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Search clinical trials for: Spinal Muscular Atrophy type II
Total 104163 results
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Masonic Cancer Center, University of MinnesotaCompletedSoft Tissue Sarcoma | Medulloblastoma | Retinoblastoma | Rhabdomyosarcoma | Hepatoblastoma | Primary Malignant Brain Neoplasms | CNS Tumors | Germ Cell Tumors | Ewing's Family Tumors | Renal Tumors | Supra-tentorial Primative Neuro-Ectodermal Tumor (PNET) | Atypical Teratoid/Rhabdoid Tumor (AT/RT)United States
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Grand Valley State UniversityActive, not recruitingCerebral Palsy | Spinal Cord Injuries | Spinal Muscular Atrophy | Genetic Disease | Spina Bifida | Development DelayUnited States
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Rigshospitalet, DenmarkUltragenyx Pharmaceutical IncCompletedTarui Disease | Debrancher Deficiency | GYG1 DEFICIENCYDenmark
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Fundación Cardiovascular de ColombiaSanadores Ambientales SANAM Company SASCompletedSarcopenia | Respiratory Function LossColombia
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Fondazione Policlinico Universitario Agostino Gemelli...CompletedMuscular Atrophy, Spinal | UltrasoundItaly
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Istanbul Physical Medicine Rehabilitation Training...CompletedAnkylosing SpondylitisTurkey
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National Cancer Institute (NCI)Active, not recruitingLeiomyosarcoma | Fibrosarcoma | Liposarcoma | Mesenchymal Chondrosarcoma | Stage III Soft Tissue Sarcoma AJCC v7 | Stage IV Soft Tissue Sarcoma AJCC v7 | Malignant Peripheral Nerve Sheath Tumor | PEComa | Synovial Sarcoma | Epithelioid Sarcoma | Alveolar Soft Part Sarcoma | Undifferentiated High Grade Pleomorphic... and other conditionsUnited States, Canada, Puerto Rico
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Charite University, Berlin, GermanyMax Planck Institute for Infection BiologyCompletedAmyotrophic Lateral Sclerosis (ALS)Germany
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Incyte CorporationTerminatedUrothelial CarcinomaUnited States, France, Italy
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University of AlbertaWithdrawnHealthy | Amyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Frontotemporal Dementia | Muscular Atrophy, ProgressiveCanada
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Clinic for Special ChildrenGenentech, Inc.Active, not recruitingSpinal Muscular AtrophyUnited States
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BiogenCompletedSpinal Muscular AtrophyGermany
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AdventHealth Translational Research InstituteActive, not recruitingType 2 Diabetes | Exercise | Muscular Atrophy | Sedentary Behavior | Pre-diabetesUnited States
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BiogenCompletedSpinal Muscular AtrophyUnited States, Spain, Germany, United Kingdom, Australia, Japan, Canada, Belgium, France, Hong Kong, Italy, Korea, Republic of, Sweden, Turkey
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Fred Hutchinson Cancer CenterActive, not recruitingMyasthenia Gravis | Neuromyelitis Optica | Autoimmune Disease | Chronic Inflammatory Demyelinating Polyneuropathy | Lambert Eaton Myasthenic Syndrome | Cerebellar Degeneration | Stiff Person Syndrome | Opsoclonus Myoclonus Syndrome | Neurologic Autoimmune Disease | Autologous Transplant Autoimmune | Multiple... and other conditionsUnited States
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Nemours Children's ClinicCompletedMuscular Dystrophy | Spinal Muscular Atrophy | Arthrogryposis
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National Cancer Institute (NCI)Active, not recruitingHLRCC | Sporadic Papillary Renal Cell CancerUnited States
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Advenchen Laboratories, LLCActive, not recruitingLeiomyosarcoma | Synovial Sarcoma | Alveolar Soft Part Sarcoma | Soft-Tissue SarcomaUnited States, United Kingdom, Spain, China, Italy
