- ICH GCP
- US Clinical Trials Registry
- Search trials
Search clinical trials for: Genetic research
Total 96483 results
-
Bionou Research, S.L.Biopolis S.L.Recruiting
-
Hugo W. Moser Research Institute at Kennedy Krieger...RecruitingNeurodegenerative Diseases | Ataxia | Cerebellar Ataxia | Leukodystrophy | Adrenomyeloneuropathy | LBSL | Leukoencephalopathy With Brainstem and Spinal Cord Involvement and Lactate Elevation | Leukoencephalopathy With Brain Stem and Spinal Cord Involvement and High Lactate Syndrome (Disorder)United States
-
Shandong UniversityThe First Affiliated Hospital with Nanjing Medical University; Changhai Hospital and other collaboratorsRecruitingReproductive Techniques, Assisted | DNA MethylationChina, Thailand
-
International Rett Syndrome FoundationBaylor College of Medicine; Children's Hospital of Philadelphia; University of... and other collaboratorsRecruitingNervous System Diseases | Neurologic Manifestations | Neurobehavioral Manifestations | Genetic Diseases, X-Linked | Intellectual Disability | Neurodevelopmental Disorders | Neurologic Disorder | Rett Syndrome | Genetic Disease | Rett Syndrome, AtypicalUnited States
-
PfizerPfizerRecruitingSickle Cell DiseaseUnited States, Nigeria, Kenya, Lebanon
-
National Cancer Institute (NCI)RecruitingLynch SyndromeUnited States, Puerto Rico
-
AbiliTech Medical Inc.Richard M. Schulze Family FoundationRecruitingCerebral Palsy | Muscular Dystrophies | Duchenne Muscular Dystrophy | Becker Muscular Dystrophy | Spinal Muscular Atrophy | Limb Girdle Muscular Dystrophy | FSHDUnited States
-
AbbVieRecruitingCNV | AMD | nAMD | Wet Age-related Macular Degeneration | wAMD | WetAMDUnited States, Puerto Rico, Canada
-
PfizerRecruiting
-
Novo Nordisk A/SRecruitingSickle Cell DiseaseSpain, United States, United Kingdom, Canada, Italy, India, Turkey, Greece, South Africa, Oman, France, Lebanon
-
Eva Morava-KoziczNot yet recruitingSLC35A2-CDG - Solute Carrier Family 35 Member A2 Congenital Disorder of GlycosylationUnited States
-
Eva Morava-KoziczNot yet recruitingPGM1-CDG - Phosphoglucomutase 1-Related Congenital Disorder of GlycosylationUnited States
-
Hospital Vall d'HebronRecruitingColorectal Cancer | Liver Metastases | Genetic ChangeSpain
-
Murdoch Childrens Research InstituteNational Health and Medical Research Council, Australia; Royal Children's Hospital and other collaboratorsRecruitingCommunicable Diseases | Quality of Life | Inflammation | Obesity | Congenital Abnormalities | Genetics | Healthy Aging | Child Development | Diet | Mental Health | Disability | Injuries | Cognition | Child Health | Environmental Exposure | Noncommunicable Diseases | Physical Fitness | Intergenerational Relations | Social Determinants... and other conditionsAustralia
-
King's College Hospital NHS TrustKing's College London; University College London Hospitals; University of Sheffield and other collaboratorsRecruitingSickle Cell DiseaseUnited Kingdom
-
AstraZenecaRecruitingNeurofibromatosis Type 1Spain, United Kingdom, Israel, France, Italy, Portugal, Switzerland, Germany, Austria
-
Ann & Robert H Lurie Children's Hospital of ChicagoPatient-Centered Outcomes Research Institute; Johns Hopkins University; University... and other collaboratorsNot yet recruiting
-
Denali Therapeutics Inc.RecruitingMucopolysaccharidosis IIUnited States, Spain, United Kingdom, Czechia, France, Canada, Italy, Belgium, Netherlands, Germany, Argentina, Sweden, Turkey, Brazil, Colombia
-
University Hospital, BordeauxNot yet recruiting
-
Chinese University of Hong KongHealth and Medical Research FundRecruitingFirst Trimester Abortion | Surgical Abortion | Miscarriage With AfibrinogenemiaHong Kong
-
Erin RothwellNational Human Genome Research Institute (NHGRI)RecruitingPregnancy | Shared Decision Making | Genetic Testing | Genetic Counseling | Prenatal DisorderUnited States
-
Tetra Discovery PartnersRecruitingFragile X SyndromeUnited States
-
PTC TherapeuticsRecruitingA Study to Evaluate the Safety and Efficacy of PTC518 in Participants With Huntington's Disease (HD)Huntington DiseaseUnited States, Austria, Spain, United Kingdom, Australia, France, Germany, Netherlands, Italy, New Zealand, Canada
-
University of Maryland, BaltimoreRecruitingFamilial Hypercholesterolemia | Long QT Syndrome | Genetic Testing | EthicsUnited States
-
Medical University of BialystokRecruitingObesity | PreDiabetes | Prediabetic StatePoland
-
Novo Nordisk A/SRecruitingSGA, Turner Syndrome, Noonan Syndrome, ISSKorea, Republic of, United States, Ireland, United Kingdom, Finland, France, Netherlands, Japan, Thailand, Belgium, China, Israel, Brazil, India, Portugal, Austria, Bulgaria, Canada, Croatia, Germany, Greece, Malaysia, Poland, Saudi Arabia and more
