- ICH GCP
- US Clinical Trials Registry
- Search trials
Search clinical trials for: chromosome 1q
Total 2704 results
-
Minoryx Therapeutics, S.L.RecruitingCerebral Adrenoleukodystrophy (cALD)United States, Brazil, Argentina
-
Shanghai General Hospital, Shanghai Jiao Tong University...Innostellar BiotherapeuticsRecruitingX-linked RetinoschisisChina
-
Federico II UniversityRecruiting
-
Children's Hospital of Fudan UniversityRecruitingPrader-Willi SyndromeChina
-
ApcinteX LtdCentessa Pharmaceuticals plcRecruitingHemophilia A | Hemophilia BUnited States, Italy, Spain, Taiwan, Australia, Belgium, United Kingdom, France, Germany, India, South Africa, Poland, Canada, Armenia, Turkey
-
ApcinteX LtdCentessa Pharmaceuticals plcRecruitingHemophilia B | Hemophilia B With InhibitorUnited States, Spain, Australia, Taiwan, France, Armenia, Germany
-
Istituto Auxologico ItalianoRecruitingPrader-Willi SyndromeItaly
-
Institut Jerome LejeuneRecruitingGenetic Markers and Biomarkers in Patients With Intellectual Disabilities of Genetic Origin (BioJeL)Intellectual Disability | Down SyndromeFrance
-
Institut Jerome LejeuneRecruiting
-
Fondazione Policlinico Universitario Agostino Gemelli...Recruiting
-
Sqy TherapeuticsBiotrialRecruitingDuchenne Muscular DystrophyFrance
-
Aelis FarmaEuropean CommissionRecruiting
-
Laboratoires VivacyRecruitingAging | Aesthetics | Volume Deficiency in the Mid-FaceFrance
-
University of AarhusRecruitingFertility Disorders | Turner Syndrome | Premature Ovarian FailureDenmark
-
University of SienaRecruiting
-
Masonic Cancer Center, University of MinnesotaRecruitingAcute Myeloid Leukemia | Juvenile Myelomonocytic Leukemia | Acute Lymphoblastic Leukemia | AML | Acute Leukemia | Neurofibromatosis 1 | Hematologic Malignancy | Myelodysplasia | Minimal Residual Disease | Chromosome Abnormality | Monosomy 7 | Remission | Somatic Mutation | Cytogenetic Abnormality | TP53 | Fetal Hemoglobin | Intrachromosomal Amplification of Chromosome... and other conditionsUnited States
-
Novo Nordisk A/SRecruitingTurner Syndrome | Noonan Syndrome | SGA | ISSKorea, Republic of, Malaysia, Netherlands, Spain, United States, Poland
-
Riphah International UniversityNot yet recruiting
-
Rigshospitalet, DenmarkNot yet recruitingMuscular Dystrophy | Duchenne Muscular Dystrophy | Becker Muscular DystrophyDenmark
-
Centre Hospitalier Universitaire, AmiensCentre Henri Becquerel; Hôpital Jeanne de Flandre LIlleRecruitingMyeloproliferative Neoplasm | Optical Genome Mapping | Cytogenetics | Clonality | Prognostic StratificationFrance
-
University Hospital Schleswig-HolsteinMichael J. Fox Foundation for Parkinson's ResearchRecruitingDystonia | Parkinson | Dystonia, Familial | DYT3 | DYT5 | PINK1 Gene DeletionGermany
-
The Emmes Company, LLCUltragenyx Pharmaceutical Inc; Parent Project Muscular Dystrophy; Department...RecruitingDuchenne Muscular DystrophyUnited States
-
Institute of Hematology & Blood Diseases HospitalNot yet recruiting
-
Albina Nowak, MDNot yet recruiting
-
Chiesi Farmaceutici S.p.A.ICON plcRecruiting
-
Children's Oncology GroupNational Cancer Institute (NCI)RecruitingDown Syndrome | Myeloid Leukemia Associated With Down Syndrome | B Acute Lymphoblastic Leukemia Associated With Down SyndromeUnited States
-
Mackay Memorial HospitalRecruiting
-
Children's Hospital Medical Center, CincinnatiSanofiRecruitingFabry DiseaseUnited States
-
University Hospital, BordeauxRecruitingIntellectual Disability | Cystic Fibrosis | Neurodegeneration With Brain Iron Accumulation (NBIA) | Congenital Heart Defect | Albinism | Rubinstein-Taybi Syndrome | Periventricular Nodular HeterotopiaFrance
-
REGENXBIO Inc.RecruitingDuchenne Muscular DystrophyUnited States
-
PfizerRecruitingDuchenne Muscular DystrophyUnited States
-
Ariel UniversityAssociazione Italiana Rett (AIRETT)Not yet recruitingRett SyndromeItaly
-
Centre Hospitalier Universitaire de LiegeSanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier Régional... and other collaboratorsRecruitingCongenital Adrenal Hyperplasia | Hemophilia A | Hemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystic Fibrosis | Alpha 1-Antitrypsin Deficiency | Sickle Cell Disease | Fanconi Anemia | Chronic Granulomatous Disease | Wilson Disease | Severe Congenital Neutropenia | Ornithine Transcarbamylase... and other conditionsBelgium
-
REGENXBIO Inc.RecruitingDuchenne Muscular DystrophyUnited States
-
Yonsei UniversityRecruitingFabry DiseaseKorea, Republic of
-
Avidity Biosciences, Inc.RecruitingDuchenne Muscular Dystrophy | Exon 44United States
-
University of ManchesterManchester University NHS Foundation Trust; Great Ormond Street Hospital for... and other collaboratorsRecruiting
-
Stephan EliezRecruitingtACS | 22Q11 Deletion SyndromeSwitzerland
-
University of Colorado, DenverChildren's Hospital Los AngelesRecruiting
-
Institute of Hematology & Blood Diseases HospitalRecruitingPrecursor Cell Lymphoblastic Leukemia-LymphomaChina
-
Ionis Pharmaceuticals, Inc.RecruitingPelizaeus-Merzbacher DiseaseFrance, Australia, Germany, Netherlands
-
Maimonides Medical CenterRecruitingAggression | Behavioral Symptoms | Pathologic Processes | Nervous System Diseases | Obesity | Neurologic Manifestations | Neurobehavioral Manifestations | Congenital Abnormalities | Overnutrition | Nutrition Disorders | Genetic Diseases, Inborn | Intellectual Disability | Self-Injurious Behavior | Abnormalities, Multiple and other conditionsUnited States
-
Muş Alparlan UniversityHacettepe UniversityRecruitingDuchenne Muscular DystrophyTurkey
-
Institute of Hematology & Blood Diseases HospitalNot yet recruiting
-
Boston Children's HospitalRecruitingDown SyndromeUnited States
-
Institute of Hematology & Blood Diseases HospitalNot yet recruiting
-
Hoffmann-La RocheRecruitingAngelman SyndromeAustralia, United States, Spain, Italy, France, Germany
-
Vyant BioNot yet recruiting
-
University of California, San FranciscoRecruitingMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VI | Wolman Disease | Pompe Disease Infantile-Onset | Mucopolysaccharidosis IV A | Mucopolysaccharidosis VII | Neuronopathic Gaucher DiseaseUnited States
-
PfizerRecruitingHemophilia A | Hemophilia BDenmark, Taiwan, Canada, Turkey, Spain, China, United Kingdom, South Africa, Saudi Arabia, Israel, Korea, Republic of, Austria, Germany, Japan, Australia, Italy, India, Slovakia, France, United States, Brazil, Argentina