Clinical Trials Sponsored by Congenital Muscle Disease International Registr

Total 4 results

  • Cure CMD
    Congenital Muscle Disease International Registr
    Withdrawn
    LAMA2-MD (Merosin Deficient Congenital Muscular Dystrophy, MDC1A)
    United States
  • Cure CMD
    University of Michigan; Congenital Muscle Disease International Registr
    Completed
    X-linked Myotubular Myopathy
    United States
  • Cure CMD
    University of Chicago; Boston Children's Hospital; Valerion Therapeutics, LLC; Congenital...
    Completed
    Myotubular Myopathy
    United States
  • Sanford Health
    National Ataxia Foundation; Beyond Batten Disease Foundation; Pitt Hopkins Research... and other collaborators
    Recruiting
    Mitochondrial Diseases | Retinitis Pigmentosa | Myasthenia Gravis | Eosinophilic Gastroenteritis | Multiple System Atrophy | Leiomyosarcoma | Leukodystrophy | Anal Fistula | Spinocerebellar Ataxia Type 3 | Friedreich Ataxia | Kennedy Disease | Lyme Disease | Hemophagocytic Lymphohistiocytosis | Spinocerebellar Ataxia... and other conditions
    United States, Australia
3
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