-
Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsRecruitingSickle Cell Disease | Hemoglobinopathies | Hematological Diseases | Hydroxyurea Failure | Hydroxyurea IntoleranceUnited States, Italy, United Kingdom, Germany
-
Federal State Budget Institution Research Center...Recruiting
-
Freeline TherapeuticsRecruitingGaucher Disease, Type 1Spain, Israel, United States, United Kingdom, Brazil, Germany, Paraguay
-
Baylor College of MedicineRecruiting
-
Jaeb Center for Health ResearchDepartment of Health and Human Services; Food and Drug Administration (FDA); Conquering...RecruitingGyrate Atrophy | Gyrata of Choroid and Retina; Atrophy | Ornithine-δ-aminotransferase | OAT | Chorioretinal DegenerationUnited States, Finland, France, United Kingdom, Germany, Brazil, Canada
-
University of EdinburghEuropean Research CouncilRecruitingPaget Disease | Paget Disease of BoneUnited Kingdom
-
Novo Nordisk A/SRecruitingHaemophilia A With or Without InhibitorsIndia, China, Korea, Republic of, Canada, Spain, Netherlands, South Africa, United States, Israel, Poland, United Kingdom, Italy, Japan, Lithuania, Portugal, Switzerland, Taiwan
-
Bionano GenomicsColumbia University; University of Iowa; Medical College of Wisconsin; Augusta... and other collaboratorsRecruitingIntellectual Disability | Autism Spectrum Disorder | Fragile X Syndrome | Developmental Disability | Congenital Anomaly | Facioscapulohumeral Muscular Dystrophy 1United States
-
University of FloridaNational Human Genome Research Institute (NHGRI)RecruitingSickle Cell Disease | Sickle Cell TraitUnited States
-
Edgewise Therapeutics, Inc.Medpace, Inc.; SYSNAV; ImagingNMDRecruitingBecker Muscular DystrophyUnited States, Spain, Netherlands, United Kingdom
-
Arkansas Children's Hospital Research InstituteRecruitingPrimary Ciliary DyskinesiaUnited States
-
Odense University HospitalNovo Nordisk A/S; Department of Nephrology, Odense University Hospital; The A... and other collaboratorsRecruitingKidney Failure, Chronic | Kidney Injury | Risk Reduction | Contrast-induced NephropathyDenmark
-
SanofiRecruitingFabry DiseaseItaly, United States, Austria, China, Czechia, Denmark, France, Germany, Greece, Japan, Korea, Republic of, Netherlands, Norway, Spain, Taiwan, Turkey, United Kingdom, Canada, Poland
-
Arbor Research Collaborative for HealthRecruiting
-
Goldman, Butterwick, Fitzpatrick and GroffGalderma R&DNot yet recruitingSkin LaxityUnited States
-
Washington University School of MedicineNational Institute on Aging (NIA); Alzheimer's Association; Eisai Inc.; Accelerating...RecruitingDementia | Alzheimers Disease | Alzheimers Disease, FamilialUnited States, Canada, Italy, Argentina, Australia, Colombia, Netherlands, Puerto Rico, Spain, United Kingdom, France, Ireland, Mexico, Brazil, Japan, Germany
-
Virginia Commonwealth UniversityEdgewise Therapeutics, Inc.RecruitingMuscular Dystrophies | Becker Muscular Dystrophy | Muscular Dystrophy in Children | Muscular Dystrophy, BeckerUnited States, New Zealand, United Kingdom
-
Great Ormond Street Hospital for Children NHS Foundation...National Institute for Health Research, United Kingdom; The Freya FoundationRecruitingPyruvate Dehydrogenase Complex Deficiency | Pyruvate Dehydrogenase E1 Alpha Deficiency | Pyruvate Dehydrogenase E1-Beta Deficiency | Pyruvate Dehydrogenase E2 Deficiency | Pyruvate Dehydrogenase Phosphatase DeficiencyUnited Kingdom
-
Seagen Inc.Merck Sharp & Dohme LLCRecruitingColorectal NeoplasmsUnited States, Canada, Italy, Argentina, United Kingdom, China, Japan, Belgium, France, Korea, Republic of, Spain, Taiwan, Brazil, Ireland, Netherlands, Australia, Slovakia, Chile, Poland, Norway, Switzerland, Austria, Germany, Portugal, Gree... and more
-
4D Molecular TherapeuticsRecruiting
-
Essentia HealthSt. Luke's Hospital of Duluth; WHITESIDE Institute for Clinical ResearchRecruitingFamilial Hypercholesterolemia | Genetic Disease | Cholesterol, ElevatedUnited States
-
Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy...RecruitingHaploidentical Hematopoietic Cell Transplantation Using TCR Alpha/Beta and CD19 Depletion (HAPLOTAB)Myelodysplastic Syndromes | Primary Immunodeficiency Diseases | Hemoglobinopathies | Chronic Myeloid Leukemia | Cytopenia | Severe Aplastic Anemia | Bone Marrow Failure Syndrome | Acute Myeloid Leukemia in Remission | Hemophagocytic Lymphohistiocytoses | Acute Lymphoblastic Leukemia in Remission | Severe...United States
-
SanofiRecruiting