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Search clinical trials for: Antisense OligoNucleotide strategy
Total 2029 results
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University Hospital, MontpellierHôpital Cochin; Hôpital Necker-Enfants Malades; Foch Hospital, Suresnes, FRANCERecruitingCystic Fibrosis | CFTR Gene MutationFrance
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Algemeen Ziekenhuis Maria MiddelaresNot yet recruiting
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Massachusetts General Hospitaln-Lorem FoundationNot yet recruiting
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CAMP4 Therapeutics CorporationRecruiting
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QurAlis CorporationRecruitingAmyotrophic Lateral SclerosisCanada, Germany, Netherlands, Ireland, United Kingdom, Belgium
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GlaxoSmithKlineRecruitingChronic Hepatitis BItaly, Japan, Spain, Korea, Republic of, Argentina, Canada, France, Poland
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GlaxoSmithKlineRecruitingChronic Hepatitis B | Hepatitis B, ChronicUnited States, Australia, France, Germany, Italy, Spain, Taiwan, Mexico, United Kingdom, Greece, Korea, Republic of, China, Argentina, Brazil, Bulgaria, Japan, Poland, Hungary, Philippines, Singapore, India, Turkey, Thailand, Canada, Ro... and more
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First Affiliated Hospital of Fujian Medical UniversityPeking Union Medical College Hospital; Fujian Medical University Union HospitalRecruiting
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ProQR TherapeuticsRecruitingEye Diseases | Neurologic Manifestations | Retinal Degeneration | Retinal Dystrophies | Sensation Disorders | Vision Disorders | Blindness | Leber Congenital Amaurosis | Leber Congenital Amaurosis 10 | Retinal Disease | Eye Disorders CongenitalBelgium, Brazil, Canada, Germany, Italy, Netherlands, United Kingdom
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Brigham and Women's HospitalNot yet recruitingTransthyretin Amyloid CardiopathyUnited States
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Bio-Path Holdings, Inc.RecruitingFallopian Tube Neoplasms | Carcinoma, Ovarian Epithelial | Solid Tumor | Endometrial Cancer | Peritoneal Cancer | Solid Tumor, AdultUnited States
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Bio-Path Holdings, Inc.RecruitingFollicular Lymphoma | Hodgkin Lymphoma | Waldenstrom Macroglobulinemia | Mantle Cell Lymphoma | Marginal Zone Lymphoma | Chronic Lymphocytic Leukemia (CLL) | Small Lymphocytic Lymphoma (SLL) | DLBCL | Cutaneous T-cell Lymphoma (CTCL) | Peripheral T-cell Lymphoma (PTCL)United States
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Assistance Publique - Hôpitaux de ParisRecruiting
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Novartis PharmaceuticalsActive, not recruitingProgressive Supranuclear Palsy (PSP)Germany, United Kingdom, Canada, United States
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AstraZenecaCompleted
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n-Lorem FoundationMayo ClinicActive, not recruitingAmyotrophic Lateral SclerosisUnited States
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University of California, San DiegoCalifornia Institute for Regenerative Medicine (CIRM); n-Lorem FoundationActive, not recruitingGenetic DiseaseUnited States
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Daiichi Sankyo Co., Ltd.Orphan Disease Treatment Institute Co., Ltd.Completed
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Hoffmann-La RocheCompletedHuntingtons DiseaseUnited States, United Kingdom, Australia, Canada, Japan, Poland, Netherlands, Germany, Russian Federation, France, Spain, Argentina, New Zealand, Austria, Denmark, Italy, Switzerland, Chile
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AutotelicbioCompletedSolid TumorKorea, Republic of
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Praxis Precision MedicinesActive, not recruitingEpilepsy | SCN2A-DEEUnited States
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Daiichi Sankyo Co., Ltd.Active, not recruitingDuchenne Muscular DystrophyJapan
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Institut National de la Santé Et de la Recherche...Biogen; Ionis Pharmaceuticals, Inc.CompletedSpinocerebellar Ataxia Type 2 | Spinocerebellar Ataxia Type 7France
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ProQR TherapeuticsTerminatedEye Diseases | Retinitis Pigmentosa | Eye Diseases, Hereditary | Vision Disorders | Retinal Disease | Eye Disorders Congenital | Usher Syndrome Type 2 | Deaf BlindUnited States, United Kingdom
