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Search clinical trials for: Mucopolysaccharidosis (MPS) III
Total 11604 results
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Hoffmann-La RocheCompletedKidney TransplantationGermany
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Sangamo TherapeuticsActive, not recruitingHemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis IIUnited States
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Alcon ResearchCompletedMyopia | Contact Lens Fit
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Mayo ClinicNational Cancer Institute (NCI)RecruitingBreast Ductal Carcinoma In SituUnited States
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Novartis PharmaceuticalsCompleted
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NovartisCompleted
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Postgraduate Institute of Medical Education and...CompletedDiabetes Complications | Charcot ArthropathyIndia
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University of California, San FranciscoRecruitingMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VI | Wolman Disease | Pompe Disease Infantile-Onset | Mucopolysaccharidosis IV A | Mucopolysaccharidosis VII | Neuronopathic Gaucher DiseaseUnited States
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Institut BergoniéCompletedUnspecified Adult Solid Tumor, Protocol Specific | Metastatic CancerFrance
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NovartisCompletedKidney Transplantation | Adverse EffectsSwitzerland
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Novartis PharmaceuticalsCompletedRenal FunctionDenmark, Norway, Sweden
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Tyme, IncCompletedPancreatic CancerUnited States
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Novartis PharmaceuticalsCompletedProphilaxis of Acute Rejection in Patients Receiving a Renal AllograftSpain
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National Cancer Institute (NCI)WithdrawnMultiple Myeloma | Non-Hodgkin Lymphoma | Acute Leukemias | Chronic Myelogous Leukemia/Other Leukemia | MDS/MPS
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Novartis PharmaceuticalsTerminatedRenal TransplantationGermany
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Irmandade Santa Casa de Misericórdia de Porto AlegreNovartisCompleted
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Epitech Group SpAAzienda Ospedaliera "Sant'Andrea"Completed
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Sarcoma Oncology Research Center, LLCTyme, IncActive, not recruitingSarcoma | Sarcoma, EwingUnited States
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Novartis PharmaceuticalsCompletedKidney Transplantation | Renal TransplantationGermany, France
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University of Maryland, BaltimoreMcMaster UniversityRecruitingOpen tíbia FractureUnited States, Canada
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Armin GoralczykUnknownLiver Transplantation | Chronic Renal InsufficiencyGermany
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Gaetano CiancioCompletedTransplant; Failure, KidneyUnited States
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Novartis PharmaceuticalsCompleted
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University Hospital, ToursNot yet recruitingRenal Transplant Rejection | Induction Therapy
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Ankara UniversityGazi UniversityCompleted
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Peking Union Medical CollegeUnknownBreast Cancer | Lung Cancer | Malignant Pleural Effusion
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Alcon ResearchCompletedRefractive Error | Presbyopia | Astigmatism | Myopia | Hyperopia
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Duke UniversityCompletedHemoglobinopathies | Thalassemia | Lysosomal Storage Disease | Immunodeficiencies | Inborn Errors of Metabolism | Sickle Cell | Non Malignant Disorders | Congenital Marrow FailuresUnited States
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PfizerTerminatedAtherosclerosis | Kidney FailureCanada, United States
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Paul SzabolcsRecruitingCongenital Bone Marrow Failure Syndromes | Inflammatory Conditions | Primary Immunodeficiency (PID) | Inherited Metabolic Disorders (IMD) | Hereditary AnemiasUnited States
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Paul SzabolcsRecruitingCongenital Bone Marrow Failure Syndromes | Inflammatory Conditions | Primary Immunodeficiency (PID) | Inherited Metabolic Disorders (IMD) | Hereditary Anemias | Systemic Juvenile Idiopathic Arthritis (sJIA)United States
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NYU Langone HealthHarvard Medical School (HMS and HSDM); National Institute on Drug Abuse (NIDA) and other collaboratorsRecruitingOpioid Use Disorder (OUD)United States
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Lundquist Institute for Biomedical Innovation at...Not yet recruitingMucopolysaccharidosis III | Sanfilippo SyndromeUnited States
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JCR Pharmaceuticals Co., Ltd.RecruitingMucopolysaccharidosis III-AGermany
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Lysosomal and Rare Disorders Research and Treatment...Team SanfilippoRecruitingSanfilippo Syndrome | MPS3United States
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JCR Pharmaceuticals Co., Ltd.RecruitingMucopolysaccharidosis IIUnited States, Germany, Spain, France, Brazil, Argentina, Turkey, United Kingdom, Poland, Italy
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Phoenix NestNational Institute of Neurological Disorders and Stroke (NINDS)Enrolling by invitationSanfilippo Syndrome Type DUnited States
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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University of ManchesterUniversity College, London; Manchester University NHS Foundation Trust; Orchard... and other collaboratorsActive, not recruitingMucopolysaccharidosis Type IIIAUnited Kingdom
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Albert Einstein College of MedicineEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationMucopolysaccharidosis II | Fabry Disease | Niemann-Pick Disease, Type C | Mucopolysaccharidosis VI | Lysosomal Acid Lipase Deficiency | Metachromatic Leukodystrophy | Gaucher Disease | Cerebrotendinous Xanthomatosis | Mucopolysaccharidosis IV A | GM1 Gangliosidosis | Mucopolysaccharidosis VII | Acid Sphingomyelinase... and other conditionsUnited States
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University of British ColumbiaMedical University of Graz; Hospital de Clinicas de Porto AlegreUnknownMorquio B Disease | GM1 Gangliosidosis Type IIICanada
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UniQure Biopharma B.V.Institut Pasteur; Venn Life SciencesCompleted
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University Hospital HeidelbergCompletedMucopolysaccharidosis Type I | Mucopolysaccharidosis Type II | Coping Behavior | Mucopolysaccharidosis Type III | Behavior DisordersGermany
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LYSOGENECompletedMucopolysaccharidosis Type III A | Sanfilippo Disease Type AFrance
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LYSOGENECompletedMucopolysaccharidosis Type III A | Sanfilippo Disease Type AFrance
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AstraZenecaRecruitingSevere Eosinophilic AsthmaChina
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Nanjing IASO Biotechnology Co., Ltd.RecruitingMultiple MyelomaChina
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Genelux CorporationNewsoara Biopharma Co., Ltd.Not yet recruitingNon-small Cell Lung Cancer Stage III | Non-small Cell Lung Cancer | Advanced Non-squamous Non-small-cell Lung Cancer | Non-small Cell Lung Cancer Stage IV | Metastatic Squamous Non-Small Cell Lung Carcinoma | Non-small Cell Lung Cancer Recurrent | Metastatic Non-squamous Non Small Cell Lung Cancer and other conditions
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The First Affiliated Hospital with Nanjing Medical...Not yet recruitingGastric Cancer | Esophagogastric Junction Adenocarcinoma
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Universität des SaarlandesRecruitingAcute Decompensated Heart FailureGermany