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Search clinical trials for: Adenosine Deaminase Deficiency
Total 10090 results
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University of California, Los AngelesRecruitingAdenosine Deaminase Severe Combined Immune DeficiencyUnited States
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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Fondazione TelethonEnrolling by invitationImmunologic Deficiency SyndromesItaly
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Fondazione TelethonCompletedImmunologic Deficiency SyndromesItaly, Israel
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University of California, Los AngelesGreat Ormond Street Hospital for Children NHS Foundation TrustEnrolling by invitationAdenosine Deaminase Deficiency | Severe Combined Immunodeficiency (SCID)United States, United Kingdom
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Chiesi Farmaceutici S.p.A.CompletedSevere Combined Immunodeficiency | Adenosine Deaminase DeficiencyUnited States
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TRPHARMActive, not recruitingBronchiectasis | Pulmonary Disease | Adenosine Deaminase DeficiencyTurkey
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TRPHARMEnrolling by invitation
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TRPHARMEnrolling by invitationAdenosine Deaminase DeficiencyTurkey
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TRPHARMEnrolling by invitationPulmonary Alveolar ProteinosisTurkey
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Great Ormond Street Hospital for Children NHS Foundation...Orchard TherapeuticsCompletedAdenosine Deaminase Deficiency | Severe Combined Immunodeficiencies (SCID)United Kingdom
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National Heart, Lung, and Blood Institute (NHLBI)CompletedCystic Fibrosis | Psuedomas InfectionUnited States
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Donald B. Kohn, M.D.National Institutes of Health (NIH); FDA Office of Orphan Products DevelopmentCompletedSevere Combined ImmunodeficiencyUnited States
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Leadiant Biosciences, Inc.CompletedSevere Combined Immunodeficiency | ADA-SCID | Adenosine Deaminase DeficiencyUnited States
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National Human Genome Research Institute (NHGRI)CompletedSevere Combined Immunodeficiency SyndromeUnited States
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Shenzhen Geno-Immune Medical InstituteUnknownAdenosine DeAminase Severe Combined ImmunoDeficiency (ADA-SCID)China
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute...CompletedSevere Combined Immunodeficiency | Adenosine Deaminase Deficiency | Immune System Disorder | Autosomal Recessive Disorder | Purine-Nucleoside Phosphorylase Deficiency | Severe Combined Immunodeficiency With Absence of T and B Cells | X-Linked Severe Combined ImmunodeficiencyUnited States
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National Human Genome Research Institute (NHGRI)National Institutes of Health Clinical Center (CC); National Cancer Institute... and other collaboratorsCompletedADA-SCID | Adenosine Deaminase DeficiencyUnited States
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Great Ormond Street Hospital for Children NHS Foundation...Completed
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National Human Genome Research Institute (NHGRI)CompletedSevere Combined ImmunodeficiencyUnited States
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IRCCS San RaffaeleFondazione TelethonCompletedSevere Combined Immunodeficiency Syndrome
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National Human Genome Research Institute (NHGRI)RecruitingMetabolic Disease | Purine-Pyrimidine Metabolism | AICDA, OMIM *605257, Immunodeficiency With Hyper-IgM, Type 2; HIGM2 | UNG, OMIM *191525, Hyper-IgM Syndrome 5 | NT5C3A<TAB>, OMIM *606224, Anemia, Hemolytic, Due to UMPH1 Deficiency | UMPS, OMIM *613891, Orotic Aciduria | DHODH, OMIM *126064,... and other conditionsUnited States
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Sohag UniversityNot yet recruitingChronic Spontaneous Urticaria
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City of Hope Medical CenterNational Cancer Institute (NCI)RecruitingRecurrent Severe Aplastic Anemia | Refractory Severe Aplastic AnemiaUnited States
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Assiut UniversityNot yet recruiting
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National Heart, Lung, and Blood Institute (NHLBI)National Institutes of Health Clinical Center (CC); National Cancer Institute...RecruitingStem Cell Transplantation | Sickle Cell Disease | Thalassemia | Graft vs Host DiseaseUnited States
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National Cancer Institute (NCI)Active, not recruitingHairy Cell LeukemiaUnited States