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ProQR TherapeuticsTerminatedEye Diseases | Neurologic Manifestations | Eye Diseases, Hereditary | Sensation Disorders | Vision Disorders | Blindness | Leber Congenital Amaurosis | Leber Congenital Amaurosis 10 | Retinal Disease | Eye Disorders CongenitalUnited States, Belgium
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ProQR TherapeuticsTerminatedRetinitis Pigmentosa | Usher Syndrome Type 2United States, Canada, France
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ProQR TherapeuticsCompletedLeber's Congenital AmaurosisUnited States, Belgium
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ProQR TherapeuticsActive, not recruitingEye Diseases | Retinitis Pigmentosa | Eye Diseases, Hereditary | Vision Disorders | Retinal Disease | Eye Disorders Congenital | Usher Syndrome Type 2 | Deaf BlindUnited States, Netherlands, United Kingdom, Germany
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TAK-Circulator Co.CompletedHealthy VolunteerJapan
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ProQR TherapeuticsActive, not recruitingEye Diseases | Retinitis | Eye Diseases, Hereditary | Retinal Dystrophies | Vision Disorders | Retinal Disease | Autosomal Dominant Retinitis Pigmentosa | Vision TunnelUnited States
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ProQR TherapeuticsCompletedEye Diseases | Retinitis Pigmentosa | Eye Diseases, Hereditary | Vision Disorders | Retinal Disease | Eye Disorders Congenital | Usher Syndrome Type 2 | Deaf BlindUnited States, Canada, France
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ProQR TherapeuticsActive, not recruitingEye Diseases | Neurologic Manifestations | Eye Diseases, Hereditary | Sensation Disorders | Vision Disorders | Blindness | Leber Congenital Amaurosis | Leber Congenital Amaurosis 10 | Retinal Disease | Eye Disorders CongenitalUnited States, Belgium, Brazil, Canada, France, Germany, Italy, Netherlands, United Kingdom
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Phoenicis TherapeuticsTerminatedEpidermolysis Bullosa Dystrophica, Recessive | Epidermolysis Bullosa Dystrophica, DominantUnited States, Spain, France
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Brigham and Women's HospitalUnknown
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ProQR TherapeuticsEuropean CommissionCompletedCystic FibrosisUnited States, France, Belgium
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Bio-Path Holdings, Inc.WithdrawnAcute Myeloid Leukemia | Myelodysplastic Syndrome | Chronic Myelogenous Leukemia, Ph1-PositiveUnited States
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Bio-Path Holdings, Inc.CompletedRecurrent Adult Acute Myeloid Leukemia | Acute Lymphoblastic Leukemia | Myelodysplastic Syndrome | Ph1 Positive CMLUnited States
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Imperial College LondonSarepta Therapeutics, Inc.; Department of Health, United KingdomCompletedDuchenne Muscular DystrophyUnited Kingdom
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ProQR TherapeuticsEuropean CommissionCompletedCystic FibrosisUnited States, Spain, United Kingdom, Germany, Italy, Belgium, Canada, Czechia, Denmark, France
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National Cancer Institute (NCI)CompletedNeoplasms | Liver MetastasesUnited States
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Sterna Biologicals GmbH & Co. KGCompleted
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Isarna Therapeutics GmbHCompletedPrimary Open Angle GlaucomaGermany
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National Cancer Institute (NCI)TerminatedGastrointestinal Neoplasms | Ovarian Neoplasms | Ovarian Cancer | Ascites | Gastrointestinal CancerUnited States
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AstraZenecaIonis Pharmaceuticals, Inc.CompletedAdvanced Adult Hepatocellular Carcinoma | Hepatocellular Carcinoma MetastaticKorea, Republic of, Taiwan, Hong Kong, Japan
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Sterna Biologicals GmbH & Co. KGCompletedMild to Moderate Atopic DermatitisGermany
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Brigham and Women's HospitalGlaxoSmithKline; Ionis Pharmaceuticals, Inc.Withdrawn
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Sterna Biologicals GmbH & Co. KGCompleted
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Abramson Cancer Center of the University of PennsylvaniaNational Cancer Institute (NCI)Completed
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Eleos, Inc.Withdrawn
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University of Southern CaliforniaSponsor Name PendingWithdrawn