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Clinical Trials Sponsored by Rare Diseases Clinical Research Network
Total 901 results
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Office of Rare Diseases (ORD)Rare Diseases Clinical Research NetworkUnknownMyelodysplastic Syndromes | Purpura, Thrombocytopenic | Anemia, Aplastic | Red-Cell Aplasia, Pure | Bone Marrow Failure Syndromes | Hemoglobinuria, Paroxysmal | Leukemia, LymphocyticUnited States
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Office of Rare Diseases (ORD)Rare Diseases Clinical Research NetworkUnknown
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Office of Rare Diseases (ORD)Rare Diseases Clinical Research NetworkUnknownMyelodysplastic SyndromeUnited States
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University of California, Los AngelesRare Diseases Clinical Research Network; Office of Rare Diseases (ORD)CompletedCerebellar Diseases | Episodic Ataxia SyndromeUnited States, Canada, United Kingdom
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Baylor College of MedicineRare Diseases Clinical Research Network; Neogenis LaboratoriesCompletedUrea Cycle Disorders, Inborn | Urea Cycle Disorder | Argininosuccinic Aciduria | Argininosuccinate Lyase DeficiencyUnited States
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University of RochesterNational Center for Research Resources (NCRR); Rare Diseases Clinical Research... and other collaboratorsCompletedAndersen-Tawil Syndrome | Andersen SyndromeUnited States, Canada, Italy, United Kingdom
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National Institute of Arthritis and Musculoskeletal...The Cleveland Clinic; Rare Diseases Clinical Research Network; Office of Rare...CompletedGiant Cell Arteritis | Takayasu's ArteritisUnited States, Canada
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Richard Barohn, MDRare Diseases Clinical Research Network; Office of Rare Diseases (ORD)CompletedMyotonic Disorders | Myotonia Congenita | Nondystrophic MyotoniasCanada, United States, United Kingdom
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Myasthenia Gravis Rare Disease NetworkRecruitingMyasthenia Gravis | MuSK Myasthenia Gravis | MuSK MGUnited States
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Andrea GropmanNational Center for Research Resources (NCRR); Rare Diseases Clinical Research... and other collaboratorsCompletedBrain Diseases, Metabolic, Inborn | Ornithine Transcarbamylase Deficiency | Urea Cycle DisorderUnited States
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University of South FloridaNational Institutes of Health (NIH); Rare Diseases Clinical Research NetworkCompletedOsteogenesis Imperfecta | Brittle Bone DisordersUnited States
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University of South FloridaNational Institutes of Health (NIH); Rare Diseases Clinical Research NetworkCompletedOsteogenesis Imperfecta | Brittle Bone DisordersUnited States
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University of PennsylvaniaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedTemporal ArteritisUnited States, Canada
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University of PennsylvaniaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedPolyarteritis NodosaUnited States, Canada
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University of PennsylvaniaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsRecruitingGiant Cell Arteritis | Microscopic Polyangiitis | Polyarteritis Nodosa | Takayasu's Arteritis | Eosinophilic Granulomatosis With Polyangiitis (Churg-Strauss) | Granulomatosis With Polyangiitis (Wegener's)United States, Canada, Turkey
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University of PennsylvaniaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedWegener's GranulomatosisUnited States
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University of PennsylvaniaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedMicroscopic Polyangiitis | Granulomatosis With Polyangiitis | Wegener'sUnited States, Canada
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University of PennsylvaniaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedTakayasu's ArteritisUnited States, Canada
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Children's Hospital Medical Center, CincinnatiNational Center for Research Resources (NCRR); Rare Diseases Clinical Research...CompletedPulmonary Alveolar ProteinosisUnited States, Germany, Italy, Japan
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); Rare Diseases... and other collaboratorsTerminatedAndersen-Tawil SyndromeUnited States
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University of CincinnatiNational Heart, Lung, and Blood Institute (NHLBI); Rare Diseases Clinical Research...CompletedPulmonary Langerhans Cell HistiocytosisUnited States
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University of CincinnatiNational Heart, Lung, and Blood Institute (NHLBI); Rare Diseases Clinical Research...CompletedBirt-Hogg-Dube SyndromeUnited States
