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Search clinical trials for: Genetic Diseases, Inborn
Total 18659 results
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South Egypt Cancer InstituteAssiut University; Shefa Al-orman Children Cancer HospitalRecruiting
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Ondokuz Mayıs UniversityRecruitingQuality of Life | Urinary Incontinence | Menopause | Wolman Disease | Psychological Well-BeingTurkey
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Staidson (Beijing) Biopharmaceuticals Co., LtdRecruiting
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Assistance Publique - Hôpitaux de ParisNot yet recruiting
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UMC UtrechtAlfasigma S.p.A.; ReumaNederland; Autoimmune Research and Collaboration HubNot yet recruitingIgG4-related Disease | Idiopathic Inflammatory Myopathies | Behcet's DiseaseNetherlands
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Oslo University HospitalRecruitingCystic Fibrosis in ChildrenNorway
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Agios Pharmaceuticals, Inc.Not yet recruitingSickle Cell Disease | Nephropathy
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Bioray LaboratoriesInstitute of Hematology & Hospital of Blood Diseases, Chinese Academy of...Not yet recruiting
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Bioray LaboratoriesNanfang Hospital, Southern Medical UniversityNot yet recruitingSickle Cell Disease
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Kirsehir Ahi Evran UniversitesiTC Erciyes UniversityNot yet recruitingChildren | Cystic Fibrosis | Lung Functions | Mothers | Laughter Yoga | Laughter Therapy | Resilience,Psychological | Psychological HealthTurkey
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Specila hospital for cerebral palsy and developmental...FRAXA Research FoundationRecruitingFragile X SyndromeSerbia
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BioMarin PharmaceuticalRecruitingDuchenne Muscular DystrophySpain, United Kingdom
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Perha PharmaceuticalsGöteborg University; Proteas BioanalyticsRecruiting
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Kanglin Biotechnology (Hangzhou) Co., Ltd.Not yet recruitingTransfusion-dependent Beta-ThalassemiaChina
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Meyer Children's Hospital IRCCSRecruiting
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Assiut UniversityNot yet recruitingBehcet Disease and Vascular Involvement
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Eli Lilly and CompanyRecruitingAtopic DermatitisChina, Korea, Republic of
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Keymed Biosciences Co.LtdNot yet recruiting
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University Hospital, ToulouseNot yet recruitingPrader-Willi SyndromeFrance
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Lynk Pharmaceuticals Co., LtdRecruitingAtopic DermatitisChina
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Pilar AzevedoQueen's University, Belfast; Medical University Innsbruck; Cystic Fibrosis Foundation and other collaboratorsRecruiting
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Novilla PharmaceuticalsNot yet recruitingAcute Pain | Gout Flare | Acute Gouty ArthritisAustralia
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Walter Reed National Military Medical CenterRecruitingThyroid Eye Disease | Graves Ophthalmopathy | Graves DiseaseUnited States
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Novartis PharmaceuticalsRecruitingHypercholesterolaemia | Familial HypercholesterolaemiaJapan
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Radboud University Medical CenterEnzyre B.V.Recruiting
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Assiut UniversityNot yet recruitingBehcet Disease and Vascular Affection
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Pole Sante Grace de DieuRecruiting
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Xinhua Hospital, Shanghai Jiao Tong University...Shanghai Vitalgen BioPharma Co., Ltd.RecruitingType II Gaucher DiseaseChina
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Nordlandssykehuset HFUniversity of Oslo; Norwegian University of Science and Technology; The University... and other collaboratorsRecruitingPorphyria, Acute IntermittentNorway
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bluebird bioCenter for International Blood and Marrow Transplant ResearchRecruitingBeta-ThalassemiaUnited States
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Karolinska InstitutetRecruitingTourette Syndrome | Chronic Tic DisorderSweden
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Sunshine Guojian Pharmaceutical (Shanghai) Co.,...Recruiting
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UniQure Biopharma B.V.RecruitingFabry DiseaseUnited States
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Sarepta Therapeutics, Inc.RecruitingDuchenne Muscular DystrophyUnited States
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Abyss IngredientsEurofinsRecruitingEczema | Atopic DermatitisSpain
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Investigación en Hemofilia y FisioterapiaRecruiting
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S.LAB (SOLOWAYS)Center of New Medical TechnologiesRecruiting
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Nationwide Children's HospitalNational Heart, Lung, and Blood Institute (NHLBI); National Institutes of Health... and other collaboratorsNot yet recruitingSickle Cell DiseaseUnited States
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Investigación en Hemofilia y FisioterapiaRecruiting
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University of California, San FranciscoJohns Hopkins University; Baylor College of Medicine; Children's Hospital of... and other collaboratorsNot yet recruiting
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Université de SherbrookeCanadian Institutes of Health Research (CIHR); Centre de recherche du Centre... and other collaboratorsNot yet recruiting
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Central Hospital, Nancy, FranceRecruiting
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Université du Québec à ChicoutimiMcGill University; Université de Sherbrooke; University of Alberta; University... and other collaboratorsRecruitingAutosomal Recessive Spastic Ataxia of Charlevoix-Saguenay | Spastic Paraplegia 7Canada
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Université de SherbrookeCanadian Institutes of Health Research (CIHR); Centre de recherche du Centre... and other collaboratorsNot yet recruitingFragile X Syndrome
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Massachusetts General HospitalPatient-Centered Outcomes Research InstituteNot yet recruitingNeurofibromatosis 1United States
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University of MiamiFlorida lions eye bankNot yet recruitingCorneal Edema | Fuchs' Endothelial DystrophyUnited States
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Brunel UniversityRoyal Free Hospital NHS Foundation TrustRecruiting
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Chung-Hsing WangSanofiNot yet recruiting
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Incyte CorporationRecruitingPregnancy Related | Atopic DermatitisUnited States
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University Hospital, AntwerpUniversity Hospital, GhentRecruitingMarfan Syndrome | FBN1 MutationBelgium