neurofibroma | NF1 | MonotherapyUnited States
-
AbbVieRecruitingImmunoglobulin Light Chain (AL) AmyloidosisJapan, United States, Australia
-
Elpida Therapeutics SPCNot yet recruitingNeuromuscular Diseases | Peripheral Neuropathy | Neuro-Degenerative Disease
-
Ionis Pharmaceuticals, Inc.RecruitingPelizaeus-Merzbacher DiseaseFrance, Netherlands