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Search clinical trials for: neutral lipid storage disease
Total 385121 results
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Mansoura University Children HospitalUnknownHCV | Gaucher DiseaseEgypt
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Amicus TherapeuticsCompletedFabry DiseaseUnited States, Italy, Spain, Turkey, Brazil, Canada, United Kingdom, France, Poland, Australia, Egypt, Argentina, Denmark
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Amicus TherapeuticsCompletedFabry DiseaseUnited States
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Ulla Feldt-RasmussenCompleted
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Ulla Feldt-RasmussenCompleted
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PfizerCompletedGaucher DiseaseIsrael, South Africa, Paraguay
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PfizerCompletedGaucher DiseaseUnited States, Chile, United Kingdom, Israel, Canada, Spain, South Africa, Italy
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PfizerCompletedGaucher DiseaseUnited Kingdom, Canada, Israel, United States, Australia, Spain
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PfizerCompletedGaucher DiseaseChile, United Kingdom, Canada, Spain, Israel, United States, Australia, South Africa
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Amicus TherapeuticsCompletedFabry DiseaseUnited States, Australia, France, United Kingdom, Brazil, Canada
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Amicus TherapeuticsTerminatedFabry DiseaseUnited Kingdom, United States, Australia, Brazil, France
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Amicus TherapeuticsTerminatedFabry DiseaseAustralia, United States, Italy, Spain, Belgium, Turkey, Brazil, Argentina, United Kingdom, Denmark, France, Canada, Egypt
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Amicus TherapeuticsCompletedGaucher Disease | Gaucher Disease, Type 1 | Type 1 Gaucher DiseaseUnited States
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PfizerCompletedGaucher DiseaseIsrael, Paraguay, South Africa
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PfizerNo longer availableGaucher DiseaseUnited States, Israel
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Amicus TherapeuticsCompletedFabry DiseaseFrance, United Kingdom
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Rennes University HospitalCompleted
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Amicus TherapeuticsCompletedGaucher Disease | Gaucher Disease, Type 1 | Type 1 Gaucher DiseaseUnited Kingdom, Israel, South Africa, United States
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Amicus TherapeuticsCompletedGaucher Disease | Gaucher Disease, Type 1 | Type 1 Gaucher DiseaseUnited Kingdom, United States
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Chiayi Christian HospitalSanofiUnknown
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase Deficiency | LAL-Deficiency | Cholesterol Ester Storage Disease (CESD)France, United Kingdom, United States, Canada, Czechia
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Yasmeen Abd Elbaset HamzaaUnknownGaucher Disease
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Innovations for Poverty ActionUniversity of California, Berkeley; Tufts University; University of California... and other collaboratorsCompleted
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PfizerTerminatedCardiovascular DiseaseFinland, United States, Netherlands, Spain, Korea, Republic of, China, Israel, Belgium, Germany, Australia, Czechia, Taiwan, Denmark, United Kingdom, Hungary, Poland, France, Mexico, Turkey, Canada, New Zealand, Colombia, Switzerland, Irelan... and more
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Idorsia Pharmaceuticals Ltd.Completed
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University Hospital, RouenUnknownAnderson-Fabry DiseaseFrance
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PfizerBristol-Myers SquibbCompletedAtrial FibrillationKorea, Republic of, Spain, United States, Israel, Germany, Belgium, Japan, Sweden, Canada, Denmark, Italy, Romania
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Zymenex A/SCompletedInfantile Globoid Cell LeukodystrophyUnited States
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National Institute of Diabetes and Digestive and...Hennepin County Medical Center, MinneapolisCompletedDiabetic NephropathyUnited States
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Baylor Research InstituteTexas Scottish Rite Hospital for ChildrenWithdrawnGaucher Disease Type 1 | Gaucher Disease Type 3United States
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Eunice Kennedy Shriver National Institute of Child...Washington University School of Medicine; Weill Medical College of Cornell...CompletedNeimann-Pick DiseaseUnited States
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Masonic Cancer Center, University of MinnesotaCompletedMucopolysaccharidosis | Hurler Syndrome | Sphingolipidoses | Peroxisomal Disorders | Krabbe Disease | Adrenoleukodystrophy (ALD) | Hunter Syndrome | Sly Syndrome | Fucosidosis | Aspartylglucosaminuria | Alpha Mannosidosis | Metachromatic Leukodystrophy (MLD) | Maroteaux-Lamy SyndromeUnited States
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ProtalixWithdrawn
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Masonic Cancer Center, University of MinnesotaCompletedNiemann-Pick Disease | Wolman Disease | Adrenoleukodystrophy | Batten Disease | Metachromatic Leukodystrophy | GM1 Gangliosidosis | Fucosidosis | Globoid Cell Leukodystrophy | Gaucher's Disease | Tay Sachs Disease | Sandhoff DiseaseUnited States
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Masonic Cancer Center, University of MinnesotaTerminatedSphingolipidoses | Niemann-Pick Disease, Type C | Krabbe Disease | Sly Syndrome | Fucosidosis | Aspartylglucosaminuria | Alpha Mannosidosis | Hurler's Syndrome | Maroteaux-Lamy Syndrome | Wolman's Disease | Niemann-Pick Disease Type BUnited States
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University Hospital HeidelbergCompletedFabry Disease | Chronic Abdominal Pain | Chronic Pain in the ExtremitiesGermany
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Greenovation Biotech GmbHFGK Clinical Research GmbHCompleted
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University Hospital, CaenUnknown
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)CompletedChronic Myelomonocytic Leukemia | Adult Acute Megakaryoblastic Leukemia (M7) | Adult Acute Minimally Differentiated Myeloid Leukemia (M0) | Adult Acute Monoblastic Leukemia (M5a) | Adult Acute Monocytic Leukemia (M5b) | Adult Acute Myeloblastic Leukemia With Maturation (M2) | Adult Acute Myeloblastic... and other conditionsUnited States
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Ankara UniversityAlexion PharmaceuticalsCompleted
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University of WashingtonNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsUnknown
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McGill University Health Centre/Research Institute...CompletedFamilial Dysautonomia | Tay Sachs Disease | Canavan DiseaseCanada
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Amicus TherapeuticsCompleted
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Taipei Veterans General Hospital, TaiwanSanofiUnknownFabry Disease, Cardiac Variant
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ISU Abxis Co., Ltd.CompletedGaucher Disease, Type 1
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National Institute of Neurological Disorders and...CompletedType 2 Gaucher DiseaseUnited States
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National Institute of Neurological Disorders and...CompletedGaucher DiseaseUnited States
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National Institute of Neurological Disorders and...National Institute of Neurological Disorders and Stroke@@@Shire Human Genetic...Completed
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National Institute of Neurological Disorders and...CompletedFabry DiseaseUnited States