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Tesaro, Inc.Gynecologic Oncology Group; European Network of Gynaecological Oncological... and other collaboratorsActive, not recruitingOvarian NeoplasmsUnited States, Spain, Finland, Czechia, Italy, Denmark, Germany, Belgium, Israel, Canada, Russian Federation, Sweden, United Kingdom, Poland, Ireland, Ukraine, France, Norway, Switzerland, Hungary
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City of Hope Medical CenterCalifornia Institute for Regenerative Medicine (CIRM)Active, not recruitingSickle Cell Disease | Anemia, Sickle Cell | Hemoglobinopathies | Thalassemia | Sickle Cell DisorderUnited States
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Eda Cetin OzdemirCompletedPeriodontal DiseasesTurkey
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National Heart, Lung, and Blood Institute (NHLBI)Active, not recruitingSickle Cell DiseaseUnited States
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University of NebraskaAstex Pharmaceuticals, Inc.CompletedMyelodysplastic Syndromes | Multiple Myeloma | Chronic Lymphocytic Leukemia | Peripheral T-cell Lymphoma | Acute Lymphocytic Leukemia | Acute Myelogenous Leukemia | Chronic Myelogenous Leukemia | Non-Hodgkins Lymphoma | Hodgkins DiseaseUnited States
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University of California, San FranciscoNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Tufts... and other collaboratorsCompletedVitamin B1 Deficiency | Thiamine DeficiencyUnited States
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University of NebraskaNational Cancer Institute (NCI)WithdrawnLymphoma | Myelodysplastic Syndromes | Leukemia | Chronic Myeloproliferative Disorders | Nonmalignant NeoplasmUnited States
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Incyte CorporationCompletedGraft-versus-host Disease (GVHD)Belgium, Italy, Spain, Saudi Arabia, Turkey, United Kingdom, Germany, Greece, Canada, Austria, France, Israel, Netherlands, Sweden, Switzerland, Korea, Republic of, Bulgaria, Japan, Norway, Czechia, Russian Federation, Jordan, Hungary, Ind... and more
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Eastern Cooperative Oncology GroupNational Cancer Institute (NCI)Completed
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Eastern Cooperative Oncology GroupNational Cancer Institute (NCI)Terminated
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Eastern Cooperative Oncology GroupNational Cancer Institute (NCI)CompletedMyelodysplastic Syndromes | Leukemia | Myelodysplastic/Myeloproliferative NeoplasmsUnited States
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University of PennsylvaniaSuspendedLipid Metabolism, Inborn Errors | Cholesterol, HDL | Tangier Disease | LCAT Deficiency | Cholesteryl Ester Transfer Protein (CETP) DeficiencyUnited States
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M.D. Anderson Cancer CenterAstex Pharmaceuticals, Inc.; PharmatechCompleted
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Alliance for Clinical Trials in OncologyNational Cancer Institute (NCI)CompletedGraft Versus Host DiseaseUnited States
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National Heart, Lung, and Blood Institute (NHLBI)National Cancer Institute (NCI); Blood and Marrow Transplant Clinical Trials...CompletedGraft vs Host Disease | Immune System DisordersUnited States
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Astex Pharmaceuticals, Inc.TerminatedAcute Graft Versus Host DiseaseUnited States
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)CompletedAcute Myeloid Leukemia | Hodgkin Lymphoma | Waldenstrom Macroglobulinemia | Acute Lymphoblastic Leukemia | Chronic Lymphocytic Leukemia | Non-Hodgkin Lymphoma | Plasma Cell Myeloma | Myelodysplastic/Myeloproliferative Neoplasm | Graft Versus Host Disease | Chronic Myelogenous Leukemia, BCR-ABL1 PositiveUnited States, Italy
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Mayo ClinicNational Cancer Institute (NCI)Completed
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National Cancer Institute (NCI)CompletedPancreatic Neoplasms | Mesothelioma | Adenocarcinoma of LungUnited States
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Weill Medical College of Cornell UniversityRobert Wood Johnson FoundationCompletedObstructive Sleep Apnea
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M.D. Anderson Cancer CenterCompletedChronic Lymphocytic Leukemia | Cutaneous T-cell Lymphoma | Peripheral T-cell LymphomaUnited States
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Mayo ClinicNational Cancer Institute (NCI)CompletedChronic Lymphocytic Leukemia | Stage III Small Lymphocytic Lymphoma | Stage IV Small Lymphocytic Lymphoma | Stage 0 Chronic Lymphocytic Leukemia | Stage I Chronic Lymphocytic Leukemia | Stage II Chronic Lymphocytic Leukemia | Stage I Small Lymphocytic Lymphoma | Stage III Chronic Lymphocytic Leukemia and other conditionsUnited States