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Search clinical trials for: genetic research
Total 96533 results
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The University of The West IndiesRecruiting
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Avidity Biosciences, Inc.RecruitingPhase 1/2 Study of AOC 1020 in Adults With Facioscapulohumeral Muscular Dystrophy (FSHD) (FORTITUDE)Muscular Dystrophies | Muscular Dystrophy, Facioscapulohumeral | FSHD | Facio-Scapulo-Humeral Dystrophy | FMD | Facioscapulohumeral Muscular Dystrophy 1 | FSHD2 | FSHD1 | FMD2 | Fascioscapulohumeral Muscular Dystrophy | Fascioscapulohumeral Muscular Dystrophy Type 1 | Fascioscapulohumeral Muscular Dystrophy... and other conditionsUnited States, United Kingdom, Canada
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Hospital Universitari Vall d'Hebron Research InstituteQueen's University, Belfast; Cystic Fibrosis Foundation; Hospital Vall d'Hebron; European Cystic Fibrosis Society - Clinical Trial NetworkRecruiting
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Children's Hospital of PhiladelphiaNational Institutes of Health (NIH); National Human Genome Research Institute...Recruiting
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Eli Lilly and CompanyRecruitingEczema | Atopic DermatitisUnited States, Taiwan, Spain, Mexico, Japan, Brazil, Australia, Canada, Czechia, France, Germany, Argentina, Poland
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Hospital del Río HortegaFundación de Investigación Biomédica - Hospital Universitario de La Princesa and other collaboratorsRecruiting
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ReCode TherapeuticsRecruitingPrimary Ciliary DyskinesiaUnited Kingdom, United States, Australia, New Zealand
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Novo Nordisk A/SRecruitingTurner Syndrome | Noonan Syndrome | SGA | ISSKorea, Republic of, Malaysia, Netherlands, Spain, United States, Poland
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National Health Research Institutes, TaiwanNational Taiwan University Hospital; Chang Gung Memorial Hospital; Kaohsiung... and other collaboratorsRecruiting
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Leiden University Medical CenterUniversity Medical Center Groningen; UMC Utrecht; Academisch Medisch Centrum... and other collaboratorsRecruitingCOVID-19 | Post-Acute COVID19 Syndrome | Post-COVID-19 Syndrome | Post-Acute COVID-19 | Post COVID-19 Condition | Multi-System Inflammatory Syndrome in Children | Pediatric Inflammatory Multisystem SyndromeNetherlands
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Aldeyra Therapeutics, Inc.Recruiting
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St. Jude Children's Research HospitalRecruitingRefractory Hematologic Malignancy | Relapsed Hematologic MalignancyUnited States
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Arcturus Therapeutics, Inc.Novotech CRORecruiting
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The Emmes Company, LLCUltragenyx Pharmaceutical Inc; Parent Project Muscular Dystrophy; Department...RecruitingDuchenne Muscular DystrophyUnited States
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Amydis Inc.National Institutes of Health (NIH); National Institute on Aging (NIA)Recruiting
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Lysosomal and Rare Disorders Research and Treatment...Team SanfilippoRecruitingSanfilippo Syndrome | MPS3United States
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AmgenRecruitingAtopic DermatitisUnited States, Korea, Republic of, Taiwan, Spain, Croatia, China, Greece, Belgium, Thailand, Puerto Rico, Hungary, Poland, Germany, Brazil, Italy, Japan, Canada, France, Romania, Chile
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Academisch Medisch Centrum - Universiteit van Amsterdam...ZonMw: The Netherlands Organisation for Health Research and DevelopmentRecruitingAtopic Dermatitis | Atopic Dermatitis EczemaNetherlands
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University Hospital, BordeauxRecruitingIntellectual Disability | Cystic Fibrosis | Neurodegeneration With Brain Iron Accumulation (NBIA) | Congenital Heart Defect | Albinism | Rubinstein-Taybi Syndrome | Periventricular Nodular HeterotopiaFrance
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Incyte CorporationRecruiting
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Astria Therapeutics, Inc.RecruitingHereditary AngioedemaUnited States, United Kingdom, Canada, Germany, Bulgaria, Czechia
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H. Lee Moffitt Cancer Center and Research InstituteRecruitingLynch Syndrome | Pancreatic Ductal Adenocarcinoma | Chronic Pancreatitis | Pancreatic Cyst | Ataxia Telangiectasia | FAP | Peutz-Jeghers Syndrome | PALB2 Gene Mutation | BRCA Mutation | Fatty Pancreas | Genetic Pancreatic Cancer | Genetic Pancreatitis | Familial Atypical Multiple Mole-MelanomaUnited States
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ADARx Pharmaceuticals, Inc.RecruitingHereditary AngioedemaAustralia
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Postgraduate Institute of Medical Education and...RecruitingIntrahepatic Cholestasis of Pregnancy | Genetic Mutation | Health Related Quality of LifeIndia
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PfizerRecruitingDuchenne Muscular DystrophyUnited States
