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Search clinical trials for: Alpha galactosidase deficiency
Total 18176 results
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Genzyme, a Sanofi CompanyRecruitingFabry DiseaseCroatia, United States, Argentina, Australia, Belgium, Bulgaria, Canada, Germany, Hong Kong, India, Indonesia, Korea, Republic of, Kuwait, Malaysia, Philippines, Poland, Romania, Singapore, Slovakia, Taiwan, Thailand, United Kingdom, Vietn... and more
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Genzyme, a Sanofi CompanyTerminatedFabry Disease | Alpha Galactosidase A DeficiencyUnited States, Austria, United Kingdom
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Greenwood Genetic CenterCompletedGalactosialidosis | Sialidosis | Fucosidosis | Aspartylglucosaminuria | Alpha Mannosidosis | Beta Mannosidosis | Mucolipidosis II | Mucolipidosis III | Schindler DiseaseUnited States
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ProtalixChiesi Farmaceutici S.p.A.CompletedFabry DiseaseUnited States, Serbia, Spain, United Kingdom, Australia, Paraguay
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Cedars-Sinai Medical CenterNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsUnknown
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University of MilanKolfarma s.r.l. - Italy; Fondazione TelethonRecruiting
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Wave Life Sciences Ltd.Not yet recruiting
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Beam Therapeutics Inc.Not yet recruitingAlpha 1-Antitrypsin DeficiencyUnited Kingdom
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Chiesi Farmaceutici S.p.A.ICON plcNot yet recruiting
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Hospital Universitari Vall d'Hebron Research InstituteErasme University Hospital; Cyprus Institute of Neurology and Genetics; EuroBloodNet...RecruitingIron Metabolism Disorders | Sickle Cell Disease | Thalassemia | Hemolytic; Anemia, Hereditary, Due to Enzyme Disorder | Anemia Due to Membrane Defect | CDA | Sideroblastic Anemia | Constitutional Aplastic Anemia | Hereditary AnemiaSpain
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Wave Life Sciences Ltd.RecruitingAlpha-1 Antitrypsin DeficiencyUnited Kingdom
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Chiesi Farmaceutici S.p.A.Not yet recruiting
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TakedaRecruitingAlpha1-Antitrypsin DeficiencyItaly, United States, Poland, Portugal
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Krystal Biotech, Inc.RecruitingAlpha 1-Antitrypsin DeficiencyUnited States
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Permian Health Lung InstituteThe Gambia Committee on Traditional Practices Affecting the Health of Women...Not yet recruitingCOPD | Lung Function Decreased | Alpha 1-AntitrypsinGambia
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Valneva Austria GmbHRecruitingChikungunya Virus InfectionPanama
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Inhibrx, Inc.Not yet recruitingEmphysema | Alpha 1-Antitrypsin Deficiency
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Inhibrx Biosciences, IncRecruitingEmphysema | Alpha 1-Antitrypsin DeficiencyUnited States, Australia, United Kingdom, New Zealand
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Bio Sidus SARecruiting
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Chiesi Farmaceutici S.p.A.ICON plcRecruiting
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Centre Hospitalier Universitaire de LiegeSanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier Régional... and other collaboratorsRecruitingCongenital Adrenal Hyperplasia | Hemophilia A | Hemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystic Fibrosis | Alpha 1-Antitrypsin Deficiency | Sickle Cell Disease | Fanconi Anemia | Chronic Granulomatous Disease | Wilson Disease | Severe Congenital Neutropenia | Ornithine Transcarbamylase... and other conditionsBelgium
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TakedaTakeda Development Center Americas, Inc.RecruitingAlpha1-Antitrypsin DeficiencyUnited States, Belgium, Switzerland, Canada, Australia, Germany, United Kingdom, Austria, France, Spain, Portugal, Italy, Poland, Brazil
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Assiut UniversityNot yet recruitingPre-Eclampsia | Intrauterine Growth Restriction | alpha1 Anti-trypsin
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University of ThessalyNot yet recruitingOxidative Stress | Carbohydrate Metabolism Disorder | G6PD Deficiency
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University of California, Los AngelesRecruitingAdenosine Deaminase Severe Combined Immune DeficiencyUnited States
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National Cancer Institute (NCI)RecruitingLynch SyndromeUnited States, Puerto Rico
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Universidade do PortoHospital da Luz, Lisboa; Hospital Pedro Hispano; Centro Hospitalar de Leiria; Centro... and other collaboratorsRecruitingFabry DiseasePortugal
