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Search clinical trials for: X-linked centronuclear myopathy
Total 445 results
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St. Jude Children's Research HospitalNational Heart, Lung, and Blood Institute (NHLBI); Assisi Foundation; California...SuspendedSevere Combined Immunodeficiency Disease, X-linkedUnited States
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Beth Israel Deaconess Medical CenterCompletedStroke | Parkinson's Disease | Myasthenia Gravis | Amyotrophic Lateral Sclerosis (ALS) | MyopathiesUnited States
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Rigshospitalet, DenmarkOdense University Hospital; University of Southern DenmarkCompletedMyositis | Dermatomyositis | Polymyositis | Immune-Mediated Necrotizing MyopathyDenmark
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Abcuro, Inc.Syneos HealthActive, not recruitingInclusion Body MyositisUnited States, Australia, Belgium, France, Canada, Germany, United Kingdom
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University of IowaActive, not recruitingAcute Kidney Injury | Critical Illness Myopathy | Dialysis; ComplicationsUnited States
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The Hospital for Sick ChildrenCompletedX-linked Lymphoproliferative Syndrome Type 2 (XLP-2)Canada
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Leipzig University Medical CenterEuropean Leukodystrophy AssociationCompletedX-linked AdrenoleukodystrophyGermany
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Nova Scotia Health AuthorityCanadian Cancer Society (CCS)Enrolling by invitationBrain Cancer | Glioblastoma Multiforme of BrainCanada
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Hospital Universitari Vall d'Hebron Research InstituteCompletedQuality of Life | MyositisSpain
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National Institute of Environmental Health Sciences...CompletedDermatomyositis | Idiopathic Inflammatory MyopathiesUnited States
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National Human Genome Research Institute (NHGRI)Active, not recruitingWiskott- Aldrich Syndrome | ADA Deficient SCIDUnited States
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Novartis PharmaceuticalsActive, not recruitingType 2 Spinal Muscular AtrophyUnited States, China, Saudi Arabia, Thailand, Singapore, Brazil, Malaysia, Taiwan, Colombia, Mexico, Denmark, Egypt, India, South Africa, Vietnam
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Leadiant Biosciences, Inc.National Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsActive, not recruiting
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bluebird bioActive, not recruitingCerebral Adrenoleukodystrophy (CALD) | Adrenoleukodystrophy (ALD) | X-Linked Adrenoleukodystrophy (X-ALD)United States, Argentina, Australia, Brazil, France, Germany, Netherlands, United Kingdom, Italy
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Reata, a wholly owned subsidiary of BiogenAbbVieCompletedMItochondrial MyopathiesUnited States, Denmark
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Sándor BeniczkyUniversity of Aarhus; Danish Council for Independent Research; Søster og Verner...CompletedCritical Illness Myopathy | Myopathy Critical IllnessDenmark
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Novartis PharmaceuticalsActive, not recruitingSpinal Muscular AtrophyJapan, Belgium, Spain, Canada, United States, Australia, Italy, France, Netherlands
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Maastricht UniversityCompleted
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Novartis PharmaceuticalsCompletedSpinal Muscular AtrophyTaiwan, Belgium, Canada, United States, Australia, France, Italy, Portugal, United Kingdom
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Vanderbilt UniversityActive, not recruitingCognitive Impairment | MyopathyUnited States
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State University of New York - Upstate Medical...TerminatedFamilial Encephalopathy With Neuroserpin Inclusion Bodies | X-linked Mental Retardation | Congenital Vertical Talus | Idiopathic Generalised Epilepsy | Familial DementiaUnited States
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Astellas Gene TherapiesActive, not recruitingX-Linked Myotubular MyopathyUnited States, Canada, France, Germany
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Stealth BioTherapeutics Inc.Active, not recruitingMitochondrial Diseases | Mitochondrial Myopathies | Mitochondrial Complex I Deficiency | Mitochondrial Pathology | Mitochondrial DNA Depletion | Mitochondrial DNA Mutation | Mitochondrial DNA Deletion | Mitochondrial Metabolism DefectSpain, United States, Italy, Netherlands, Australia, Germany, Hungary, New Zealand, Norway, United Kingdom
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Wuerzburg University HospitalKyowa Kirin, Inc.Active, not recruiting
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University of ManchesterKing's College Hospital NHS Trust; Northern Care Alliance NHS Foundation Trust and other collaboratorsActive, not recruitingMyositis | Idiopathic Inflammatory MyopathyUnited Kingdom