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Pneumonia Research Network on Genetic Resistance...Charite University, Berlin, Germany; University of Leipzig; Jena University HospitalRecruitingPneumonia | Sepsis | Shock, SepticGermany
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St. Jude Children's Research HospitalWallace H. Coulter FoundationRecruitingIdentifying the Determinants of Bleeding and Hypermobility in Patients With Heavy Menstrual BleedingHypermobile Ehlers-Danlos Syndrome | Heavy Menstrual Bleeding | Hypermobility Syndrome (Disorder)United States
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Hoffmann-La RocheRecruitingHuntington DiseaseUnited States, Australia, Argentina, Canada, Germany, Italy, France, United Kingdom, Spain, Portugal, New Zealand, Austria, Poland, Switzerland, Denmark
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Novo Nordisk A/SRecruitingHaemophilia A With Inhibitors | Haemophilia ATaiwan, Canada, Spain, Netherlands, Korea, Republic of, India, United States, United Kingdom, China, Portugal, Lithuania, Turkey, South Africa, Ireland, Italy, France, Japan, Belgium, Malaysia, Poland, Austria, Bulgaria, Denmark, Germany and more
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REGENXBIO Inc.RecruitingDuchenne Muscular DystrophyUnited States
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ACELYRIN Inc.RecruitingThyroid Eye DiseaseUnited States, Australia
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Novartis PharmaceuticalsRecruitingHeterozygous or Homozygous Familial HypercholesterolemiaNetherlands, Israel, Hungary, Italy, Germany, Turkey, Spain, United States, France, Norway, Russian Federation, South Africa, United Kingdom, Canada, Switzerland, Brazil, Lebanon, Slovenia, Poland, Taiwan, Malaysia
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International University of Health and WelfareJapan Agency for Medical Research and Development; Chugai Pharmaceutical; Keio...RecruitingPulmonary Arterial HypertensionJapan
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University of Wisconsin, MadisonNational Institute on Aging (NIA)Recruiting
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TakedaTakeda Development Center Americas, Inc.RecruitingAlpha1-Antitrypsin DeficiencyUnited States, Belgium, Switzerland, Canada, Australia, Germany, United Kingdom, Austria, France, Spain, Portugal, Italy, Poland, Brazil
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National Tuberous Sclerosis AssociationRecruitingTuberous Sclerosis | LymphangioleiomyomatosisUnited States, Canada
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Avidity Biosciences, Inc.RecruitingDuchenne Muscular Dystrophy | Exon 44United States
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Vertex Pharmaceuticals IncorporatedModerna, IncRecruitingCystic FibrosisUnited States, United Kingdom, Australia, Canada
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Otsuka Beijing Research InstituteRecruitingAtopic Dermatitis (AD)China
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German Cancer Research CenterUniversity Hospital Heidelberg; University Hospital DresdenNot yet recruitingRelapsed/Refractory Acute Myeloid Leukemia (AML)Germany
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Olatec Therapeutics LLCRecruitingArthritis | Joint Pain | Gout | Gout Flare | Gouty Arthritis | Acute Gout Flare | Gout AttackUnited States, Spain, France
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National Human Genome Research Institute (NHGRI)RecruitingGenetic ConditionsUnited States
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Enliven TherapeuticsRecruitingHER2-positive Metastatic Breast Cancer | HER2 Gene Mutation | HER2 Mutant Non-small Cell Lung Cancer | HER2 AmplificationSpain, United States, Korea, Republic of, Taiwan, Italy, Australia, France
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Otsuka Beijing Research InstituteRecruiting
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Jaeb Center for Health ResearchRecruitingCystic FibrosisUnited States
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Sanguine BiosciencesRecruitingHeart Diseases | Stroke | Lymphoma | Multiple Sclerosis | Kidney Diseases | Diabetes | Leukemia | Age-Related Macular Degeneration | Cancer | Arthritis | Schizophrenia | Thyroid Diseases | Parkinson Disease | Hepatitis | Vasculitis | Psoriasis | Asthma | Amyloidosis | Fibromyalgia | Graves Disease | Alzheimer Disease | Celiac Disease | Cirr... and other conditionsUnited States
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SWOG Cancer Research NetworkNational Cancer Institute (NCI); Genentech, Inc.RecruitingDiffuse Large B-Cell Lymphoma | Recurrent Diffuse Large B-Cell Lymphoma | Refractory Diffuse Large B-Cell Lymphoma | Primary Mediastinal (Thymic) Large B-Cell Lymphoma | Grade 3b Follicular Lymphoma | Transformed Follic Lymph to Diff Large B-Cell Lymphoma | Transformed Marg Zone Lymph to Diff...United States
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PfizerPfizerRecruitingSickle Cell DiseaseUnited States, Nigeria
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Hoffmann-La RocheRecruitingAngelman SyndromeUnited States, Australia, Italy, France, Spain, Germany
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Novo Nordisk A/SRecruiting