Clinical Trials Sponsored by PTC Therapeutics
Total 8137 results
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Vakzine Projekt Management GmbHUniversity of Stellenbosch; Children's Infectious Diseases Clinical Research... and other collaboratorsCompleted
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Starpharma Pty LtdNational Institute of Allergy and Infectious Diseases (NIAID); Eunice Kennedy... and other collaboratorsCompletedHealthyUnited States, Puerto Rico
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National Institute of Dental and Craniofacial Research...National Institute of Neurological Disorders and Stroke (NINDS); Sorrento Therapeutics...RecruitingPalliative Care | Intractable PainUnited States
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Minneamrita Therapeutics LLCCancer Research UK; Barts & The London NHS Trust; Queen Mary University of London and other collaboratorsCompletedPancreatic CancerUnited States
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Selcuk UniversityTC Erciyes University; Dokuz Eylul University; Ankara University; Selcuk University...Not yet recruitingSudden Cardiac Death | Arrythmia | ICDTurkey
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Albert Einstein College of MedicineEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationMucopolysaccharidosis II | Fabry Disease | Niemann-Pick Disease, Type C | Mucopolysaccharidosis VI | Lysosomal Acid Lipase Deficiency | Metachromatic Leukodystrophy | Gaucher Disease | Cerebrotendinous Xanthomatosis | Mucopolysaccharidosis IV A | GM1 Gangliosidosis | Mucopolysaccharidosis VII | Acid Sphingomyelinase... and other conditionsUnited States
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PIQUR Therapeutics AGHospital Universitari Vall d'Hebron Research Institute; Institut Català d'Oncologia and other collaboratorsCompletedMetastatic Breast CancerSpain, United Kingdom
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National Human Genome Research Institute (NHGRI)National Center for Advancing Translational Sciences (NCATS); Therapeutics...CompletedGNE Myopathy | Hereditary Inclusion Body Myopathy (HIBM)United States
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University of California, San FranciscoNational Institute of Allergy and Infectious Diseases (NIAID); University of... and other collaboratorsActive, not recruitingChlamydia | Gonorrhea | SyphilisUnited States
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SpeeDx Pty LtdGerman Federal Ministry of Education and Research; Wellcome Trust; Biomedical... and other collaboratorsNot yet recruiting
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University of ManchesterUniversity College, London; Manchester University NHS Foundation Trust; Orchard... and other collaboratorsActive, not recruitingMucopolysaccharidosis Type IIIAUnited Kingdom
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Enzyvant Therapeutics GmBHNational Institute of Allergy and Infectious Diseases (NIAID); Eunice Kennedy... and other collaboratorsTerminatedDiGeorge Anomaly
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Enzyvant Therapeutics GmBHNational Institute of Allergy and Infectious Diseases (NIAID); Eunice Kennedy... and other collaboratorsCompletedDiGeorge Syndrome | DiGeorge Anomaly | Complete DiGeorge Anomaly | Complete DiGeorge SyndromeUnited States
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University of California, Los AngelesNational Institute of Allergy and Infectious Diseases (NIAID); National Heart... and other collaboratorsCompleted
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Enzyvant Therapeutics GmBHNational Institute of Allergy and Infectious Diseases (NIAID); Eunice Kennedy... and other collaboratorsApproved for marketingDiGeorge Syndrome | DiGeorge Anomaly | Complete DiGeorge Anomaly | Complete DiGeorge SyndromeUnited States
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ScandiBio Therapeutics ABGöteborg University; Helsinki University Central Hospital; Sahlgrenska University... and other collaboratorsUnknownNon-alcoholic Fatty Liver Disease (NAFLD)Turkey
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Enzyvant Therapeutics GmBHNational Institute of Allergy and Infectious Diseases (NIAID); Eunice Kennedy... and other collaboratorsCompletedDiGeorge Syndrome | DiGeorge Anomaly | Complete DiGeorge Anomaly | Complete DiGeorge SyndromeUnited States
