- ICH GCP
- US Clinical Trials Registry
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Search clinical trials for: Adenoassociated Virus (AAV)
Total 25249 results
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Terence FlotteMassachusetts General Hospital; University of Massachusetts, WorcesterActive, not recruitingTay-Sachs Disease | Sandhoff DiseaseUnited States
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MeiraGTx UK II LtdSyne Qua Non Limited; EMAS PharmaCompletedAchromatopsiaUnited Kingdom, United States
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MeiraGTx UK II LtdCompletedLeber Congenital AmaurosisUnited Kingdom, United States
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MeiraGTx UK II LtdSyne Qua Non Limited; EMAS PharmaCompleted
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MeiraGTx UK II LtdSyne Qua Non LimitedCompletedEye Diseases | Retinal Diseases | Eye Diseases, Hereditary | Leber Congenital Amaurosis (LCA)United States, United Kingdom
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Libella Gene TherapeuticsUnknown
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Libella Gene TherapeuticsUnknownEvaluation of Safety and Tolerability of Libella Gene Therapy for Critical Limb Ischemia: AAV- hTERTCritical Limb IschemiaColombia
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Libella Gene TherapeuticsUnknownAlzheimer DiseaseColombia
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VegaVect, Inc.National Eye Institute (NEI)Active, not recruiting
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MeiraGTx UK II LtdJanssen Research & Development, LLCCompleted
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Lantu BiopharmaNot yet recruitingSpinal Muscular Atrophy
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MeiraGTx, LLCActive, not recruitingParkinson DiseaseUnited States
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Neurologix, Inc.Weill Medical College of Cornell University; North Shore University HospitalCompletedParkinson's DiseaseUnited States
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University of PennsylvaniaUniversity of South Florida; University of OxfordCompletedVasculitis | Churg-Strauss Syndrome (CSS) | Microscopic Polyangiitis (MPA) | Eosinophilic Granulomatosis With Polyangiitis (Churg-Strauss) (EGPA) | Granulomatosis With Polyangiitis (Wegener's) (GPA) | Wegener Granulomatosis (WG) | ANCA-Associated Vasculitis (AAV)United States
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University of OxfordUniversity College, London; Moorfields Eye Hospital NHS Foundation TrustCompleted
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Neuracle Genetics, IncORA, Inc.RecruitingAge-Related Macular DegenerationCanada
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Mitsubishi Tanabe Pharma CorporationRecruitingAntineutrophil Cytoplasmic Antibody (ANCA) -Associated Vasculitis (AAV)Japan
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REGENXBIO Inc.National Heart, Lung, and Blood Institute (NHLBI)TerminatedHomozygous Familial Hypercholesterolemia (HoFH)United States, Canada, Italy, Netherlands
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PfizerRecruitingHemophilia A | Hemophilia BAustralia, United States, Turkey
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National Institute of Allergy and Infectious Diseases...Immune Tolerance Network (ITN)TerminatedANCA-Associated VasculitisUnited Kingdom
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MeiraGTx, LLCEnrolling by invitationParkinson DiseaseUnited States
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ArthrogenUnknown
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Tianjin Medical University Cancer Institute and...UnknownStage IV Gastric CancerChina
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Genzyme, a Sanofi CompanyCompleted
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ArthrogenCentre for Human Drug Research (CHDR)UnknownArthritis, Rheumatoid | Osteo ArthritisNetherlands
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Neurologix, Inc.TerminatedParkinson's DiseaseUnited States
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Orel Regional Hospital, RussiaUnknown
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Spark Therapeutics, Inc.Recruiting
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UniQure Biopharma B.V.Not yet recruitingAmyotrophic Lateral SclerosisUnited States
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Mayo ClinicGenentech, Inc.TerminatedMicroscopic Polyangiitis | Granulomatosis With Polyangiitis | ANCA Associated VasculitisUnited States
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Jichi Medical UniversityTakara Bio Inc.; Gene Therapy Research Institution,Co.,Ltd.Terminated
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Adrenas Therapeutics IncRecruitingCongenital Adrenal HyperplasiaUnited States
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Institute of Hematology & Blood Diseases HospitalNot yet recruiting
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UniQure Biopharma B.V.RecruitingHuntington's DiseaseUnited States
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CSL BehringActive, not recruitingHemophilia BUnited States, Belgium, Netherlands, Denmark, Germany, Ireland, Sweden, United Kingdom
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Vifor Fresenius Medical Care Renal PharmaRecruiting
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NGGT (Suzhou) Biotechnology Co., Ltd.Not yet recruitingPhenylketonurias
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Second Affiliated Hospital, School of Medicine,...Recruiting
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International AIDS Vaccine InitiativeNational Institute of Allergy and Infectious Diseases (NIAID); Children's Hospital...Unknown
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Zhongmou TherapeuticsRecruitingX-linked RetinoschisisChina
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NovelMed TherapeuticsNot yet recruitingAnti-Neutrophil Cytoplasmic Antibody-Associated Vasculitis
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International AIDS Vaccine InitiativeChildren's Hospital of Philadelphia; Nationwide Children's Hospital; Targeted...CompletedHIV InfectionBelgium, Germany, India
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University College, LondonRecruitingOrnithine Transcarbamylase DeficiencyUnited Kingdom
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Freeline TherapeuticsCompletedHemophilia B | Blood Coagulation Disorders, Inherited | Blood Coagulation Disorder | Haematologic DiseaseUnited States, United Kingdom, Australia, Netherlands, Austria, France, Ireland, Italy, Turkey, Canada, Germany, South Africa
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BioMarin PharmaceuticalActive, not recruiting
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Spark TherapeuticsCompleted
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Shanghai Vitalgen BioPharma Co., Ltd.Not yet recruitingGlutaric Acidemia Type I | Glutaric Aciduria Type IChina
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AmgenRecruitingAntineutrophil Cytoplasmic Antibody-associated VasculitisUnited States
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UniQure Biopharma B.V.RecruitingHuntington DiseasePoland, United Kingdom, Germany