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Peter MerkelNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedTakayasu ArteritisUnited States, Canada
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Mayo ClinicNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompleted
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National Institute of Allergy and Infectious Diseases...Rare Diseases Clinical Research Network; Primary Immune Deficiency Treatment...CompletedWiskott-Aldrich SyndromeUnited States, Canada
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National Institute of Allergy and Infectious Diseases...Rare Diseases Clinical Research Network; Primary Immune Deficiency Treatment...Enrolling by invitationGranulomatous Disease, ChronicUnited States, Canada
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University of PittsburghNational Institute of Neurological Disorders and Stroke (NINDS); Rare Diseases...RecruitingPyruvate Dehydrogenase Complex Deficiency DiseaseUnited States
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Icahn School of Medicine at Mount SinaiNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Rare... and other collaboratorsCompletedErythropoietic Protoporphyria | EPP | XLP | X-Linked Protoporphyria | XLPP | X-Linked Dominant Erythropoietic Protoporphyria | XLEPP | XLDPUnited States
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Children's Hospital Medical Center, CincinnatiNational Heart, Lung, and Blood Institute (NHLBI); Rare Diseases Clinical Research...CompletedAutoimmune Pulmonary Alveolar ProteinosisUnited States
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Children's Hospital Medical Center, CincinnatiRare Diseases Clinical Research Network; National Center for Advancing Translational...CompletedAutoimmune Pulmonary Alveolar ProteinosisUnited States
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South East Asia Infectious Disease Clinical Research...Wellcome TrustCompleted
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University of FloridaEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedObesity | Prader-Willi SyndromeUnited States
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The Cleveland ClinicRecordati Rare DiseasesNot yet recruitingMild Autonomous Cortisol Secretion (MACS)United States
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Assistance Publique - Hôpitaux de ParisFrench rare diseases Healthcare Network; The French Foundation for Rare DiseasesActive, not recruitingAmelogenesis Imperfecta | Dentinogenesis Imperfecta | Dentin AnomaliesFrance
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University of Alabama at BirminghamPorphyria Rare Disease Clinical Research ConsortiumCompletedErythropoietic Protoporphyria (EPP)United States
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North Toronto Primary Care Research NetworkCompleted
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South East Asia Infectious Disease Clinical Research...University of OxfordCompleted
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Spanish Network for Research in Infectious DiseasesEuropean Society of Clinical Microbiology and Infectious DiseasesCompletedPathologic Processes | Sepsis | Systemic Inflammatory Response Syndrome | Inflammation | Bacterial Infections | Bacteremia | Infection | Organ Transplantation | Clinically Significant BacteremiaSpain
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NeuraLightEuropean Clinical Research Infrastructure NetworkRecruitingParkinson DiseaseUnited States, Switzerland, Portugal, United Kingdom, Spain
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Epidemiological and Clinical Research Information...CompletedGastrointestinal Neoplasms | Digestive System Neoplasms | Neoplasm Metastasis | Colorectal Neoplasms | Intestinal NeoplasmsJapan
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European Vision Institute Clinical Research NetworkCompletedNormal Subjects, AmetropiaSpain
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North Toronto Primary Care Research NetworkCompletedBlood PressureCanada
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Epidemiological and Clinical Research Information...Unknown
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Epidemiological and Clinical Research Information...Unknown
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European Vision Institute Clinical Research NetworkCompletedType 2 Diabetes | Non Proliferative Diabetic RetinopathyPortugal
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North Toronto Primary Care Research NetworkWithdrawn
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University of OxfordSouth East Asia Infectious Disease Clinical Research NetworkCompletedMetabolic DiseaseThailand
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National Institute of Allergy and Infectious Diseases...Mexican Emerging Infectious Diseases Clinical Research NetworkCompletedSevere Acute Respiratory IllnessMexico
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Chinese Chronic Respiratory Disease Research NetworkNot yet recruiting
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Chinese Chronic Respiratory Disease Research NetworkRecruiting