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Search clinical trials for: genetic disorders
Total 154527 results
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Red Nucleus Enterprise Solutions, LLCRecruiting
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BiogenNot yet recruiting
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.Not yet recruiting
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Assiut UniversityNot yet recruitingCardiovascular Diseases | Wilson's Disease
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SanofiRecruiting
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A2 Biotherapeutics Inc.Tempus AIRecruitingCancer | Colorectal Cancer | Ovarian Neoplasms | Ovarian Cancer | NSCLC | Lung Cancer | Rectal Cancer | Non Small Cell Lung Cancer | Mesothelioma | Mesothelioma, Malignant | Colon Cancer | Pancreas Cancer | Colorectal Adenocarcinoma | Solid Tumor, Adult | CRC | Pancreatic Neoplasm | Ovary Cancer | NSCLC, Recurrent | Non-Small Cell... and other conditionsUnited States
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Institut National de la Santé Et de la Recherche...RecruitingOCD | Tic Disorders | Gilles de la Tourette SyndromeFrance
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University Hospital OlomoucUniversity Hospital Ostrava; Tomas Bata Hospital, Czech Republic; General University... and other collaboratorsRecruitingCushing Syndrome | Pheochromocytoma | Adrenocortical Carcinoma | Adrenal Cortex Diseases | Adrenocortical Adenoma | Adrenal Tumor | Adrenalectomy; Status | Adrenal Mass | Adrenal Hyperplasia | Adrenal Disease | Adrenocortical Tumor | Conn Adenoma | Adrenal Gland MetastasisCzechia
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East Kent Hospitals University NHS Foundation TrustNot yet recruitingHaemophiliaUnited Kingdom
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Brigham and Women's HospitalChildren's Hospital of Philadelphia; University of Michigan; University of Southern... and other collaboratorsRecruitingObstructive Sleep Apnea | Down SyndromeUnited States
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University Hospital, BordeauxNot yet recruitingNervous System Diseases | Genetic Disease
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Inozyme PharmaRecruitingGeneralized Arterial Calcification of Infancy | Autosomal Recessive Hypophosphatemic Rickets | Ectonucleotide Pyrophosphatase/Phosphodiesterase1 DeficiencyUnited States, United Kingdom, Canada
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LG ChemNot yet recruitingPOMC Deficiency Obesity | PCSK1 Deficiency Obesity | LEPR Deficiency ObesityFrance, United Kingdom
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Rachel G. Greenberg, MD, MB, MHSEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsNot yet recruitingHyperactivity in Children With Down Syndrome | Impulsivity in Children With Down SyndromeUnited States
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Qilu Hospital of Shandong UniversityNot yet recruiting
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Rigshospitalet, DenmarkRecruitingPolyneuropathies | Diabetic Polyneuropathy | Chronic Inflammatory Demyelinating Polyneuropathy (CIDP) | POEMS Syndrome | Multifocal Motor Neuropathy | Charcot-Marie-Tooth | hATTR Amyloidosis | Vasculitic Neuropathy | Idiopathic NeuropathyDenmark
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SanofiRecruiting
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Beijing Children's HospitalOffice for Rare Conditions Registries, University of GlasgowRecruitingGrowth Disorders | Growth Hormone TreatmentChina
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Institut National de la Santé Et de la Recherche...RecruitingMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VI | Mucopolysaccharidosis III | Mucopolysaccharidosis IV | Mucopolysaccharidosis VII | Multiple Sulfatase Deficiency Disease | Mucopolysaccharidosis IXFrance
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Ragaee Saeed MahmoudRecruiting
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TakedaRecruitingHunter SyndromeCanada, France
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Masonic Cancer Center, University of MinnesotaRecruiting
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Children's Health IrelandBelfast Health and Social Care Trust; University of Edinburgh; University Hospital... and other collaboratorsRecruitingQuality of Life | Obstructive Sleep Apnea | Down Syndrome | Behavior | Adherence, TreatmentUnited Kingdom, Ireland
