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Search clinical trials for: Muscular Dystrophies
Total 12848 results
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Charite University, Berlin, GermanyCompletedDuchenne Muscular DystrophyGermany
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Expansion Therapeutics, Inc.CompletedMyotonic Dystrophy | Myotonic Dystrophy, Type 1 (DM1)United States
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Taiho Pharmaceutical Co., Ltd.Completed
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ReveraGen BioPharma, Inc.University of Pittsburgh; Cooperative International Neuromuscular Research...CompletedDuchenne Muscular DystrophyUnited States, Canada, United Kingdom, Sweden, Australia, Israel
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Wave Life Sciences Ltd.TerminatedDuchenne Muscular DystrophyUnited States, Belgium, United Kingdom, Czechia, Canada, France, Italy, Sweden
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Rare Disease Research, LLCSarepta Therapeutics, Inc.TerminatedDuchenne Muscular DystrophyUnited States
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Sarepta Therapeutics, Inc.CompletedDuchenne Muscular DystrophyUnited States
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BioLeaders CorporationCompleted
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Newcastle-upon-Tyne Hospitals NHS TrustCompletedDuchenne Muscular DystrophyUnited Kingdom
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Newcastle-upon-Tyne Hospitals NHS TrustCompletedMyotonic Dystrophy Type 1United Kingdom
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Mallinckrodt ARD LLCTerminatedMuscular Dystrophy, DuchenneSpain, Bulgaria, Italy, United States, Mexico, Israel, Serbia, Turkey
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Marmara UniversityUnknownDuchenne Muscular Dystrophy
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Gillette Children's Specialty HealthcareCompletedCerebral Palsy | Muscular Dystrophy | Osteopenia | Rett Syndrome | Spinal Muscular Atrophy | Spina BifidaUnited States
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Gillette Children's Specialty HealthcareUniversity of MinnesotaCompletedSpinal Muscular Dystrophy | Neuromuscular DisabilityUnited States
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Medical University of BialystokUnknownIncrease Muscle Strength in Patients With Muscular DystrophyPoland
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University of Sao PauloCompletedDuchenne Muscular Dystrophy
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Sarepta Therapeutics, Inc.CompletedDuchenne Muscular Dystrophy (DMD)United States
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Sarepta Therapeutics, Inc.Completed
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Children's Hospital Medical Center, CincinnatiIpsen; Charley's FundCompletedDuchenne Muscular DystrophyUnited States
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University Hospital, MontpellierAgence de La BiomédecineActive, not recruitingFragile X Syndrome | Huntington Disease | Myotonic Dystrophy 1France
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Hoffmann-La RocheCompletedDuchenne Muscular DystrophyUnited States, Belgium, Canada, Australia, Japan, France, Netherlands, Spain, Argentina, Germany, Italy, United Kingdom, Sweden
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Gokce Yagmur Gunes GencerHacettepe UniversityCompletedMuscular Dystrophy, Duchenne | Upper Extremity | Respiratory FunctionsTurkey
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Swiss Federal Institute of TechnologyCompletedMuscle Weakness | Muscular Dystrophies | Muscular Dystrophy | Muscular Dystrophy, Facioscapulohumeral | Scapular Dyskinesis | Muscular WeaknessGermany, Switzerland
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PfizerTerminatedDuchenne Muscular DystrophyUnited States, Australia, Canada, United Kingdom, Japan, Bulgaria, Italy, Poland
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PTC TherapeuticsCompletedDuchenne Muscular Dystrophy | Becker Muscular Dystrophy | DystrophinopathyUnited Kingdom, Canada, Germany, Spain, Sweden, Italy, Australia, Belgium, France, Israel
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University Hospital, CaenUniversity Hospital, Rouen; Centre Hospitalier Universitaire, Amiens; University... and other collaboratorsTerminatedMuscular Dystrophy, Oculopharyngeal | PtosisFrance
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Catabasis PharmaceuticalsTerminatedDuchenne Muscular DystrophyUnited States, Canada, Australia, United Kingdom, Germany, Sweden
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PfizerTerminatedDuchenne Muscular DystrophyUnited States, Canada, United Kingdom, Japan, Italy
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Hoffmann-La RocheTerminatedMuscular Dystrophy (DMD)United States, Canada
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Gaziosmanpasa Research and Education HospitalCompletedCOVID-19 | Cerebral Palsy | Muscular Dystrophies | Disabilities MultipleTurkey
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedDuchenne Muscular DystrophyUnited States
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University of Sao PauloCompletedDuchenne Muscular DystrophyBrazil
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Children's Hospital Medical Center, CincinnatiCompletedDuchenne Muscular Dystrophy | Spinal Muscular Atrophy | Congenital Muscular Dystrophy
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Sarepta Therapeutics, Inc.University College, London; Catholic University of the Sacred Heart; University... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited Kingdom, United States, France, Italy
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Duke UniversityTerminatedInfantile Neuroaxonal DystrophyUnited States
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Newcastle UniversityUnknownHereditary Inclusion Body Myopathy | GNE MyopathyUnited Kingdom
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South Valley UniversityUnknownMuscular DystrophyEgypt
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Processa PharmaceuticalsTerminatedDuchenne Muscular DystrophyUnited States
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Processa PharmaceuticalsTerminated
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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NS Pharma, Inc.Approved for marketingMuscular Dystrophy, Duchenne | DMD
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PTC TherapeuticsTerminatedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States, Spain, Korea, Republic of, Belgium, France, Canada, Australia, United Kingdom, Israel, Italy, Germany, Brazil, Bulgaria, Chile, Czechia, Poland, Sweden, Switzerland, Turkey
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University of FloridaEngage Health Inc.CompletedDuchenne Muscular DystrophyUnited States
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PTC TherapeuticsCompletedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States, Spain, Korea, Republic of, Belgium, France, Canada, Australia, United Kingdom, Israel, Italy, Brazil, Chile, Czechia, Sweden, Switzerland, Turkey, Germany, Poland
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States, United Kingdom
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Altoosi University CollegeBabylon UniversityUnknownCerebral Palsy | Cancer | HIV/AIDS | Muscular Dystrophy | Cystic Fibrosis | Cardiac Anomaly | Batten's DiseaseIraq
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States, Belgium, Australia, Canada, France, Germany, Israel, Italy, Spain, Sweden, United Kingdom
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GlaxoSmithKlineCompleted
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Capricor Inc.CompletedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States
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Centre d'Investigation Clinique et Technologique...Completed