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Search clinical trials for: Purine-Pyrimidine Metabolism, Inborn Errors
Total 15870 results
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TakedaCompleted
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TakedaCompleted
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PharmosUnknownHyperuricemia | GoutUnited States
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BioCryst PharmaceuticalsCompleted
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BioCryst PharmaceuticalsCompleted
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Savient PharmaceuticalsCompleted
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Savient PharmaceuticalsCompletedChronic Gout Refractory to Conventional TherapyUnited States
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White River Junction Veterans Affairs Medical CenterCompletedGout | Gout AcuteUnited States
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Savient PharmaceuticalsCompletedGoutUnited States, Canada, Mexico
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Nuon Therapeutics, Inc.CompletedHyperuricemia | Moderate to Severe GoutUnited States
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University of South FloridaCompleted
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NovartisCompletedAcute Gouty ArthritisGermany, Switzerland
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National Center for Research Resources (NCRR)University of California, San DiegoCompleted
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Dacima ConsultingSociété Tunisienne D'endocrinologie De Diabétologie Et Des Maladies MétaboliquesNot yet recruitingHypoparathyroidism | Pseudo HypoparathyroidismTunisia
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Atlantic Health SystemRegeneron PharmaceuticalsNot yet recruitingFamilial Hypercholesterolemia | High Density Lipoprotein Deficiency | Lipoprotein Types--Lp System Lp(A) Hyperlipoproteinemia | Apolipoprotein B 100, Familial Defective | Low-Density-Lipoid-Type HyperlipoproteinemiaUnited States
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Hospices Civils de LyonNot yet recruitingWilson DiseaseFrance
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Rocket Pharmaceuticals Inc.Not yet recruitingPyruvate Kinase DeficiencySpain, United States
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Leiden University Medical CenterThe Dutch Brain Foundation (funding)Not yet recruitingCerebral Amyloid Angiopathy
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AstraZenecaRecruitingCarpal Tunnel Syndrome | Amyloidosis | Polyneuropathy | Hereditary Transthyretin AmyloidosisRussian Federation
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Tisento TherapeuticsNot yet recruitingMitochondrial Encephalopathy, Lactic Acidosis and Stroke-Like Episodes (MELAS Syndrome)United States, Australia, Italy, Germany, Canada, United Kingdom
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Institute of Liver and Biliary Sciences, IndiaRecruitingGlycogen Storage DiseasesIndia
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Alnylam PharmaceuticalsRecruitingCerebral Amyloid AngiopathyCanada
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GeneCradle IncRecruitingPompe Disease (Late-onset)China
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Laval UniversityRecruitingFamilial Hypercholesterolemia | Cholesterol, Elevated | Nutrition, HealthyCanada
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AstraZenecaRecruiting
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Fondazione SISA (Societa Italiana per lo Studio...RecruitingFamilial Hypercholesterolemia | Genetic DisorderItaly
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Cliniques universitaires Saint-Luc- Université...RecruitingRare Diseases | Inborn Errors of MetabolismBelgium
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Alnylam PharmaceuticalsRecruitingHereditary Amyloidosis, Transthyretin-Related | Asymptomatic Carrier StateFrance
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John Paul II Hospital, KrakowRecruitingTransthyretin AmyloidosisPoland
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Fondation Ophtalmologique Adolphe de RothschildNot yet recruitingAlbinism, Ocular
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AstraZenecaRecruitingTransthyretin Amyloidosis Cardiomyopathy, Heart Failure With Preserved Ejection FractionRussian Federation
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Jirair Krikor BedoyanUltragenyx Pharmaceutical IncRecruitingPyruvate Dehydrogenase Complex DeficiencyUnited States
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Rigshospitalet, DenmarkNot yet recruitingBrain Diseases | Genetic Diseases, Inborn | Metabolism, Inborn Errors | Brain Diseases, Metabolic | Phenylketonurias | Brain Diseases, Metabolic, Inborn | Amino Acid Metabolism, Inborn Errors | Metabolic DiseaseDenmark
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Medical University of ViennaUniversity of Vienna; Griffith UniversityRecruiting
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NGGT (Suzhou) Biotechnology Co., Ltd.Not yet recruitingPhenylketonurias
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Lundquist Institute for Biomedical Innovation at...Not yet recruitingMucopolysaccharidosis III | Sanfilippo SyndromeUnited States
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Maastricht University Medical CenterRecruitingQuality of Life | Tuberous Sclerosis | Basal Cell Nevus Syndrome | Cutis Laxa | Epidermolysis Bullosa | Ichthyosis | Ectodermal Dysplasia | Albinism | Birt-Hogg-Dube Syndrome | Palmoplantar KeratosesNetherlands
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Hospital do CoracaoUniversity of Sao Paulo; Instituto Dante Pazzanese de Cardiologia; National Institute...Not yet recruiting
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Chiesi Farmaceutici S.p.A.ICON plcNot yet recruiting
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Caroline Michaela KistorpSanofiNot yet recruitingChronic Kidney Diseases | Fabry DiseaseDenmark
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National Taiwan University HospitalRecruiting
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Forge Biologics, IncNot yet recruitingKrabbe DiseaseUnited States
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BioMarin PharmaceuticalRecruitingPhenylketonuria (PKU)United States
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PTC TherapeuticsRecruitingPhenylketonuriaUnited States
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metaX Institut fuer Diatetik GmbHGreat Ormond Street Hospital for Children NHS Foundation Trust; Birmingham...Not yet recruitingAlkaptonuria | Homocystine; Metabolic Disorder | Tyrosinemia, Type I | Tyrosinemia, Type II | Tyrosinemia, Type III | MSUD (Maple Syrup Urine Disease)