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Clinical Trials Sponsored by Novartis Gene Therapies
Total 34 results
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Novartis Gene TherapiesTerminatedSpinal Muscular AtrophyUnited States
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Novartis Gene TherapiesCompletedSpinal Muscular Atrophy 1United States
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Novartis Gene TherapiesCompletedGene Therapy | SMA - Spinal Muscular AtrophyUnited States
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Novartis Gene TherapiesCompletedSMAFrance, United Kingdom, Italy, Belgium
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Novartis Gene TherapiesActive, not recruitingSpinal Muscular Atrophy 1United States
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Novartis Gene TherapiesActive, not recruitingSMA | Spinal Muscular Atrophy Type II | Spinal Muscular Atrophy Type I | Spinal Muscular Atrophy Type IIIUnited States, Belgium, France, Japan, United Kingdom, Italy, Taiwan, Australia, Canada
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Novartis Gene TherapiesPRA Health SciencesCompletedSpinal Muscular Atrophy Type IKorea, Republic of, Taiwan, Japan
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Novartis Gene TherapiesPRA Health SciencesCompletedSpinal Muscular AtrophyUnited States, United Kingdom, Australia, Belgium, Canada, Japan
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Sio Gene TherapiesTerminatedParkinson DiseaseUnited Kingdom, France
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Taysha Gene Therapies, Inc.Withdrawn
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Taysha Gene Therapies, Inc.RecruitingRett SyndromeUnited States, United Kingdom
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Taysha Gene Therapies, Inc.RecruitingRett SyndromeUnited States, Canada
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Astellas Gene TherapiesRecruitingPompe Disease (Late-onset)United States, Spain, France, Taiwan, Italy
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Astellas Gene TherapiesCompletedX-linked Myotubular MyopathyUnited States, France, United Kingdom, Canada, Germany
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Astellas Gene TherapiesCompletedMales With X-linked Myotubular Myopathy (XLMTM)United States, United Kingdom
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Axovant Sciences Ltd.TerminatedDementia With Lewy BodiesUnited States, Canada, France, Italy, Netherlands, Spain, United Kingdom
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Axovant Sciences Ltd.CompletedAlzheimer's Disease | Dementia With Lewy Bodies | Parkinson's Disease DementiaUnited States
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Axovant Sciences Ltd.CompletedAlzheimer's DiseaseUnited States, Argentina, Australia, Bulgaria, Canada, Chile, Croatia, France, Germany, Italy, Korea, Republic of, Poland, Serbia, Singapore, Slovakia, Spain, Taiwan, United Kingdom, Czechia
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Axovant Sciences Ltd.CompletedLewy Body Dementia | Visual HallucinationsUnited States
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Astellas Gene TherapiesRecruitingPompe Disease (Late-onset)United States, United Kingdom
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Astellas Gene TherapiesActive, not recruitingX-Linked Myotubular MyopathyUnited States, Canada, France, Germany
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Axovant Sciences Ltd.CompletedREM Sleep Behavior Disorder | Dementia With Lewy Bodies | Parkinson's Disease DementiaUnited States
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Axovant Sciences Ltd.TerminatedAlzheimer's DiseaseUnited States, Argentina, Australia, Bulgaria, Canada, Chile, Croatia, Czechia, France, Germany, Italy, Korea, Republic of, Poland, Serbia, Singapore, Slovakia, Spain, Taiwan, United Kingdom
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Axovant Sciences Ltd.CompletedDementia With Lewy BodiesUnited States, Canada, France, Italy, Netherlands, Spain, United Kingdom
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Axovant Sciences Ltd.TerminatedREM Sleep Behavior Disorder | Dementia With Lewy Bodies | Lewy Body Dementia | Parkinson's Disease Dementia | Visual HallucinationsUnited States
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BioNTech Cell & Gene Therapies GmbHRecruitingSolid TumorAustralia, Germany, Netherlands, Sweden
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Axovant Sciences Ltd.Oxford BioMedicaTerminatedParkinson's DiseaseFrance, United Kingdom
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University of OxfordHoffmann-La Roche; Oxford University Hospitals NHS Trust; Novartis Gene TherapiesRecruiting
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Dr. Anupam SehgalTaysha Gene Therapies, Inc.; GlycoNetActive, not recruitingInfantile GM2 Gangliosidosis (Disorder)Canada
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Novartis PharmaceuticalsInnovative Therapies For Children with Cancer ConsortiumRecruitingNeuroblastomaGermany, Italy, Singapore, Spain, United States, Australia, France
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Taysha Gene Therapies, Inc.National Institute of Neurological Disorders and Stroke (NINDS)Active, not recruitingGene Transfer | Giant Axonal NeuropathyUnited States
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National Human Genome Research Institute (NHGRI)Sio Gene TherapiesRecruitingGangliosidosis | Lysosomal Diseases | GM1United States
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Swiss GO Trial GroupHoffmann-La Roche; Novartis Pharmaceuticals; AGO Study Group; Anticancer Fund,... and other collaboratorsRecruitingFallopian Tube Neoplasms | Peritoneal Neoplasms | Ovarian Neoplasm Epithelial | High-grade Serous Ovarian Carcinoma (HGSOC) | Low-grade Serous Ovarian Carcinoma (LGSOC) | Ovarian Endometrioid CarcinomaAustria, Switzerland, Germany
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Albert Einstein College of MedicineEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationMucopolysaccharidosis II | Fabry Disease | Niemann-Pick Disease, Type C | Mucopolysaccharidosis VI | Lysosomal Acid Lipase Deficiency | Metachromatic Leukodystrophy | Gaucher Disease | Cerebrotendinous Xanthomatosis | Mucopolysaccharidosis IV A | GM1 Gangliosidosis | Mucopolysaccharidosis VII | Acid Sphingomyelinase... and other conditionsUnited States