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University of AarhusCompletedX-linked Hypophosphatemia | Hereditary HypophosphatemiaDenmark
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UCB BIOSCIENCES, Inc.Zogenix, Inc.Active, not recruitingThymidine Kinase 2 DeficiencyUnited States, Israel, Spain
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Radboud University Medical CenterCompletedMDC1A | SELENON-related MyopathyNetherlands
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Qilu Hospital of Shandong UniversityActive, not recruitingConnective Tissue Diseases | Interstitial Lung Disease | PirfenidoneChina
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Bristol-Myers SquibbCompletedDermatomyositis | Polymyositis | Autoimmune Necrotizing Myopathy | Overlap Myositis | Juvenile Myositis Above the Age of 18France, United States, Australia, Brazil, Czechia, Germany, Italy, Japan, Korea, Republic of, Mexico, Sweden
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Medialis Ltd.Metabolic Support UKCompletedX-linked Hypophosphatemia (XLH)United Kingdom
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University of ManchesterKarolinska Institutet; Eli Lilly and Company; Clinical Trials Unit, ManchesterCompletedIdiopathic Inflammatory MyopathiesUnited Kingdom
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Barts & The London NHS TrustImperial College London; Queen Mary University of LondonTerminatedCushing Syndrome | Pheochromocytoma | Conns Syndrome | Metabolic MyopathyUnited Kingdom
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Orthopedic Hospital Vienna SpeisingCompleted
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Health Discovery LabsNational Institute for Biomedical Imaging and Bioengineering (NIBIB); University... and other collaboratorsCompletedICU Acquired WeaknessUnited States
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University of FloridaLive Like Bella Pediatric Cancer ResearchCompletedCommon Variable Immunodeficiency | Severe Combined Immunodeficiency | Sickle Cell Disease | Hurler Syndrome | Chronic Granulomatous Disease | Thalassemia | Wiskott-Aldrich Syndrome | Adrenoleukodystrophy | X-linked Lymphoproliferative Disease | Diamond Blackfan Anemia | Bone Marrow Failure Syndrome | Hemophagocytic... and other conditionsUnited States
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SwanBio Therapeutics, Inc.Active, not recruitingAMN | AMN Gene Mutation | X-ALDUnited States, Netherlands, Germany
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University of PecsActive, not recruitingHealthy | Rheumatoid Arthritis | Systemic Lupus Erythematosus | Systemic Sclerosis | Myopathies, InflammatoryHungary
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University of NebraskaNational Institute on Aging (NIA); American Heart AssociationCompletedPeripheral Arterial DiseaseUnited States
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Zogenix MDS, Inc.Zogenix, Inc.WithdrawnThymidine Kinase 2 Deficiency
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Zogenix MDS, Inc.Zogenix, Inc.CompletedThymidine Kinase 2 DeficiencySpain, United States, Russian Federation, Turkey
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Zogenix MDS, Inc.CompletedThymidine Kinase 2 (TK2)United States, Spain, Israel
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Yale UniversityCompleted
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Kyowa Kirin Co., Ltd.Active, not recruiting
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Cambridge University Hospitals NHS Foundation TrustUniversity of Cambridge; Medical Research Council Mitochondrial Biology UnitCompletedMitochondrial Diseases | Mitochondrial Myopathies | Progressive External Ophthalmoplegia | Progressive Ophthalmoplegia | Progressive; Ophthalmoplegia, External | Mitochondria DNA Deletion | MELASUnited Kingdom
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Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy...Active, not recruitingNon-Hodgkin's Lymphoma | Acute Lymphoblastic Leukemia | Chronic Myeloid Leukemia | Myelodysplastic SyndromeUnited States
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Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy...Active, not recruitingAcute Myeloid Leukemia | Acute Lymphoblastic Leukemia | Non Hodgkin Lymphoma | Myelodysplastic Syndrome | Chronic Myelogenous Leukemia | Hemophagocytic Lymphohistiocytosis | Epstein Barr Virus Infection | X-linked Lymphoproliferative Disease | Hemophagocytic Syndrome | Familial Hemophagocytic LymphohistiocytosisUnited States
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Applied Genetic Technologies CorpCompletedX-linked RetinoschisisUnited States
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Kyowa Kirin Pharmaceutical Development LtdCompletedX-Linked HypophosphataemiaUnited Kingdom
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University of HelsinkiHelsinki University Central Hospital; University of Iowa; Institute for Molecular...CompletedMitochondrial Myopathies