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Search clinical trials for: Beta thalassemia major
Total 12938 results
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CorrectSequence Therapeutics Co., LtdFirst Affiliated Hospital of Guangxi Medical UniversityActive, not recruiting
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CorrectSequence Therapeutics Co., LtdFirst Affiliated Hospital of Guangxi Medical UniversityEnrolling by invitation
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Actinogen MedicalAXIOM Real Time MetricsActive, not recruitingCognitive Impairment | Major Depressive Disorder | MDDAustralia, United Kingdom
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Sanguine BiosciencesCompletedDepression | Melanoma | Epilepsy | Lymphoma | Multiple Sclerosis | Kidney Cancer | Cervical Cancer | Diabetes Mellitus | Leukemia | Breast Cancer | Chronic Kidney Diseases | Chronic Obstructive Pulmonary Disease | Parkinson's Disease | Systemic Lupus Erythematosus | Multiple Myeloma | Hepatitis B | Insomnia | Colorectal Cancer | HIV/AID... and other conditionsUnited States
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Roswell Park Cancer InstituteActive, not recruitingAcute Myeloid Leukemia | Polycythemia Vera | Myelofibrosis | Chronic Myelomonocytic Leukemia | Waldenstrom Macroglobulinemia | Acute Lymphoblastic Leukemia | Chronic Lymphocytic Leukemia | Secondary Acute Myeloid Leukemia | Sickle Cell Disease | Myelodysplastic Syndrome | Plasma Cell Myeloma | Chronic Granulomatous... and other conditionsUnited States
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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bluebird bioActive, not recruitingTransfusion-dependent Beta-ThalassemiaUnited States, France, United Kingdom, Australia, Thailand, Italy, Germany, Greece
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National Institute of Blood and Marrow Transplant...Completed
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bluebird bioCompletedBeta-ThalassemiaUnited States, Germany, United Kingdom, France, Greece, Italy
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsEnrolling by invitationHematologic Diseases | Genetic Diseases, Inborn | Sickle Cell Disease | Hemoglobinopathies | Sickle Cell Anemia | Thalassemia | Beta-ThalassemiaUnited States, Canada, Italy, United Kingdom, Germany
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Bioray LaboratoriesXiangya Hospital of Central South University; First Affiliated Hospital of... and other collaboratorsEnrolling by invitation
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Ionis Pharmaceuticals, Inc.TerminatedBeta Thalassemia IntermediaAustralia, Thailand, Greece, Lebanon, Turkey
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National Heart, Lung, and Blood Institute (NHLBI)Active, not recruitingSickle Cell Disease | Congenital Hemolytic AnemiaUnited States
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St. Jude Children's Research HospitalNational Heart, Lung, and Blood Institute (NHLBI)Active, not recruitingSickle Cell DiseaseUnited States
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Rare Partners srl Impresa SocialeUniversità degli Studi di FerraraCompletedBeta-ThalassemiaItaly
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Otsuka Pharmaceutical Development & Commercialization...Iqvia Pty LtdTerminatedPost-traumatic Stress Disorder (PTSD)United States
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Silence Therapeutics plcCompletedNon-transfusion-dependent Thalassemia | Low Risk Myelodysplastic Syndrome | Very-Low Risk Myelodysplastic SyndromeThailand, Israel, Jordan, United Kingdom, Germany, Italy, Malaysia
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CelgeneAcceleron Pharma, Inc., a wholly-owned subsidiary of Merck & Co., Inc., Rahway...CompletedThalassemiaUnited States, Greece, Italy, Lebanon, Thailand, United Kingdom
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Vifor (International) Inc.Labcorp Corporation of America Holdings, IncCompletedBeta-Thalassemia | Non-transfusion-dependent ThalassemiaGreece, Israel, Italy, Lebanon, Thailand
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NYU Langone HealthTerminatedOpioid Pain MedicationUnited States
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Children's Hospital KarachiCompleted
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Institute of Hematology & Blood Diseases Hospital...EdiGene Inc.; The Affiliated Hospital Of Guizhou Medical University; Zunyi Medical...Active, not recruitingTransfusion Dependent Beta-ThalassaemiaChina
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Laureate Institute for Brain Research, Inc.National Institute of Mental Health (NIMH)CompletedAnorexia Nervosa | Brain Injury | Generalized Anxiety Disorder | Major Depressive Disorder | Panic DisorderUnited States
