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Search clinical trials for: Inherited Retinal Disorders
Total 149351 results
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Shanghai General Hospital, Shanghai Jiao Tong University...RecruitingInherited Retinal DystrophiesChina
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University Hospital, ToulouseFrench network for inherited hemorragic diseases; National Reference Centre...RecruitingThrombocytopeniaFrance
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McMaster UniversityRecruiting
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Masonic Cancer Center, University of MinnesotaRecruitingMyelodysplastic Syndromes | Fanconi Anemia | Dyskeratosis Congenita | Severe Aplastic Anemia | Bone Marrow Failure | T Cell Receptor Alpha/Beta Depletion | Telomere Biology DisorderUnited States
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Centre Hospitalier Universitaire, AmiensRecruitingAge-related Macular Degeneration (AMD)France
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Shanghai Eye Disease Prevention and Treatment CenterRecruitingDiabetic Retinopathy | Visual Impairment | Diabetic MaculopathyChina
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University of NebraskaNational Cancer Institute (NCI); VA Nebraska Western Iowa Health Care System; Virginia Mason Hospital/Medical CenterRecruitingDiabetes Mellitus, Type 2 | PreDiabetes | Genetic Predisposition to Disease | Chronic Pancreatitis | Inherited Disease | Pancreas CystUnited States
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Second Affiliated Hospital, School of Medicine,...RecruitingCognitive Dysfunction | Cerebral Small Vessel Diseases | RetinopathyChina
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Centre Hospitalier Universitaire DijonRecruitingType 1 Diabetes PatientsFrance
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Randy KardonRecruitingLeber Hereditary Optic Neuropathy | Ischemic Optic Neuropathy | Hemianopia | Branch Retinal Artery Occlusion | Acute Zonal Occult Outer RetinopathyUnited States
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Universitaire Ziekenhuizen KU LeuvenRecruitingGlaucoma | Age-Related Macular Degeneration | Diabetic Retinopathy | Dementia | Alzheimer Disease | Mild Cognitive Impairment | Alzheimer DementiaBelgium
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eyeDNA TherapeuticsRecruitingRetinitis PigmentosaFrance
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World Federation of HemophiliaRecruitingHemophilia A | Hemophilia B | Von Willebrand DiseasesCanada
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GenSight BiologicsRecruitingNon-syndromic Retinitis PigmentosaUnited States, France, United Kingdom
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Duke UniversityUniversity of Edinburgh in Scotland; Tan Tock Seng Hospital in Singapore; Queens...RecruitingMultiple Sclerosis | Parkinson's Disease | Traumatic Brain Injury | Down Syndrome | Mild Cognitive Impairment | Frontotemporal Dementia | Huntington Disease | Amyotrophic Lateral Sclerosis (ALS) | Alzheimer's Disease | Concussion | Post-Traumatic Stress Disorder | Neuro-Degenerative Disease | Lewy Body Dementia | Normal... and other conditionsUnited States
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University of MiamiRecruitingMultiple Sclerosis | Diabetic Retinopathy | Dementia | Dry Eye Syndromes | Presbyopia | MyopiaUnited States
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Hadassah Medical OrganizationHebrew University of JerusalemRecruitingRetinal Degeneration | Retinitis Pigmentosa | CannabisIsrael
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University Hospital, LilleRecruitingVon Willebrand DiseasesFrance
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St. Jude Children's Research HospitalRecruitingPancreatic Cancer | Hodgkin Lymphoma | Lynch Syndrome | Tuberous Sclerosis | Fanconi Anemia | AML | Non Hodgkin Lymphoma | Familial Adenomatous Polyposis | Acute Leukemia | Nevoid Basal Cell Carcinoma Syndrome | Neurofibromatosis Type 1 | Neuroblastoma | Retinoblastoma | MDS | Rhabdomyosarcoma | Von Hippel-Lindau Disease | Adrenocortical Carcinoma and other conditionsUnited States
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Children's Hospital of PhiladelphiaRecruitingParoxysmal Nocturnal Hemoglobinuria | Acquired Aplastic Anemia | Inherited Bone Marrow Failure SyndromesUnited States
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MD Stem CellsRecruitingGlaucoma | Age-Related Macular Degeneration | Macular Degeneration | Retinitis Pigmentosa | Leber Hereditary Optic Neuropathy | Optic Atrophy | Blindness | Optic Neuropathy | Vision, Low | Retinal Disease | Stargardt Disease | Maculopathy | Retinopathy | Optic Nerve Disease | Nonarteritic Ischemic Optic Neuropathy | Vision... and other conditionsUnited States, United Arab Emirates
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University College, LondonMedical Research CouncilRecruiting
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PedNet Haemophilia Research FoundationLund University HospitalRecruitingFactor IX Deficiency | Factor VIII DeficiencyNorway, Austria, Belgium, Canada, Czechia, Denmark, Finland, France, Germany, Greece, Ireland, Israel, Italy, Netherlands, Portugal, Spain, Sweden, Switzerland, United Kingdom
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Mayo ClinicRecruitingHematologic Neoplasms | Myeloid Malignancy | Cytopenia | Bone Marrow Failure Syndrome | Clonal Cytopenia of Undetermined Significance | Clonal Hematopoiesis of Indeterminate Potential | Low Risk Myelodysplastic Syndrome | Inherited Bone Marrow Failure Syndrome | Clonal Expansion | Hereditary Neoplastic... and other conditionsUnited States