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Fox Chase Cancer CenterActive, not recruitingSoft Tissue SarcomaUnited States
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Columbia UniversityUniversitat Autonoma de Barcelona; Instituto de Salud Carlos III; University... and other collaboratorsActive, not recruitingThymidine Kinase 2 Deficiency | Mitochondrial DNA Depletion Syndrome 2 Myopathic TypeUnited States
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Duke UniversityCReATe Consortium (funded by NIH/NCATS/NINDS)CompletedAmyotrophic Lateral Sclerosis | Progressive Muscular AtrophyUnited States
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City of Hope Medical CenterNational Cancer Institute (NCI)Active, not recruitingMetastatic Leiomyosarcoma | Stage III Uterine Corpus Leiomyosarcoma AJCC v8 | Stage IV Uterine Corpus Leiomyosarcoma AJCC v8 | Unresectable Leiomyosarcoma | Stage IIIA Uterine Corpus Leiomyosarcoma AJCC v8 | Stage IIIB Uterine Corpus Leiomyosarcoma AJCC v8 | Stage IIIC Uterine Corpus Leiomyosarcoma... and other conditionsUnited States
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Novartis PharmaceuticalsCompletedSpinal Muscular AtrophyTaiwan, Belgium, Canada, United States, Australia, France, Italy, Portugal, United Kingdom
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Emory UniversityNational Cancer Institute (NCI)WithdrawnStage II Intrahepatic Cholangiocarcinoma AJCC v8 | Stage III Intrahepatic Cholangiocarcinoma AJCC v8 | Resectable Intrahepatic Cholangiocarcinoma | Stage 0 Intrahepatic Cholangiocarcinoma AJCC v8 | Stage I Intrahepatic Cholangiocarcinoma AJCC v8United States
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Fundació Institut de Recerca de l'Hospital de la...Terminated
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Hospices Civils de LyonCompletedSpinal Muscular AtrophyFrance
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Istanbul Medipol University HospitalActive, not recruitingMuscular Atrophy, SpinalTurkey
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Novartis PharmaceuticalsCompleted
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BiogenActive, not recruitingMuscular Atrophy, SpinalUnited States, Spain, Germany, Italy, Israel
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National Cancer Institute (NCI)Canadian Cancer Trials GroupActive, not recruitingAcute Lymphoblastic Leukemia | B Acute Lymphoblastic Leukemia, Philadelphia Chromosome NegativeUnited States, Canada, Israel, Puerto Rico
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Noha Khaled ShoukryActive, not recruitingChronic Low-back Pain | Lumbar Disc Herniation | Chronic Ankle Injuries | Calf Muscle WeaknessEgypt
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BiogenCompletedMuscular Atrophy, SpinalChina
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BayerTerminatedOsteosarcoma | Ewing Sarcoma | Neuroblastoma | Rhabdomyosarcoma | Relapsed or Refractory Solid Tumors or Lymphoma in ChildrenUnited States
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Washington University School of MedicineCompletedDoxorubicin With Upfront Dexrazoxane for the Treatment of Advanced or Metastatic Soft Tissue SarcomaSoft Tissue Sarcoma | Sarcoma, Soft Tissue | Leiomyosarcoma | Fibrosarcoma | Liposarcoma | Angiosarcoma | Malignant Peripheral Nerve Sheath Tumor | Synovial Sarcoma | Undifferentiated Pleomorphic Sarcoma | Epithelioid Sarcoma | MyxofibrosarcomaUnited States
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Biohaven Pharmaceuticals, Inc.Active, not recruitingNeuromuscular Diseases | Spinal Muscular Atrophy | SMAUnited States, Netherlands, United Kingdom, Spain, Czechia, Belgium, Germany, Italy, Poland
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Memorial Sloan Kettering Cancer CenterNational Cancer Institute (NCI)Active, not recruiting