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Ann & Robert H Lurie Children's Hospital of ChicagoNational Heart, Lung, and Blood Institute (NHLBI)Active, not recruitingSickle Cell Disease | Sickle B+ Thalassemia | Sickle Beta Zero Thalassemia | Sickle Cell Hemoglobin CUnited States
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Thais CesarIngredients by Nature TMCompletedPre DiabetesBrazil
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Istanbul UniversityCompletedHeart Diseases | Breast Cancer | Thalassemia MinorTurkey
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Cairo UniversityCompletedQuality of Life | Fatigue | Cognitive Change | Beta-ThalassemiaEgypt
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bluebird bioCompletedBeta-ThalassemiaFrance, United Kingdom, United States, Thailand, Italy, Germany
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EdiGene (GuangZhou) Inc.PLA 923 HospitalActive, not recruitingTransfusion Dependent Beta-ThalassaemiaChina
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CelgeneAcceleron Pharma Inc. (a wholly owned subsidiary of Merck Sharp and Dohme...CompletedBeta-Thalassemia | Erythrocyte TransfusionUnited States, Israel, Australia, Turkey, Taiwan, Malaysia, United Kingdom, Canada, Thailand, France, Lebanon, Italy, Bulgaria, Greece, Tunisia
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Invenux, LLCState University of New York - Downstate Medical CenterActive, not recruitingSickle Cell Disease | Sickle-Beta Zero ThalassemiaUnited States
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Talaris Therapeutics Inc.Duke UniversityWithdrawnAnemia, Sickle Cell | Thalassemia | Beta-Thalassemia | Bone Marrow Failure Syndromes | Diamond-Blackfan Anemia | Alpha-Thalassemia | Complex and Transfusion-dependent HemoglobinopathiesUnited States
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EdiGene (GuangZhou) Inc.Active, not recruitingTransfusion Dependent Beta-ThalassaemiaChina
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IRCCS San RaffaeleTelethon Institute for Gene Therapy (OSR-TIGET)Active, not recruiting
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Vifor (International) Inc.Labcorp Drug Development IncWithdrawnBeta-ThalassemiaUnited States, Bulgaria, Israel
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Case Western Reserve UniversityNational Heart, Lung, and Blood Institute (NHLBI)CompletedHematologic Diseases | Iron Overload | Hemoglobinopathies | Thalassemia | Beta-Thalassemia | Anemia (Iron-Loading)
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CelgeneCompletedMyelodysplastic Syndromes | Beta-thalassemiaAustria
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Prothya BiosolutionsTerminated
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Imara, Inc.Terminatedβ ThalassemiaIsrael, France, Malaysia, Turkey, Denmark, Georgia, Greece, Italy, Lebanon, Morocco, Netherlands, Tunisia, United Kingdom
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Nova Laboratories LimitedCompletedSickle Cell Disease | Sickle Cell Hemoglobin C | Sickle Cell-beta-thalassemia | Sickle-Cell; Hemoglobin Disease, ThalassemiaUnited Kingdom, Jamaica
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Children's Hospital KarachiCompleted
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Institut National de la Santé Et de la Recherche...CompletedMajor Depressive Disorder | Major Depressive EpisodeFrance
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Spectrum Health HospitalsTerminated
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute... and other collaboratorsCompletedNon-Neoplastic Hematologic and Lymphocytic DisorderUnited States
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La Jolla Pharmaceutical CompanyTerminatedBeta-ThalassemiaAustralia, Thailand, United States, Greece, Italy, Lebanon, Turkey, United Kingdom
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Ann & Robert H Lurie Children's Hospital of ChicagoCompletedSickle Cell Disease | Sickle B+ Thalassemia | Sickle Beta Zero Thalassemia | Sickle Cell Hemoglobin CUnited States
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Protagonist Therapeutics, Inc.CompletedChronic Anemia | β-thalassemia | Ineffective ErythropoiesisUnited States, Malaysia, Turkey, Thailand, United Kingdom, Italy, Lebanon, Tunisia, Greece
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Protagonist Therapeutics, Inc.Completedβ-thalassemia | Ineffective ErythropoiesisMalaysia, Thailand, United States, Greece, United Kingdom, Turkey, Lebanon, Tunisia
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ShireTerminatedBeta-Thalassemia | Transfusional Iron OverloadUnited States, Lebanon, Canada, Italy, Turkey
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NovartisCompletedIron Overload | Beta-thalassemiaUnited States