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Search clinical trials for: Oculopharyngeal muscular dystrophy
Total 12870 results
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Children's Hospital Medical Center, CincinnatiActive, not recruitingMusculoskeletal Abnormalities | Duchenne Muscular DystrophyUnited States
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Northwestern UniversityCompletedBecker Muscular Dystrophy | Limb-girdle Muscular DystrophyUnited States
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Children's National Research InstituteActive, not recruitingGenetic Diseases, Inborn | Musculoskeletal Diseases | Muscular Dystrophies | Cardiac FibrosisUnited States
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Sarepta Therapeutics, Inc.Active, not recruiting
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Children's National Research InstituteFoundation to Eradicate DuchenneActive, not recruitingDuchenne Muscular DystrophyUnited States
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Kevin FlaniganActive, not recruitingDuchenne Muscular DystrophyUnited States
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AMO Pharma LimitedCompletedCongenital Myotonic DystrophyUnited States, Canada, New Zealand, Australia, United Kingdom
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Assistance Publique - Hôpitaux de ParisCompletedDuchenne Muscular Dystrophy | Spinal Muscular AtrophyFrance
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Hugo W. Moser Research Institute at Kennedy Krieger...Active, not recruitingFacioscapulohumeral Muscular DystrophyUnited States
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Sarepta Therapeutics, Inc.TerminatedAn Extension Study to Evaluate Casimersen or Golodirsen in Patients With Duchenne Muscular DystrophyDuchenne Muscular DystrophyUnited States, Belgium, Canada, Spain, United Kingdom, Czechia, Germany, Israel, Bulgaria, France, Italy, Poland, Sweden
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Sarepta Therapeutics, Inc.TerminatedDuchenne Muscular DystrophyBelgium, France, Italy, United Kingdom
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aTyr Pharma, Inc.CompletedFacioscapulohumeral Muscular DystrophyUnited States, Italy, Netherlands
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Ondokuz Mayıs UniversityCompletedDuchenne Muscular Dystrophy (DMD)Turkey
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Solid Biosciences Inc.CompletedDuchenne Muscular DystrophyUnited States
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Assistance Publique - Hôpitaux de ParisNational Research Agency, FranceCompletedRheumatoid Arthritis | Uveitis | Vasculitis | Type 1 Diabetes | Crohn's Disease | Myositis | Healthy Volunteer | Ankylosing Spondylitis | FMF | Systemic Lupus Erythematosus/Antiphospholipid Syndrome | Cryopyrin-Associated Periodic Syndromes /TNF-receptor Associated Periodic Syndrome | Ulcerative Rectocolitis | Unclassified...France
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Sarepta Therapeutics, Inc.Hoffmann-La RocheEnrolling by invitation
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Hacettepe UniversityCompletedDuchenne Muscular Dystrophy | Ambulation Difficulty | Ambulation Disorder, NeurologicTurkey
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Daiichi Sankyo Co., Ltd.Active, not recruitingDuchenne Muscular DystrophyJapan
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IRCCS San Camillo, Venezia, ItalyUniversita di Verona; Fondazione IRCCS Ca' Granda, Ospedale Maggiore Policlinico and other collaboratorsEnrolling by invitationCalpain-3 Deficiency Limb Girdle Muscular Dystrophy Type 2AItaly
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Avidity Biosciences, Inc.Active, not recruitingNervous System Diseases | Genetic Diseases, Inborn | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Neurodegenerative Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Heredodegenerative Disorders, Nervous System | Myotonic Dystrophy | Myotonic Disorders | Myotonic Dystrophy... and other conditionsUnited States
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.CompletedDuchenne Muscular DystrophySpain, United States, Russian Federation, Italy, China, Turkey
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Fulcrum TherapeuticsActive, not recruitingFacioscapulohumeral Muscular Dystrophy 1Netherlands
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Fulcrum TherapeuticsActive, not recruitingFacioscapulohumeral Muscular Dystrophy (FSHD)United States, Canada, France, Spain