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Enzyvant Therapeutics GmBHNational Institute of Allergy and Infectious Diseases (NIAID); Eunice Kennedy... and other collaboratorsCompletedDiGeorge Anomaly | Complete DiGeorge Anomaly | Complete DiGeorge Syndrome | Complete Atypical DiGeorge Anomaly | Complete Atypical DiGeorge SyndromeUnited States
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Enzyvant Therapeutics GmBHNational Institute of Allergy and Infectious Diseases (NIAID); Eunice Kennedy... and other collaboratorsCompletedDiGeorge Syndrome | Complete Typical DiGeorge AnomalyUnited States
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University of Massachusetts, WorcesterNational Institute of Allergy and Infectious Diseases (NIAID); Aurum Institute and other collaboratorsRecruitingTuberculosis | Pulmonary Tuberculosis | HIV CoinfectionSouth Africa
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Omar JawdatRare Diseases Clinical Research Network; Terra Biological LLC; Clinical Research...Unknown
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Tuscaloosa Research & Education Advancement CorporationBaylor College of Medicine; James J. Peters Veterans Affairs Medical Center; Acorda... and other collaboratorsCompletedPosttraumatic Stress DisorderUnited States
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Johns Hopkins UniversityEli Lilly and Company; National Heart, Lung, and Blood Institute (NHLBI); The... and other collaboratorsCompletedSystemic Sclerosis | Pulmonary Arterial Hypertension | Pulmonary Hypertension | Connective Tissue Disease | Scleroderma Spectrum of DiseasesUnited States
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University of Yaounde 1Biotechnology Center (BTC), University of Yaounde I, Cameroon; National Malaria... and other collaboratorsNot yet recruiting
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University Hospital, AntwerpKarolinska Institutet; Erasmus Medical Center; University of California, San... and other collaboratorsCompletedTraumatic Brain InjuryGermany, Norway, United Kingdom, Belgium, Netherlands, Denmark, Finland, Sweden, France, Switzerland, Israel, Spain, Austria, Serbia, Latvia, Hungary, Italy, Lithuania, Romania
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Pharmacotherapies for Alcohol and Substance Use...Yale University; United States Department of Defense; VA Connecticut Healthcare... and other collaboratorsNot yet recruitingEffect of Sublingual Formulation of Dexmedetomidine Hydrochloride (HCl) (BXCL501) - Outpatient StudyPost Traumatic Stress Disorder (PTSD) | Alcohol Use Disorder (AUD)United States
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Pharmacotherapies for Alcohol and Substance Use...Yale University; United States Department of Defense; VA Connecticut Healthcare... and other collaboratorsCompletedPost Traumatic Stress Disorder (PTSD) | Alcohol Use Disorder (AUD)United States
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ERP Biomarker Qualification ConsortiumMerck Sharp & Dohme LLC; Novartis; Takeda; H. Lundbeck A/S; Astellas Pharma Inc; Alkermes... and other collaboratorsCompleted
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University of Yaounde 1Biotechnology Center (BTC), University of Yaounde I, Cameroon; National Malaria... and other collaboratorsNot yet recruiting
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Programme PAC-CI, Site ANRS-MIE de Côte d'IvoireUniversity of Toronto; Institut de Sante Publique, d'Epidemiologie et de Developpement and other collaboratorsCompletedHIV InfectionsCôte D'Ivoire
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Universitätsklinikum Hamburg-EppendorfLudwig-Maximilians - University of Munich; Philipps University Marburg Medical... and other collaboratorsCompleted
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Canadian Cancer Trials GroupCanadian Cancer Society (CCS); ATGen Canada Inc; Ontario Institute for Cancer... and other collaboratorsActive, not recruiting
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Rush University Medical CenterUniversity of Wisconsin, Milwaukee; Advocate Health Care; Children's Bureau -... and other collaboratorsRecruitingPregnancy Related | Parent-Child Relations | Parenting | Education | Antenatal Care | CounselingUnited States
