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Search clinical trials for: Nedostatek guanidinoacetátu methyltransferázy (GAMT)
Total 4949 results
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HaEmek Medical Center, IsraelCompleted
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Yale UniversityNational Heart, Lung, and Blood Institute (NHLBI); National Center for Research...CompletedSleep DeprivationUnited States
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University of WuerzburgCompletedAdrenal Insufficiency | Addison's DiseaseGermany
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Lund University HospitalCompletedCardiovascular Diseases
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University of AarhusCompletedAddison Syndrome
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Radboud University Medical CenterUnknownHIV Infections | Vitamin D DeficiencyNetherlands
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Great Lakes Research Into Practice NetworkRobert Wood Johnson Foundation; Agency for Healthcare Research and Quality... and other collaboratorsUnknownTobacco Use Disorder | Alcohol Abuse | Poor Diet | Lack of Physical ActivityUnited States
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The Center for Rheumatic Disease, Allergy, & ImmunologyGrifols Therapeutics LLCCompletedInfections | IgG DeficiencyUnited States
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Saint Louis VA Medical CenterCompleted
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Altus PharmaceuticalsCompleted
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University Hospital, Strasbourg, FranceUnknownTransient Tachypnoea of the NewbornFrance
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University of TurkuOulu University Hospital; University of Helsinki; Tampere UniversityUnknown
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Sheba Medical CenterUnknownInfantile Canavan Disease | Deficiency Disease, AspartoacylaseIsrael
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Eli Lilly and CompanyCompletedMajor Depressive DisorderUnited States
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Pennsylvania College of OptometryNational Eye Institute (NEI)CompletedConvergence InsufficiencyUnited States
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Pennsylvania College of OptometryCompletedConvergence InsufficiencyUnited States
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Singapore National Eye CentreSingapore Eye Research InstituteSuspended
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St. Vincent's Medical CenterInflammation Research Foundation, Marblehead, MA.; NeuroScience, Inc., Osceola...CompletedSleep DeprivationUnited States
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EpicentreMédecins Sans Frontières, France; Embassy of France in Uganda; National Sleeping...TerminatedTrypanosomiasis, AfricanUganda
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London School of Hygiene and Tropical MedicineMedical Research Council; National Malaria Control Programme, The GambiaCompleted
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University of AarhusCompletedVitamin B12 DeficiencyDenmark
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J. Uriach and CompanyUnknownColorectal Neoplasm | Iron Deficiency AnemiaSpain
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University Hospital, AngersNovo Nordisk A/SUnknown
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Novalar Pharmaceuticals, Inc.CompletedSoft Tissue Anesthesia (Numbness)United States
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National Heart and Lung InstituteWexham Park Hospital; 4th Military HospitalUnknownHeart Diseases | Anemia, Iron-Deficiency | Chronic Heart FailurePoland, United Kingdom
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National Center for Research Resources (NCRR)James Whitcomb Riley Hospital for ChildrenCompletedThrombocytopenia | Dyskeratosis Congenita | Fanconi's Anemia | Shwachman Syndrome
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University of MinnesotaUnknown
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National Center for Research Resources (NCRR)University of California, Los AngelesCompletedThrombocytopenia | Inborn Errors of Metabolism | Metachromatic Leukodystrophy | Fanconi's Anemia | Thalassemia Major | Pure Red-Cell AplasiaUnited States
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National Center for Research Resources (NCRR)University of PittsburghTerminatedAlpha 1-Antitrypsin DeficiencyUnited States
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Fairview University Medical CenterUnknownMucopolysaccharidosis I | Niemann-Pick Disease | Mucopolysaccharidosis VI | Wolman Disease | Adrenoleukodystrophy | Metachromatic Leukodystrophy | Pulmonary Complications | Fucosidosis | Globoid Cell Leukodystrophy | Gaucher's Disease | Mannosidosis | I Cell DiseaseUnited States
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National Center for Research Resources (NCRR)University of California, Los AngelesCompleted
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Astra USACompletedHIV Infections | Hypocalcemia | Cytomegalovirus InfectionsUnited States
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National Center for Research Resources (NCRR)University of California, San DiegoCompletedFanconi Syndrome | Cystinosis
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Fairview University Medical CenterCompleted
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National Center for Research Resources (NCRR)University of PennsylvaniaCompletedOsteoporosis | Growth Hormone DeficiencyUnited States
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Dana-Farber Cancer InstituteUnknownFanconi's AnemiaUnited States
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National Center for Research Resources (NCRR)Eunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedPrecocious Puberty | HypogonadismUnited States
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National Center for Research Resources (NCRR)Northwestern UniversityCompletedGrowth Hormone Deficiency
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Eunice Kennedy Shriver National Institute of Child...Children's National Research InstituteTerminatedPhase I Pilot Study of Liver-Directed Gene Therapy for Partial Ornithine Transcarbamylase DeficiencyOrnithine Transcarbamylase Deficiency Disease
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Fairview University Medical CenterCompletedMyelodysplastic Syndromes | Leukemia, Lymphocytic, Acute | Fanconi's Anemia | Leukemia, Nonlymphocytic, AcuteUnited States
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Eunice Kennedy Shriver National Institute of Child...University of WashingtonUnknownWiskott-Aldrich Syndrome | Leukocyte Adhesion Deficiency Syndrome | X-Linked Agammaglobulinemia | X-Linked Hyper IgM SyndromeUnited States
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National Center for Research Resources (NCRR)National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); University...CompletedEnd Stage Renal Disease | Renal OsteodystrophyUnited States
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University of MinnesotaCompleted
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Eunice Kennedy Shriver National Institute of Child...Rockefeller UniversityCompletedHyperbilirubinemia | Glucosephosphate Dehydrogenase Deficiency | Hemolytic Disease of NewbornUnited States
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National Center for Research Resources (NCRR)University of North CarolinaCompletedHemophilia B | Factor IX Deficiency
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National Center for Research Resources (NCRR)UNC Lineberger Comprehensive Cancer CenterCompletedMetabolism, Inborn Errors | Methionine Adenosyltransferase Deficiency
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National Center for Research Resources (NCRR)Completed
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National Center for Research Resources (NCRR)National Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompleted
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National Institute of Environmental Health Sciences...Completed