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University of California, IrvineHudson Valley Healing Arts CenterNot yet recruiting
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University of CopenhagenHvidovre University HospitalRecruitingChronic Liver DiseaseDenmark
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Great Ormond Street Hospital for Children NHS Foundation...National Institute for Health Research, United Kingdom; The Freya FoundationRecruitingPyruvate Dehydrogenase Complex Deficiency | Pyruvate Dehydrogenase E1 Alpha Deficiency | Pyruvate Dehydrogenase E1-Beta Deficiency | Pyruvate Dehydrogenase E2 Deficiency | Pyruvate Dehydrogenase Phosphatase DeficiencyUnited Kingdom
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Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy...RecruitingHaploidentical Hematopoietic Cell Transplantation Using TCR Alpha/Beta and CD19 Depletion (HAPLOTAB)Myelodysplastic Syndromes | Primary Immunodeficiency Diseases | Hemoglobinopathies | Chronic Myeloid Leukemia | Cytopenia | Severe Aplastic Anemia | Bone Marrow Failure Syndrome | Acute Myeloid Leukemia in Remission | Hemophagocytic Lymphohistiocytoses | Acute Lymphoblastic Leukemia in Remission | Severe...United States
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University Hospital, MontpellierRecruitingAromatic L-Amino Acid Decarboxylase DeficiencyFrance
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Thomayer University HospitalMasaryk UniversityRecruiting
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University of NottinghamNottingham University Hospitals NHS TrustRecruitingChronic Obstructive Pulmonary Disease | Alpha 1-Antitrypsin DeficiencyUnited Kingdom
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Grifols Therapeutics LLCRecruiting
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SphinCS Lyso Gemeinnutzige UG (Haftungsbeschrankt)RecruitingGangliosidoses | Galactosialidosis | Sialidosis | GM1 Gangliosidosis | Tay-Sachs Disease | Sandhoff Disease | Morquio B Disease | Gm2-Gangliosidosis, Variant B1 | GM2 Activator DeficiencyGermany
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Paul SzabolcsRecruitingCongenital Bone Marrow Failure Syndromes | Inflammatory Conditions | Primary Immunodeficiency (PID) | Inherited Metabolic Disorders (IMD) | Hereditary AnemiasUnited States
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Johns Hopkins All Children's HospitalRecruitingMetabolic Disease | Primary Immune Deficiency DisordersUnited States
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National Cancer Institute (NCI)RecruitingAcute Adult T-Cell Leukemia/Lymphoma | Adult T-Cell Leukemia/Lymphoma | Chronic Adult T-Cell Leukemia/Lymphoma | HTLV-1 InfectionUnited States
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Kamada, Ltd.Syneos HealthRecruitingAlpha 1-Antitrypsin DeficiencyUnited Kingdom, Sweden, Ireland, Netherlands, Belgium, Finland
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Hospital Universitari Vall d'Hebron Research InstituteEuropean Respiratory SocietyRecruitingAlpha 1-Antitrypsin DeficiencySpain
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Alpha-1 FoundationRecruiting
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National Institute of Allergy and Infectious Diseases...Not yet recruitingHyper-Immunoglobulin E. Syndrome (HEIS) | Chronic Granulomatous Disease (CGD)United States
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CSL BehringRecruitingAcute-graft-versus-host DiseaseUnited States, Korea, Republic of, Spain, Australia, Germany, Italy, Turkey, Japan
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Masonic Cancer Center, University of MinnesotaRecruitingMyelodysplastic Syndromes | Fanconi Anemia | Dyskeratosis Congenita | Severe Aplastic Anemia | Bone Marrow Failure | T Cell Receptor Alpha/Beta Depletion | Telomere Biology DisorderUnited States
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McMaster UniversitySt. Joseph's Healthcare HamiltonRecruitingBronchiectasis | Chronic Obstructive Pulmonary Disease | Asthma | Emphysema | Pulmonary Fibrosis | Alpha 1-Antitrypsin Deficiency | Bronchopulmonary Dysplasia | Sarcoidosis, PulmonaryCanada
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University of PittsburghRecruitingLysosomal Storage Diseases | Leukodystrophy | Niemann-Pick Diseases | Batten Disease | Gaucher Disease | Krabbe Disease | Alpha-Mannosidosis | Osteopetrosis | Tay-Sachs Disease | Pelizaeus-Merzbacher Disease | Sandhoff Disease | GM1 Gangliosidoses | MPS I | MPS II | Vanishing White Matter Disease | Multiple Sulfatase Deficiency... and other conditionsUnited States
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Children's Hospital of PhiladelphiaUniversity of California, San FranciscoRecruitingImmunodeficiencies | Immune Dysregulation SyndromesUnited States
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Schön Klinik Berchtesgadener LandCSL BehringRecruitingChronic Obstructive Pulmonary DiseaseGermany