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Search clinical trials for: SMA - Spinal Muscular Atrophy
Total 38841 results
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AnnJi Pharmaceutical Co., Ltd.Active, not recruitingSpinal and Bulbar Muscular Atrophy | Kennedy's DiseaseUnited States
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University of MiamiNational Institute of Neurological Disorders and Stroke (NINDS); National Institutes...Active, not recruitingAmyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Frontotemporal Dementia | Progressive Muscular Atrophy | ALS-Frontotemporal DementiaUnited States
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BiogenActive, not recruitingSpinal Muscular AtrophyUnited States, Taiwan, Israel, Australia, Qatar, United Kingdom, Turkey, Italy, Germany, Argentina, Canada
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The Hong Kong Polytechnic UniversityCompletedEndocrine System Diseases | Muscular Atrophy, Spinal | Child With Cancer | Child With Cerebral PalsyChina
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Sanguine BiosciencesCompletedDepression | Melanoma | Epilepsy | Lymphoma | Multiple Sclerosis | Kidney Cancer | Cervical Cancer | Diabetes Mellitus | Leukemia | Breast Cancer | Chronic Kidney Diseases | Chronic Obstructive Pulmonary Disease | Parkinson's Disease | Systemic Lupus Erythematosus | Multiple Myeloma | Hepatitis B | Insomnia | Colorectal Cancer | HIV/AID... and other conditionsUnited States
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University of MiamiNational Institute of Neurological Disorders and Stroke (NINDS); St. Jude Children... and other collaboratorsEnrolling by invitationAmyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Frontotemporal Dementia | Progressive Muscular Atrophy | Hereditary Spastic Paraplegia | Multisystem ProteinopathyUnited States, South Africa, Germany
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Hoffmann-La RocheActive, not recruitingSpinal Muscular AtrophyBelgium, United States, United Kingdom, France, Poland, Italy, Switzerland, Netherlands, Germany
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Hoffmann-La RocheActive, not recruitingMuscular Atrophy, SpinalUnited States, Belgium, Brazil, Russian Federation, Australia, Taiwan, Poland
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BiogenEnrolling by invitationMuscular Atrophy, SpinalUnited States, Spain, Taiwan, Chile, Saudi Arabia, Brazil, Russian Federation, Mexico, Germany, Estonia, Japan, Canada, Colombia, Lebanon, Poland, Italy, China
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Novartis Gene TherapiesActive, not recruitingSpinal Muscular Atrophy 1United States
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Grand Valley State UniversityActive, not recruitingCerebral Palsy | Spinal Cord Injuries | Spinal Muscular Atrophy | Genetic Disease | Spina Bifida | Development DelayUnited States
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Fondazione Policlinico Universitario Agostino Gemelli...CompletedMuscular Atrophy, Spinal | UltrasoundItaly
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Charite University, Berlin, GermanyMax Planck Institute for Infection BiologyCompletedAmyotrophic Lateral Sclerosis (ALS)Germany
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Clinic for Special ChildrenGenentech, Inc.Active, not recruitingSpinal Muscular AtrophyUnited States
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Nemours Children's ClinicCompletedMuscular Dystrophy | Spinal Muscular Atrophy | Arthrogryposis
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Duke UniversityCReATe Consortium (funded by NIH/NCATS/NINDS)CompletedAmyotrophic Lateral Sclerosis | Progressive Muscular AtrophyUnited States
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Hoffmann-La RocheCompletedMuscular Atrophy, SpinalBelgium, United States, China, Spain, Japan, France, Brazil, Croatia, Italy, Russian Federation, Saudi Arabia, Serbia, Switzerland, Turkey, Ukraine, Poland
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Istanbul Medipol University HospitalActive, not recruitingMuscular Atrophy, SpinalTurkey
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BiogenActive, not recruitingMuscular Atrophy, SpinalUnited States, Spain, Germany, Italy, Israel
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BiogenCompletedMuscular Atrophy, SpinalChina
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University of VermontUniversity of South CarolinaCompleted
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University of NottinghamActive, not recruiting
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University College London HospitalsCompletedDistal Hereditary Motor Neuropathy, Type II | Distal Hereditary Motor Neuropathy, Type V | Distal Hereditary Motor Neuronopathy Type I | Distal Hereditary Motor Neuronopathy Type VIUnited Kingdom