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Baxalta now part of ShireTakeda Development Center Americas, Inc.RecruitingVon Willebrand DiseaseUnited States, Belgium, Spain, Italy, Turkey, Germany, Austria, France, Czechia, Russian Federation, Ukraine, United Kingdom, Netherlands
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Children's Hospital of PhiladelphiaRecruiting
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Goethe UniversitySociety for Thrombosis and Haemostasis Research (Germany)RecruitingHemophilia A | Hemophilia B | Children | Drug Specific AntibodiesGermany
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Unity Health TorontoRecruitingRhegmatogenous Retinal DetachmentCanada
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Brugmann University HospitalRecruiting
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Medical University of ViennaRecruitingHealthy | Alzheimer Disease | Mild Cognitive ImpairmentAustria
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Assistance Publique Hopitaux De MarseilleRecruitingInherited Metabolic Diseases Requiring Restrictive and Specific DietFrance
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Swiss Hemophilia NetworkRecruiting
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Grifols Therapeutics LLCInstituto Grifols, S.A.Recruiting
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Karolinska InstitutetRecruiting
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Joanne Kurtzberg, MDThe Marcus FoundationRecruitingMucopolysaccharidosis II | Brain Diseases, Metabolic, Inborn | Adrenoleukodystrophy | Batten Disease | Leukodystrophy, Metachromatic | Leukodystrophy, Globoid Cell | Alpha-Mannosidosis | Tay-Sachs Disease | Pelizaeus-Merzbacher Disease | Sandhoff Disease | Neimann Pick Disease | Sanfilippo MucopolysaccharidosesUnited States
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Haemophilia Centre Rhine MainSkane University Hospital; University of Bonn; Hopital Cardiologique Louis Pradel...Recruiting
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Masonic Cancer Center, University of MinnesotaRecruitingSickle Cell Disease | Severe Congenital Neutropenia | Paroxysmal Nocturnal Hemoglobinuria | Glanzmann Thrombasthenia | Shwachman-Diamond Syndrome | Diamond Blackfan Anemia | Transfusion Dependent Alpha- or Beta- Thalassemia | Non-Malignant Hematologic DisordersUnited States
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Masonic Cancer Center, University of MinnesotaRecruitingHurler Syndrome | Sphingolipidoses | Peroxisomal Disorders | Metachromatic Leukodystrophy | Alpha-Mannosidosis | Hunter Syndrome | Mucopolysaccharidosis Disorders | Maroteaux Lamy Syndrome | Sly Syndrome | Fucosidosis | Aspartylglucosaminuria | Glycoprotein Metabolic Disorders | Recessive Leukodystrophies | Globoid... and other conditionsUnited States
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Paul SzabolcsRecruitingCongenital Bone Marrow Failure Syndromes | Inflammatory Conditions | Primary Immunodeficiency (PID) | Inherited Metabolic Disorders (IMD) | Hereditary Anemias | Systemic Juvenile Idiopathic Arthritis (sJIA)United States
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The Familial Hypercholesterolemia FoundationRecruitingHypercholesterolemiaUnited States
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National Institute of Neurological Disorders and...RecruitingMotor Neuron Disease | Neuromuscular Disease | Inherited Neuromuscular Conditions | Inherited NeuropathiesUnited States
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Medical University of ViennaRecruiting
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Washington University School of MedicineRecruitingSevere Combined Immunodeficiency | Chronic Granulomatous Disease | DiGeorge Syndrome | Hemophagocytic Lymphohistiocytosis | Wiskott-Aldrich Syndrome | X-linked Lymphoproliferative Syndrome | X-linked Agammaglobulinemia | Chediak-Higashi Syndrome | IPEX | Autoimmune Lymphoproliferative Syndrome | Common Variable... and other conditionsUnited States
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University of Colorado, DenverRecruitingHearing Loss | Smith-Lemli-Opitz Syndrome | Cone-Rod DystrophyUnited States
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Washington University School of MedicineEli Lilly and Company; Hoffmann-La Roche; Avid Radiopharmaceuticals; National Institute... and other collaboratorsRecruitingDementia | Alzheimers Disease | Alzheimers Disease, FamilialUnited States, Canada, Italy, Argentina, Australia, Colombia, France, Ireland, Mexico, Netherlands, Puerto Rico, Spain, United Kingdom, Brazil, Japan, Germany
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Medical University of ViennaRecruitingAmblyopia ex Strabismus | Amblyopia ex AnisometropiaAustria
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Columbia UniversityNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingMitochondrial Diseases | Mitochondrial Disorders | Mitochondrial Genetic Disorders | Disorder of Mitochondrial Respiratory Chain Complexes | Deletion and Duplication of Mitochondrial DNAUnited States, Canada
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Masonic Cancer Center, University of MinnesotaRecruitingHemoglobinopathies | Immunodeficiencies | Hematologic DisordersUnited States
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Masonic Cancer Center, University of MinnesotaRecruitingCommon Variable Immunodeficiency | Chronic Granulomatous Disease | Hemophagocytic Lymphohistiocytosis | Wiskott-Aldrich Syndrome | X-linked Lymphoproliferative Disease | Langerhan's Cell Histiocytosis | Chediak-Higashi Syndrome | Griscelli Syndrome | Bare Lymphocyte Syndrome | SCID | Omenn's Syndrome | Reticular... and other conditionsUnited States
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National Institute of Neurological Disorders and...RecruitingMuscular Dystrophies | Inherited Neuromuscular Conditions | Inherited Neuropathies | Muscle Myopathies | Hereditary Spastic ParaplegiasUnited States