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Search clinical trials for: Autologous Lentiviral vector
Total 6701 results
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Lantu BiopharmaNot yet recruitingBeta-Thalassemia
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Orchard TherapeuticsRecruitingMPS-IH (Hurler Syndrome)Netherlands, United States, Italy, United Kingdom
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University of California, Los AngelesRecruitingAdenosine Deaminase Severe Combined Immune DeficiencyUnited States
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David WilliamsNational Heart, Lung, and Blood Institute (NHLBI); bluebird bio; California Institute... and other collaboratorsRecruitingA Gene Transfer Study Inducing Fetal Hemoglobin in Sickle Cell Disease (GRASP, BMT CTN 2001) (GRASP)Sickle Cell DiseaseUnited States
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Great Ormond Street Hospital for Children NHS Foundation...Recruiting
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Assistance Publique - Hôpitaux de ParisRecruitingArtemis (DCLRE1C ) Deficient Severe Combined ImmunodeficiencyFrance
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bluebird bioRecruitingSickle Cell DiseaseUnited States
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University of PennsylvaniaChildren's Hospital of PhiladelphiaRecruiting
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National Institute of Allergy and Infectious Diseases...RecruitingX-linked Severe Combined Immunodeficiency (XSCID)United States
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National Institute of Allergy and Infectious Diseases...Enrolling by invitationChronic Granulomatous Disease | p47 | Autosomal RecessiveUnited States
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David WilliamsActive, not recruitingGene Therapy | Severe Combined Immunodeficiency, X LinkedUnited States, United Kingdom
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University of ManchesterUniversity College, London; Manchester University NHS Foundation Trust; Orchard... and other collaboratorsActive, not recruitingMucopolysaccharidosis Type IIIAUnited Kingdom
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bluebird bioCompletedSickle Cell DiseaseUnited States
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City of Hope Medical CenterNational Cancer Institute (NCI); Mustang Bio, Inc.Active, not recruitingAcute Myeloid Leukemia | Recurrent Adult Acute Myeloid Leukemia | Secondary Acute Myeloid Leukemia | Untreated Adult Acute Myeloid Leukemia | Adult Acute Myeloid Leukemia in Remission | Refractory Acute Myeloid Leukemia | Blastic Plasmacytoid Dendritic Cell Neoplasm | Minimal Residual Disease | Acute... and other conditionsUnited States
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Assistance Publique - Hôpitaux de ParisActive, not recruiting
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City of Hope Medical CenterNational Cancer Institute (NCI)Active, not recruitingExtranodal Marginal Zone B-cell Lymphoma of Mucosa-associated Lymphoid Tissue | Nodal Marginal Zone B-cell Lymphoma | Recurrent Adult Burkitt Lymphoma | Recurrent Adult Diffuse Large Cell Lymphoma | Recurrent Adult Diffuse Mixed Cell Lymphoma | Recurrent Adult Diffuse Small Cleaved Cell Lymphoma and other conditionsUnited States
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M.D. Anderson Cancer CenterCompletedRecurrent Synovial Sarcoma | HLA-A*0201 Positive Cells Present | NY-ESO-1 Positive Tumor Cells Present | Recurrent Myxoid LiposarcomaUnited States
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David WilliamsActive, not recruiting
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Memorial Sloan Kettering Cancer CenterActive, not recruitingConfirmed Diagnosis of ß-thalassemia MajorUnited States
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Great Ormond Street Hospital for Children NHS Foundation...Orchard TherapeuticsCompletedSevere Combined Immunodeficiency Due to ADA DeficiencyUnited Kingdom
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American Gene Technologies International Inc.Enrolling by invitation
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University of California, Los AngelesOrchard Therapeutics; California Institute for Regenerative Medicine (CIRM)CompletedSevere Combined Immunodeficiency Due to ADA DeficiencyUnited States