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PATHBill and Melinda Gates Foundation; Centers for Disease Control and Prevention; PT Bio Farma and other collaboratorsRecruiting
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PATHBill and Melinda Gates Foundation; Centers for Disease Control and Prevention; PT Bio Farma and other collaboratorsRecruiting
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PT Bio FarmaNational Institute of Health Research and Development, Ministry of Health... and other collaboratorsCompleted
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GCP-Service International West GmbHSaint-Louis Hospital, Paris, France; University of Florence; Medical University... and other collaboratorsNot yet recruitingLow Risk Myelodysplastic SyndromesSpain, Poland, Italy, Germany, France
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Australian & New Zealand Children's Haematology...The Hospital for Sick Children; Kazia Therapeutics Limited; Day One Biopharmaceuticals... and other collaboratorsNot yet recruitingChildhood Cancer | Refractory Cancer | Recurrent Cancer | Childhood Solid Tumor | Childhood Brain TumorAustralia, Canada
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Kyoto UniversityOsaka University; Mie University; Tokushima University; Tokyo Metropolitan Geriatric... and other collaboratorsCompletedFamilial Alzheimer Disease (FAD) | PSEN1 MutationJapan
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PIQUR Therapeutics AGM.D. Anderson Cancer Center; Mayo Clinic; University College London Hospitals; Hospital... and other collaboratorsCompleted
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University of RochesterJohns Hopkins University; Massachusetts General Hospital; University of California... and other collaboratorsCompletedHuntington's DiseaseUnited States
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Shannaz Nadia YusharyahyaPT. Kimia Farma (Persero) Tbk; Ministry of Education, Culture, Research, and...CompletedSkin Aging | Transepidermal Water LossIndonesia
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Institut d'Anesthesiologie des Alpes MaritimesInstitut National de la Santé Et de la Recherche Médicale, France; PT Kalbe...TerminatedIntracranial Hypertension | Severe Trauma Brain InjuryFrance
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Society of Minimally Invasive Neurological Therapeutic...Egyptian Stroke Society; Egyptian Society of Neurological Surgeons; Egyptian... and other collaboratorsUnknownStroke, Acute | Stroke Hemorrhagic | Stroke, Cardiovascular | Stroke, Complication | Stroke Spinal CordEgypt
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Lawson Health Research InstituteOntario Ministry of Health and Long Term Care; Canadian Mental Health Association and other collaboratorsCompletedPsychotic Disorders | Diabetes Mellitus | SchizophreniaCanada
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Children's Hospital of PhiladelphiaEli Lilly and Company; University of Pennsylvania; Takeda; National Institute of... and other collaboratorsRecruitingMucopolysaccharidoses | Leukoencephalopathies | Leukodystrophy | Adrenoleukodystrophy | Adrenomyeloneuropathy | X-linked Adrenoleukodystrophy | Gangliosidoses | Metachromatic Leukodystrophy | Krabbe Disease | Refsum Disease | Cadasil | Sjogren-Larsson Syndrome | Allan-Herndon-Dudley Syndrome | White Matter Disease | GM2... and other conditionsUnited States
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University of NebraskaBnai Zion Medical Center; InCor Heart Institute; Microvascular Therapeutics, LLC and other collaboratorsWithdrawnMyocardial Infarction | Acute Coronary SyndromeUnited States
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ERP Biomarker Qualification ConsortiumMerck Sharp & Dohme LLC; Novartis; Takeda; H. Lundbeck A/S; Columbia University; Astellas... and other collaboratorsCompletedSchizophreniaUnited States
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Sante Diabete MaliFrench Development Agency; Société Francophone du Diabète; Centre hospitalo-universiaire...Completed
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LUNGevity FoundationBristol-Myers Squibb; Eli Lilly and Company; Merck Sharp & Dohme LLC; Novartis; T... and other collaboratorsRecruitingCaregivers | Lung Cancer PatientsUnited States