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National Institutes of Health Clinical Center (CC)CompletedRecurrent Adult Soft Tissue Sarcoma | Stage III Adult Soft Tissue Sarcoma | Stage IVA Adult Soft Tissue Sarcoma | Stage IIB Adult Soft Tissue Sarcoma | Stage IIC Adult Soft Tissue Sarcoma | Stage IVB Adult Soft Tissue Sarcoma
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National Cancer Institute (NCI)CompletedRecurrent Hodgkin Lymphoma | Refractory Hodgkin Lymphoma | Metastatic Melanoma | Stage III Cutaneous Melanoma AJCC v7 | Stage IV Cutaneous Melanoma AJCC v6 and v7 | Refractory Malignant Solid Neoplasm | Recurrent Melanoma | Recurrent Malignant Solid Neoplasm | Recurrent Neuroblastoma | Recurrent Non-Hodgkin... and other conditionsUnited States, Canada
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedChordoma | Rhabdomyosarcoma | Recurrent Childhood Rhabdomyosarcoma | Recurrent Adult Soft Tissue Sarcoma | Previously Treated Childhood Rhabdomyosarcoma | Recurrent Childhood Soft Tissue Sarcoma | Adult Rhabdomyosarcoma | Metastatic Childhood Soft Tissue Sarcoma | Untreated Childhood Rhabdomyosarcoma | Stage I Adult Soft Tissue Sarcoma AJCC v7 and other conditionsUnited States, Netherlands, Canada, Australia, New Zealand, Puerto Rico, Switzerland
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David Liebner, MDWithdrawnLocally Advanced Leiomyosarcoma | Metastatic Leiomyosarcoma | Unresectable Leiomyosarcoma | Stage III Retroperitoneal Sarcoma AJCC v8 | Stage IIIA Retroperitoneal Sarcoma AJCC v8 | Stage IIIB Retroperitoneal Sarcoma AJCC v8 | Stage IV Retroperitoneal Sarcoma AJCC v8United States
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First Affiliated Hospital of Wenzhou Medical UniversityQilu Hospital of Shandong University; Eastern Hepatobiliary Surgery Hospital; The First Affiliated Hospital of Zhejiang Chinese Medical UniversityEnrolling by invitationHepatocellular Carcinoma | SarcopeniaChina
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St. Jude Children's Research HospitalActive, not recruiting
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Cystinose StiftungLabor Becker & Kollegen, Munich, Germany; Screening Labor Hannover; Genetikum... and other collaboratorsCompletedSpinal Muscular Atrophy | Cystinosis | Cystinosis, NephropathicGermany
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Daniel BenjaminEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedHeart Failure | Epilepsy | Pain | Pneumonia | Sepsis | Inflammation | Hypertension | Chronic Kidney Diseases | Hemophilia | Schizophrenia | Central Nervous System Infections | Nosocomial Pneumonia | Insomnia | Anxiety | Bipolar Disorder | Neutropenia | Staphylococcal Infections | Bradycardia | Seizures | Urinary Tract Infections | Pulmonary... and other conditionsUnited States, Canada, United Kingdom, Israel, Singapore
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Assistance Publique - Hôpitaux de ParisCompletedDuchenne Muscular Dystrophy | Spinal Muscular AtrophyFrance
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Fred Hutchinson Cancer CenterPfizerCompletedAcute Myeloid LeukemiaUnited States
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AeRang KimTerminatedOsteosarcoma | Ewing Sarcoma | Neuroblastoma | Solid Tumors | Pediatric Cancer | Rhabdomyosarcoma | Wilms Tumor | Soft Tissue Sarcomas | Germ Cell Tumors | Hepatic TumorUnited States
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Health Education Research Foundation (HERF)CompletedAthletic Injuries | Athletic Performance | Hamstring TightnessPakistan
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Assistance Publique - Hôpitaux de ParisCompletedSpastic Paraplegia Type 5A, RecessiveFrance
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Albert Einstein College of MedicineNational Cancer Institute (NCI)TerminatedUterine Corpus Leiomyosarcoma | Stage IIA Uterine Sarcoma | Stage IIB Uterine Sarcoma | Stage IIIA Uterine Sarcoma | Stage IIIB Uterine Sarcoma | Stage IIIC Uterine Sarcoma | Stage IVA Uterine Sarcoma | Stage IVB Uterine Sarcoma | Stage IA Uterine Sarcoma | Stage IB Uterine Sarcoma | Stage IC Uterine SarcomaUnited States