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Sarepta Therapeutics, Inc.Nationwide Children's HospitalCompleted
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Brock UniversityCompletedMultiple Sclerosis | Inflammation | Muscular Dystrophies | Spinal Cord Injuries | Diet HabitCanada
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Élise DuchesneMuscular Dystrophy CanadaCompletedAutosomal Recessive Spastic Ataxia of Charlevoix-SaguenayCanada
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Universidad de AlmeriaCompletedNeurologic Disorder | Pediatric Disorder | Duchenne | Sensorimotor Disorder NosSpain
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University of RochesterCompletedFacioscapulohumeral Muscular DystrophyUnited States
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National Neuroscience InstituteNanyang Technological University; Institute for Infocomm Research; Institute... and other collaboratorsActive, not recruitingMotor Neuron Disease | Amyotrophic Lateral Sclerosis | Muscular Dystrophies | Spinal Cord Injuries | Tetraplegia | Tetraplegia/Tetraparesis | Locked-in SyndromeSingapore
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Santhera PharmaceuticalsNo longer availableDuchenne Muscular DystrophyUnited States
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Edgewise Therapeutics, Inc.CompletedNervous System Diseases | Genetic Diseases, Inborn | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Healthy VolunteerUnited States
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Cairo UniversityCompletedMuscular Dystrophy, Duchenne TypeEgypt
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GenethonActive, not recruitingLGMD2IDenmark, France, United Kingdom
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PfizerCompletedDuchenne Muscular DystrophyChina
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ML Bio Solutions, Inc.Virginia Commonwealth UniversityCompletedMuscular Dystrophies | Limb Girdle Muscular DystrophyUnited States, Denmark
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NRG OncologyNational Cancer Institute (NCI)Active, not recruitingStage II Prostate Adenocarcinoma | Stage III Prostate Adenocarcinoma | Stage I Prostate AdenocarcinomaUnited States, Canada, Puerto Rico
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Synchron Medical, Inc.WithdrawnParalysis | Amyotrophic Lateral Sclerosis | Muscular Dystrophies | Neurologic Disorder | Spinal Muscular Atrophy | Spinal Cord Injury | Stroke, Lacunar | Upper Limb Injury | Paralysis; Stroke | Stroke, BrainstemAustralia
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ReveraGen BioPharma, Inc.University of Pittsburgh; Newcastle University; European Union; Cooperative International...CompletedDuchenne Muscular DystrophyUnited States, Belgium, Canada, United Kingdom, Spain, Netherlands, Sweden, Czechia, Australia, Greece, Israel
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Barrow Neurological InstituteALS Association; Muscular Dystrophy Association; Synapse BiomedicalCompletedAmyotrophic Lateral Sclerosis (ALS)United States
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Nippon Shinyaku Co., Ltd.Active, not recruiting
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Haukeland University HospitalExtrastiftelsenCompleted
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ENCellCompletedDuchenne Muscular DystrophyKorea, Republic of
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Université de SherbrookeRare Disease FoundationCompletedMyotonic Dystrophy 1Canada
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Megan WaldropAudentes TherapeuticsActive, not recruitingDuchenne Muscular DystrophyUnited States
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Murdoch Childrens Research InstituteCompletedFacio-Scapulo-Humeral Dystrophy | FSHD2 | FSHD1Australia
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Phrixus Pharmaceuticals, Inc.Charley's FundTerminated
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Hacettepe UniversitySuleyman Demirel UniversityCompletedDuchenne Muscular Dystrophy | Ambulation Difficulty | Posture Disorders in Children | Ambulation Disorder, NeurologicTurkey
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NS Pharma, Inc.Cooperative International Neuromuscular Research Group; Nippon Shinyaku Co.... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Canada
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Vrije Universiteit BrusselCompletedMyotonic Dystrophy 1Belgium
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Hacettepe UniversityActive, not recruitingDuchenne Muscular DystrophyTurkey