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Centre d'Investigation Clinique et Technologique...Recruiting
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Sun Yat-Sen Memorial Hospital of Sun Yat-Sen UniversityNot yet recruitingAcute Leukemia | Thalassemia MajorChina
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Ruijin HospitalNot yet recruitingLymphoma | DLBCL - Diffuse Large B Cell LymphomaChina
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TiumBio Co., Ltd.RecruitingHemophilia A | Hemophilia B | Blood Coagulation DisordersKorea, Republic of
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ExoRNA BioscienceRecruiting
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Emalex Biosciences Inc.RecruitingTourette SyndromeUnited States, Canada
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University of ReginaProvincial Health Services Authority; Saskatchewan Health Authority - Regina...Not yet recruitingMental Health | Cystic Fibrosis in Children | Siblings | Internet-based InterventionCanada
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SanofiRecruitingFabry's DiseaseUnited States
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Minovia Therapeutics Ltd.RecruitingMitochondrial Diseases | Pearson SyndromeIsrael
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Friedreich's Ataxia Research AllianceRecruitingFriedreich AtaxiaUnited States, Canada, New Zealand, Australia, France, Austria, Belgium, Brazil, Czechia, Germany, Greece, Ireland, Italy, Spain, United Kingdom, India, Netherlands
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Stanford UniversityNot yet recruitingLiver Failure | Liver Cirrhosis | Hemophilia A | Hemophilia B | Hemophilia | Liver Transplant Disorder | Coagulation Factor DeficiencyUnited States
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Fred Hutchinson Cancer CenterNational Cord Blood NetworkRecruitingAcute Myeloid Leukemia | Acute Lymphoblastic Leukemia | Non-Hodgkin Lymphoma | Myelodysplastic Syndrome | Hematopoietic and Lymphoid System Neoplasm | Blastic Plasmacytoid Dendritic Cell Neoplasm | Myeloproliferative Neoplasm | Acute Leukemia of Ambiguous Lineage | Mixed Phenotype Acute Leukemia | Chronic...United States
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Second Affiliated Hospital, School of Medicine,...Not yet recruiting
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Ionis Pharmaceuticals, Inc.RecruitingMethyl CpG Binding Protein 2 (MECP2) Duplication SyndromeUnited States
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University of ReginaProvincial Health Services Authority; Saskatchewan Health Authority - Regina...RecruitingCystic Fibrosis | Mental Health | Siblings | Internet-based InterventionCanada
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Jiangsu Gensciences lnc.RecruitingHemophilia | Hemophilia A With Inhibitor | Male | Hemophilia B With InhibitorChina
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Beijing Suncadia Pharmaceuticals Co., LtdNot yet recruitingHomozygous Familial Hypercholesterolemia
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CSL BehringRecruiting
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Fundacion para la Investigacion Biomedica del Hospital...Fundación Mutua MadrileñaRecruiting
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Recursion Pharmaceuticals Inc.RecruitingSolid Tumor | APC Gene Mutation | AXIN1 Gene MutationUnited States
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University Hospital, AngersNot yet recruitingNicotinamide Adverse Reaction
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NewAmsterdam PharmaRecruitingDyslipidemias | Hypercholesterolemia | Familial Hypercholesterolemia | High Cholesterol | ASCVDUnited States
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CSL BehringRecruiting
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Shandong UniversityNot yet recruitingPeutz-Jeghers Syndrome | Small Bowel PolypChina
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ECOG-ACRIN Cancer Research GroupNational Cancer Institute (NCI)RecruitingHodgkin Lymphoma | Non-Hodgkin LymphomaUnited States
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Gazi UniversityRecruitingPrimary Immunodeficiency DiseasesTurkey
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Assiut UniversityRecruitingBehcet's Disease With Multisystem InvolvementEgypt