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Centre Hospitalier Régional de la CitadelleCompletedSafety and Efficacy Study of Pyridostigmine on Patients With Spinal Muscular Atrophy Type 3 (EMOTAS)Spinal Muscular Atrophy Type 3Belgium
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Cystinose StiftungLabor Becker & Kollegen, Munich, Germany; Screening Labor Hannover; Genetikum... and other collaboratorsCompletedSpinal Muscular Atrophy | Cystinosis | Cystinosis, NephropathicGermany
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Assistance Publique - Hôpitaux de ParisCompletedDuchenne Muscular Dystrophy | Spinal Muscular AtrophyFrance
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Eisai Co., Ltd.CompletedAmyotrophic Lateral Sclerosis (ALS)Japan
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Eisai Co., Ltd.CompletedAmyotrophic Lateral Sclerosis (ALS)Japan
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Novartis Gene TherapiesTerminatedSpinal Muscular AtrophyUnited States
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Ohio State UniversityCompletedSpinal Cord Injuries | Metabolic Disease | Skeletal Muscle AtrophyUnited States
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Northwell HealthCompletedAdult Spinal Muscular AtrophyUnited States
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Hoffmann-La RocheCompletedMuscular Atrophy, SpinalUnited States
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Fondazione Policlinico Universitario Agostino Gemelli...CompletedUltrasonography | Spinal Muscular Atrophy | Anesthesia, Spinal | Spinal Puncture ComplicationsItaly
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The Children's Hospital of Zhejiang University...Withdrawn
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Nationwide Children's HospitalNovartisActive, not recruitingSpinal Muscular Atrophy Type II | Spinal Muscular Atrophy Type IUnited States
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Duke UniversityCenters for Disease Control and Prevention; National ALS Registry; Agency for...CompletedMotor Neuron Disease | Amyotrophic Lateral Sclerosis | Progressive Muscular AtrophyUnited States
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Asan Medical CenterActive, not recruitingSarcopenia | Lumbar Spinal Stenosis | Neurogenic ClaudicationKorea, Republic of
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Universidad Autonoma de MadridKing's College London; Centro Superior de Estudios Universitarios LasalleCompletedMuscle Atrophy | Intervertebral Disc Compression | Spine InjurySpain, United Kingdom
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Novartis Gene TherapiesPRA Health SciencesCompletedSpinal Muscular Atrophy Type IKorea, Republic of, Taiwan, Japan
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Istanbul Medipol University HospitalEnrolling by invitationSpinal Muscular Atrophy | Muscle Tone PoorTurkey
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Washington University School of MedicineActive, not recruitingSpinal Muscular Atrophy | Spinal Muscular Atrophy Type 3 | Spinal Muscular Atrophy Type IIUnited States, Canada
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Istanbul Medipol University HospitalEnrolling by invitationQuality of Life | Neuromuscular Diseases | Spinal Muscular Atrophy | Pediatric DisorderTurkey
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Novartis Gene TherapiesCompletedSpinal Muscular Atrophy 1United States
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LMU KlinikumCompletedHealthy | Myotonic Dystrophy Type 2 | Pompe Disease (Late-onset) | Spinal Muscular Atrophy Type 3 | Myotonic Dystrophy Type 1 (DM1) | Facioscapulohumeral Muscular Dystrophy 1 | Inclusion Body Myositis, SporadicGermany
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Columbia UniversityBiogen; ALS AssociationCompleted
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National Institute of Neurological Disorders and...CompletedMotor Neuron Disease | Spinal and Bulbar Muscular Atrophy (SBMA)United States
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MarsiBionicsFundacion para la Investigacion Biomedica del Hospital Universitario Ramon...CompletedSpinal Muscular Atrophy Type IISpain
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Hasselt UniversityJessa Hospital; Sint-Trudo Hospital; Sint-Franciscus ZiekenhuisSuspendedExtreme Lateral Interbody FusionFUSION (XLIF) Versus Posterior Lumbar Interbody Fusion (PLIF) (XLIF)Atrophy | Muscle Damage | Degenerative Diseases, Spinal CordBelgium
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Assistance Publique - Hôpitaux de ParisCompleted
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CENTOGENE GmbH RostockCompletedScoliosis | Muscular Atrophy | Duchenne Muscular Dystrophy | Lordosis | Muscular Weakness | Increased Lordosis/Scoliosis | Hyporeflexia | Red-Green Color BlindnessEgypt, India, Albania, Pakistan, Georgia, Lebanon, Romania, Sri Lanka