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University of California, Los AngelesNational Institute of Allergy and Infectious Diseases (NIAID); National Heart... and other collaboratorsCompleted
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Great Ormond Street Hospital for Children NHS Foundation...Orchard TherapeuticsCompletedAdenosine Deaminase Deficiency | Severe Combined Immunodeficiencies (SCID)United Kingdom
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IRCCS San RaffaeleFondazione TelethonActive, not recruiting
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CSL BehringTerminated
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GenethonInstitute of Child Health; Great Ormond Street Hospital for Children NHS Foundation...Completed
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GenethonActive, not recruitingWiskott-Aldrich SyndromeUnited Kingdom, France
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Shenzhen Geno-Immune Medical InstituteUnknownAdenosine DeAminase Severe Combined ImmunoDeficiency (ADA-SCID)China
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Shenzhen Geno-Immune Medical InstituteUnknownSCID, X LinkedChina
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Shenzhen Geno-Immune Medical InstituteUnknown
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Shenzhen Geno-Immune Medical InstituteUnknown
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IRCCS San RaffaeleOrchard Therapeutics; Fondazione TelethonUnknown
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute...WithdrawnStage III Adult Hodgkin Lymphoma | Stage IV Adult Hodgkin Lymphoma | Human Immunodeficiency Virus 1 Positive | Stage I Adult Hodgkin Lymphoma | Stage II Adult Hodgkin Lymphoma | Stage I Adult Non-Hodgkin Lymphoma | Stage II Adult Non-Hodgkin Lymphoma | Stage III Adult Non-Hodgkin Lymphoma | Stage IV...United States
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GenethonHôpital Necker-Enfants MaladesCompleted
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Shenzhen Geno-Immune Medical InstituteUnknown
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National Human Genome Research Institute (NHGRI)National Institutes of Health Clinical Center (CC); National Cancer Institute... and other collaboratorsCompletedADA-SCID | Adenosine Deaminase DeficiencyUnited States
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Nanfang Hospital of Southern Medical UniversityGuangdong Yike Gene Science and Technology CO.,LtdUnknownBeta Thalassemia MajorChina
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Essen BiotechNot yet recruitingSickle Cell Disease | Sickle-Cell Disease With CrisisChina
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Theravectys S.A.Not yet recruitingHPV-Related Cervical Carcinoma | HPV Positive Oropharyngeal Squamous Cell CarcinomaUnited States
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Kanglin Biotechnology (Hangzhou) Co., Ltd.Not yet recruitingTransfusion-dependent Beta-ThalassemiaChina
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Institute of Hematology & Blood Diseases Hospital...Kanglin BiotechRecruitingTransfusion-dependent Beta-ThalassemiaChina
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Fred Hutchinson Cancer CenterBristol-Myers SquibbNot yet recruitingStage IV Prostate Cancer AJCC v8 | Prostate Carcinoma | Stage III Prostate Cancer AJCC v8 | Prostate Small Cell Neuroendocrine CarcinomaUnited States
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University Health Network, TorontoTakara Bio Inc.RecruitingRelapsed or Refractory Chronic Lymphocytic Leukemia | Relapsed or Refractory Small Lymphocytic Lymphoma | Relapsed or Refractory CD19+ B-cell LymphomaCanada
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City of Hope Medical CenterNational Cancer Institute (NCI)Recruiting
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Dr. Melody Smith, MD, MSOrca Biosystems, Inc.Recruiting
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Christian Medical College, Vellore, IndiaDr. H. Trent Spencer, Professor, Emory University of Medicine, Atlanta Ga...Recruiting
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Xinqiao Hospital of ChongqingTCRCure Biopharma Ltd.Not yet recruitingOvarian Cancer | Endometrial Cancer
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Shenzhen Geno-Immune Medical InstituteShenzhen Second People's Hospital; Shenzhen Third People's HospitalRecruiting
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Children's Hospital of Chongqing Medical UniversityRecruiting