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- US Clinical Trials Registry
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Search clinical trials for: chromosome 1q
Total 2714 results
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Eyup Hakan DuranRecruiting
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Stanford UniversityNot yet recruitingLiver Failure | Liver Cirrhosis | Hemophilia A | Hemophilia B | Hemophilia | Liver Transplant Disorder | Coagulation Factor DeficiencyUnited States
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Ionis Pharmaceuticals, Inc.RecruitingMethyl CpG Binding Protein 2 (MECP2) Duplication SyndromeUnited States
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Jiangsu Gensciences lnc.RecruitingHemophilia | Hemophilia A With Inhibitor | Male | Hemophilia B With InhibitorChina
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CSL BehringRecruiting
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Fundacion para la Investigacion Biomedica del Hospital...Fundación Mutua MadrileñaRecruiting
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CSL BehringRecruiting
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Cliniques universitaires Saint-Luc- Université...RecruitingInfertility, Male | Klinefelter SyndromeBelgium
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University of Nevada, Las VegasRecruitingDown SyndromeUnited States
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.RecruitingDuchenne Muscular DystrophyUnited States
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University of Kansas Medical CenterNot yet recruitingObesity | Alzheimer Disease | Down SyndromeUnited States
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Hasan Kalyoncu UniversityNot yet recruitingHemophilia A | Hemophilia B | HemophiliaTurkey
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Assiut UniversityNot yet recruitingHemophilia A | Hemophilia B
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Laurent ServaisSYSNAVRecruitingDuchenne Muscular Dystrophy | Myotonic Dystrophy 1 | Congenital Muscular Dystrophy | Centronuclear Myopathy | Charcot-Marie-Tooth | Fascioscapulohumeral Muscular DystrophyBelgium
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Assistance Publique - Hôpitaux de ParisNot yet recruitingPeriodontitis | Trisomy 21France
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Egyptian Chinese UniversityBenha UniversityRecruitingDuchenne Muscular DystrophyEgypt
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Massachusetts General HospitalNorthwestern University; University of Florida; University of Minnesota; Henry... and other collaboratorsRecruitingALS | Kennedy Disease | MND (Motor Neurone DIsease) | PLS | PMA - Progressive Muscular Atrophy | PBP - Progressive Bulbar PalsyUnited States, Italy
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Children's Hospital Medical Center, CincinnatiRecruitingFragile X SyndromeUnited States
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Institut National de la Santé Et de la Recherche...RecruitingPrader-Willi Syndrome | Angelman Syndrome | Beckwith-Wiedemann Syndrome | Pseudohypoparathyroidism | Silver Russell Syndrome | Transient Neonatal Diabetes Mellitus | Temple Syndrome | Kagami-Ogata Syndrome | Familial Precocious PubertyFrance
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Beijing Tiantan HospitalRecruiting
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Maimonides Medical CenterFoundation for Prader-Willi ResearchRecruitingBody Weight | Hyperphagia | Prader-Willi Syndrome | Mood | Behavior | Excessive Daytime SleepinessUnited States
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Brigham and Women's HospitalFoundation for Prader-Willi ResearchRecruiting
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University of ArizonaNational Heart, Lung, and Blood Institute (NHLBI); National Institutes of Health...RecruitingMedications for Obstructive Sleep Apnea to Improve Cognition in Children With Down Syndrome (MOSAIC)Obstructive Sleep Apnea | Down SyndromeUnited States
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Children's Hospital of PhiladelphiaNational Institute of Neurological Disorders and Stroke (NINDS); Vanderbilt...RecruitingRett Syndrome | Rett Syndrome, Atypical | RTTUnited States
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ItalfarmacoFortreaRecruitingDuchenne Muscular DystrophyBelgium, Netherlands, Canada, Italy, France, Germany, United Kingdom
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St. Jude Children's Research HospitalNot yet recruiting
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Janssen Pharmaceutical K.K.RecruitingX-Linked Retinitis PigmentosaJapan
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Cairo UniversityRecruiting
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UMC UtrechtEindhoven University of TechnologyRecruiting22q11.2 Deletion Syndrome | Adolescent Idiopathic ScoliosisNetherlands
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Tianjin Anding HospitalNot yet recruitingMajor Depressive Disorder | Bipolar Affective DisorderChina
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Assistance Publique - Hôpitaux de ParisBraintaleNot yet recruitingX-linked Adrenoleukodystrophy
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West Kazakhstan Medical UniversityRecruitingOrnithine Transcarbamylase Deficiency | Biotinidase Deficiency | Citrullinemia | Glutaric Acidemia Type II | Argininosuccinic Aciduria | Maple Syrup Urine Disease | Primary Carnitine Deficiency | Homocystinuria | Carnitine Palmitoyltransferase II Deficiency | Arginase Deficiency | Very Long-chain Acyl-CoA... and other conditionsKazakhstan
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Hereditary Neuropathy FoundationRecruitingCharcot-Marie-Tooth Disease | Charcot-Marie-Tooth Disease, Type IA | Charcot-Marie-Tooth Disease Type 2A | Charcot-Marie-Tooth | Charcot-Marie-Tooth Disease, Type IB | Charcot-Marie-Tooth Disease Type 2 | Charcot-Marie-Tooth Disease, Type 2C | Charcot-Marie-Tooth Disease Type 2A2B | Charcot-Marie-Tooth... and other conditionsUnited States
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Volastra Therapeutics, Inc.RecruitingGastric Adenocarcinoma | Uterine Carcinosarcoma | Triple Negative Breast Cancer | Advanced Solid Tumor | Head and Neck Squamous Cell Carcinoma | Esophageal Adenocarcinoma | Esophageal Squamous Cell Carcinoma | Transitional Cell Carcinoma of Bladder | Colorectal Adenocarcinoma | Gastroesophageal Junction... and other conditionsUnited States
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Hospices Civils de LyonRecruiting
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Neurogene Inc.RecruitingRett SyndromeUnited States
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Hasan Kalyoncu UniversityNot yet recruitingHemophilia B | Hemophilia | Hemophilia A, SevereTurkey
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Sarepta Therapeutics, Inc.Hoffmann-La RocheRecruitingDuchenne Muscular DystrophyBelgium, United States, Japan, Spain, Italy, United Kingdom
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Bahçeşehir UniversityRecruitingHemophilia A | Hemophilia BTurkey
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Atsena Therapeutics Inc.RecruitingX-linked RetinoschisisUnited States
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Frontera TherapeuticsPeking Union Medical College Hospital; Eye & ENT Hospital of Fudan University; Henan Provincial People's HospitalRecruitingX-Linked Retinitis PigmentosaChina
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Cairo UniversityRecruiting
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CHU de Quebec-Universite LavalRecruiting
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Cairo UniversityRecruiting
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Beni-Suef UniversityNot yet recruitingDuchenne Muscular Dystrophy
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Roopa Kanakatti Shankar, MBBS, MSRecruiting
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Innovation Research & TrainingRecruiting
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Bio Sidus SARecruiting
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Taizhou Hospital of Zhejiang Province affiliated...Sir Run Run Shaw Hospital; First Affiliated Hospital of Wenzhou Medical University and other collaboratorsRecruitingBiliary Tract CarcinomaChina